Dysferlin
Showing 1 - 12 of 12
Limb Girdle Muscular Dystrophy Trial in Columbus (SRP-6004)
Enrolling by invitation
- Limb Girdle Muscular Dystrophy
- SRP-6004
-
Columbus, OhioNationwide Children's Hospital
Jun 7, 2023
Dysferlinopathy Trial in Columbus (rAAVrh74.MHCK7.DYSF.DV)
Completed
- Dysferlinopathy
-
Columbus, OhioNationwide Children's Hosptial
May 11, 2021
Dysferlinopathy, Miyoshi Myopathy, LGMDR2 Trial in Moscow
Enrolling by invitation
- Dysferlinopathy
- +3 more
-
Moscow, Russian FederationHuman Stem Cells Institute
Jul 25, 2022
Right Ventricular Function Among Chronic Lung Disease
Not yet recruiting
- Right Ventricular Function
- Echocardiographic examination
- (no location specified)
Nov 14, 2023
Becker Muscular Dystrophy Trial in Sacramento ((-)-epicatechin)
Completed
- Becker Muscular Dystrophy
-
Sacramento, CaliforniaUniversity of California, Davis
Nov 22, 2021
Long-Term Development of Muscular Dystrophy Outcome Assessments
Not yet recruiting
- LGMD1A
- +33 more
-
Richmond, VirginiaVirginia Commonwealth University
Aug 3, 2023
Becker Muscular Dystrophy Trial in Pittsburgh (Vamorolone, Placebo)
Recruiting
- Becker Muscular Dystrophy
- Vamorolone
- Placebo
-
Pittsburgh, PennsylvaniaUniversity of Pittsburgh
Jun 22, 2022
Duchenne Muscular Dystrophy Trial in Vancouver (Vamorolone)
Recruiting
- Duchenne Muscular Dystrophy
-
Vancouver, British Columbia, CanadaBritish Columbia Children's Hospital
Mar 24, 2022
Dysferlinopathy Trial in Basel (Bortezomib)
Terminated
- Dysferlinopathy
-
Basel, SwitzerlandNeuromuskuläres Zentrum, Universitätsspital Basel
Sep 20, 2017
Genetics of Cardiovascular and Neuromuscular Disease
Recruiting
- Cardiomyopathy
- +2 more
- Blood draw (genetic testing)
-
Chicago, IllinoisUniversity of Chicago
Aug 23, 2016
LGMD2B, Miyoshi Myopathy, Dysferlinopathy Trial in Munich (deflazacort, )
Completed
- LGMD2B
- +2 more
- deflazacort
- placebo
-
Munich, GermanyFriedrich-Baur-Institute, Dept. of Neurology, Ludwig-Maximilians
Aug 31, 2015
Evaluation of Limb-Girdle Muscular Dystrophy
Completed
- Becker Muscular Dystrophy
- +3 more
-
Washington, District of Columbia
- +1 more
Mar 6, 2014