GALNS
Showing 1 - 15 of 15
Mucopolysaccharidosis IV A, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110 - Weekly, BMN 110 - Every Other Week)
Completed
- Mucopolysaccharidosis IV A
- +2 more
- BMN 110 - Weekly
- BMN 110 - Every Other Week
-
Phoenix, Arizona
- +42 more
Jul 19, 2021
Non-invasive Functional Assessment and Pathogenesis of Morquio A
Recruiting
- Mucopolysaccharidosis IV Type A
- +2 more
- Imaging, gait analysis, growth, joint test, hearing test, questionnaire, etc.
-
Wilmington, DelawareNemours Children's Health, Delaware Valley
Mar 9, 2022
Birth Defects in Neonatal Intensive Care Units
Recruiting
- Genetic Disease
- +2 more
-
Shanghai, Shanghai, ChinaChildren Hospital of Fudan University
Mar 7, 2022
Natural History of Atypical Morquio A Disease
Active, not recruiting
- Mucopolysaccharidosis IV A
- Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]
-
Bordeaux, Aquitaine, FranceRheumatology department - Bordeaux University Hospital
Feb 15, 2022
Mucopolysaccharidosis IVA (Morquio A Syndrome) Trial in Australia (BMN 110)
Completed
- Mucopolysaccharidosis IVA (Morquio A Syndrome)
- BMN 110
-
Westmead, New South Wales, Australia
- +4 more
Sep 24, 2019
Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110)
Completed
- Mucopolysaccharidosis IVA
- +2 more
- BMN 110
-
Oakland, California
- +4 more
Jul 12, 2017
Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110)
Terminated
- Mucopolysaccharidosis IVA
- +2 more
- BMN 110
-
Oakland, California
- +10 more
Dec 24, 2015
Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Germany, United Kingdom, United States (BMN 110)
Terminated
- Mucopolysaccharidosis IVA
- +2 more
- BMN 110
-
Oakland, California
- +6 more
Dec 8, 2015
Children With Mucopolysaccharidosis Type IVa
Withdrawn
- Mucopolysaccharidosis IV
- Morquio A Disease
-
Birmingham, West Midlands, United KingdomBirmingham Children's Hospital NHS Foundation Trust
Jul 27, 2016
Mucopolysaccharidosis Disorders in Patients Presenting With
Completed
- Mucopolysaccharidosis IV A
- Mucopolysaccharidosis VI
- Enzyme testing
-
Minneapolis, Minnesota
- +1 more
Jul 31, 2015
Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
Terminated
- MPS IV A
- +2 more
-
Oakland, California
- +14 more
Dec 5, 2014
Detect Unrecognized Mucopolysaccharidosis in Children Visiting
Terminated
- Mucopolysaccharidoses
- +4 more
- Dried blood spot test for MPS
-
New Brunswick, New Jersey
- +1 more
May 23, 2013