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Dysferlin

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STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Limb Girdle Muscular Dystrophy Trial in Columbus (SRP-6004)

Enrolling by invitation
  • Limb Girdle Muscular Dystrophy
  • SRP-6004
  • Columbus, Ohio
    Nationwide Children's Hospital
Jun 7, 2023

Dysferlinopathy Trial in Columbus (rAAVrh74.MHCK7.DYSF.DV)

Completed
  • Dysferlinopathy
  • Columbus, Ohio
    Nationwide Children's Hosptial
May 11, 2021

Dysferlinopathy, Miyoshi Myopathy, LGMDR2 Trial in Moscow

Enrolling by invitation
  • Dysferlinopathy
  • +3 more
    • Moscow, Russian Federation
      Human Stem Cells Institute
    Jul 25, 2022

    Right Ventricular Function Among Chronic Lung Disease

    Not yet recruiting
    • Right Ventricular Function
    • Echocardiographic examination
    • (no location specified)
    Nov 14, 2023

    Becker Muscular Dystrophy Trial in Sacramento ((-)-epicatechin)

    Completed
    • Becker Muscular Dystrophy
    • Sacramento, California
      University of California, Davis
    Nov 22, 2021

    Long-Term Development of Muscular Dystrophy Outcome Assessments

    Not yet recruiting
    • LGMD1A
    • +33 more
      • Richmond, Virginia
        Virginia Commonwealth University
      Aug 3, 2023

      Becker Muscular Dystrophy Trial in Pittsburgh (Vamorolone, Placebo)

      Recruiting
      • Becker Muscular Dystrophy
      • Pittsburgh, Pennsylvania
        University of Pittsburgh
      Jun 22, 2022

      Duchenne Muscular Dystrophy Trial in Vancouver (Vamorolone)

      Recruiting
      • Duchenne Muscular Dystrophy
      • Vancouver, British Columbia, Canada
        British Columbia Children's Hospital
      Mar 24, 2022

      Dysferlinopathy Trial in Basel (Bortezomib)

      Terminated
      • Dysferlinopathy
      • Basel, Switzerland
        Neuromuskuläres Zentrum, Universitätsspital Basel
      Sep 20, 2017

      Genetics of Cardiovascular and Neuromuscular Disease

      Recruiting
      • Cardiomyopathy
      • +2 more
      • Blood draw (genetic testing)
      • Chicago, Illinois
        University of Chicago
      Aug 23, 2016

      LGMD2B, Miyoshi Myopathy, Dysferlinopathy Trial in Munich (deflazacort, )

      Completed
      • LGMD2B
      • +2 more
      • Munich, Germany
        Friedrich-Baur-Institute, Dept. of Neurology, Ludwig-Maximilians
      Aug 31, 2015

      Evaluation of Limb-Girdle Muscular Dystrophy

      Completed
      • Becker Muscular Dystrophy
      • +3 more
        • Washington, District of Columbia
        • +1 more
        Mar 6, 2014