Fanconi Anemia
Showing 26 - 50 of 2,214
Fanconi Anemia Trial in Boston (metformin HCl)
Completed
- Fanconi Anemia
- metformin HCl
-
Boston, MassachusettsBoston Children's Hospital
Oct 9, 2020
Fanconi Anemia Trial in Cincinnati (AMD3100, AmCell CliniMACs)
Completed
- Fanconi Anemia
- AMD3100
- AmCell CliniMACs
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Oct 28, 2020
Fanconi Anemia Complementation Group A Trial in Stanford (RP-L102)
Active, not recruiting
- Fanconi Anemia Complementation Group A
- RP-L102
-
Stanford, CaliforniaStanford University Institute for Stem Cell Biology and Regenera
Nov 23, 2020
Fanconi Anemia Complementation Group A Trial in Madrid (RP-L102)
Recruiting
- Fanconi Anemia Complementation Group A
- RP-L102
-
Madrid, SpainHospital Infantil Universitario Niño Jesús (HIUNJ)
Oct 16, 2020
Adenine Phosphoribosyltransferase Deficiency, AH Amyloidosis, AHL Amyloidosis Trial in Bristol
Recruiting
- Adenine Phosphoribosyltransferase Deficiency
- +83 more
-
Bristol, South West, United KingdomZoe Plummer
Sep 26, 2023
Fanconi Anemia Trial in Cincinnati (Etanercept)
Completed
- Fanconi Anemia
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Sep 10, 2020
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Biomarker for Cystinosis Disease: BioCystinosis (BioCystinosis)
Active, not recruiting
- Renal Fanconi Syndrome
- +2 more
-
Rostock, Germany
- +3 more
May 12, 2021
Fanconi Anemia Trial in Barcelona, Madrid (procedure, biological, other, drug)
Unknown status
- Fanconi Anemia
- IV administration of Genetically Engineered Hematopoietic Stem/Progenitors Cells (HSPCs)
- +5 more
-
Barcelona, Spain
- +1 more
Nov 23, 2020
Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
Enrolling by invitation
- Fanconi Anemia Complementation Group A
- Fanconi Anemia
- Safety and efficacy assessments
-
Madrid, SpainHospital Infantil Universitario Niño Jesús (HIUNJ)
Jun 18, 2020
Fanconi Anemia Trial in Beijing, Shenzhen (Gene-modified autologous stem cells)
Unknown status
- Fanconi Anemia
- Gene-modified autologous stem cells
-
Beijing, Beijing, China
- +2 more
Sep 18, 2019
Chronic Myeloproliferative Disorders, Leukemia, Lymphoma Trial in Buffalo (biological, drug, procedure)
Completed
- Chronic Myeloproliferative Disorders
- +7 more
- anti-thymocyte globulin
- +11 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Jan 29, 2020
Fanconi Anemia Trial in Milwaukee (CliniMACs device, Busulfan, Fludarabine)
Completed
- Fanconi Anemia
- CliniMACs device
- +4 more
-
Milwaukee, WisconsinMedical College of Wisconsin
Sep 3, 2019
Acute Myeloid Leukemia in Remission, de Novo Myelodysplastic Syndrome, Fanconi Anemia Trial in Brazil, United States (procedure,
Completed
- Acute Myeloid Leukemia in Remission
- +3 more
- Allogeneic Bone Marrow Transplantation
- +7 more
-
Oakland, California
- +4 more
Jan 17, 2020
Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)
Completed
- Hurler Syndrome
- +14 more
-
Atlanta, GeorgiaChildren's Healthcare of Atlanta
Dec 20, 2019
Fanconi Anemia, Dyskeratosis Congenita Trial in Boston (danazol)
Terminated
- Fanconi Anemia
- Dyskeratosis Congenita
-
Boston, MassachusettsChildren's Hospital Boston
Jan 31, 2019
Advanced Breast Cancer, HER2/Neu Negative, Triple-Negative Breast Cancer Trial in Stanford (Talazoparib Tosylate)
Active, not recruiting
- Advanced Breast Cancer
- +2 more
- Talazoparib Tosylate
-
Stanford, CaliforniaStanford University Hospitals and Clinics
Nov 16, 2022
Hematopoietic Stem Cell Transplantation, Malignant Hematological Diseases Trial in Suzhou (Umbilical Cord Blood Transplantation)
Recruiting
- Hematopoietic Stem Cell Transplantation
- Malignant Hematological Diseases
- Umbilical Cord Blood Transplantation
-
Suzhou, Jiangsu, ChinaThe First Affiliated Hospital of Soochow university
Jul 3, 2023
Acquired Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria, Inherited Bone Marrow Failure Syndromes Trial in Philadelphia
Recruiting
- Acquired Aplastic Anemia
- +2 more
- CliniMACs
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
Mar 1, 2022
Bone Marrow Failure Syndromes Trial in Philadelphia (MRD-BMT with Fludarabine-based RIC for Acquired AA, MRD-BMT with
Recruiting
- Bone Marrow Failure Syndromes
- MRD-BMT with Fludarabine-based RIC for Acquired AA
- +2 more
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
May 6, 2022
Spectrum of Hematological Disorders in Pediatrics
Not yet recruiting
- Pancytopenia
- CBC.with with differential Peripheral smear
- (no location specified)
Jul 22, 2022
Hematopoietic Malignancy, Relapse/Recurrence, Hematopoietic Stem Cell Transplantation Trial in Suzhou (Umbilical Cord Blood
Recruiting
- Hematopoietic Malignancy
- +2 more
- Umbilical Cord Blood Transplantation
-
Suzhou, Jiangsu, ChinaThe First Affiliated Hospital of Soochow university
Nov 6, 2023
Solid Tumor, Adult Trial in Miami (Pembrolizumab 200 mg Q3W)
Active, not recruiting
- Solid Tumor, Adult
- Pembrolizumab 200 mg Q3W
-
Miami, FloridaMiami Cancer Institute at Baptist Health, Inc.
Nov 18, 2022
Acute Lymphoblastic Leukemia in Remission, Acute Myeloid Leukemia in Remission, MDS Trial in Houston (CliniMACS)
Not yet recruiting
- Acute Lymphoblastic Leukemia in Remission
- +10 more
- CliniMACS
-
Houston, Texas
- +1 more
Dec 8, 2022