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GALNS

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STUDY
CONDITIONS
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Mucopolysaccharidosis IV A, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110 - Weekly, BMN 110 - Every Other Week)

Completed
  • Mucopolysaccharidosis IV A
  • +2 more
  • BMN 110 - Weekly
  • BMN 110 - Every Other Week
  • Phoenix, Arizona
  • +42 more
Jul 19, 2021

Non-invasive Functional Assessment and Pathogenesis of Morquio A

Recruiting
  • Mucopolysaccharidosis IV Type A
  • +2 more
  • Imaging, gait analysis, growth, joint test, hearing test, questionnaire, etc.
  • Wilmington, Delaware
    Nemours Children's Health, Delaware Valley
Mar 9, 2022

Birth Defects in Neonatal Intensive Care Units

Recruiting
  • Genetic Disease
  • +2 more
    • Shanghai, Shanghai, China
      Children Hospital of Fudan University
    Mar 7, 2022

    Natural History of Atypical Morquio A Disease

    Active, not recruiting
    • Mucopolysaccharidosis IV A
    • Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]
    • Bordeaux, Aquitaine, France
      Rheumatology department - Bordeaux University Hospital
    Feb 15, 2022

    Mucopolysaccharidosis IVA (Morquio A Syndrome) Trial in Australia (BMN 110)

    Completed
    • Mucopolysaccharidosis IVA (Morquio A Syndrome)
    • BMN 110
    • Westmead, New South Wales, Australia
    • +4 more
    Sep 24, 2019

    Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110)

    Completed
    • Mucopolysaccharidosis IVA
    • +2 more
    • BMN 110
    • Oakland, California
    • +4 more
    Jul 12, 2017

    Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110)

    Terminated
    • Mucopolysaccharidosis IVA
    • +2 more
    • BMN 110
    • Oakland, California
    • +10 more
    Dec 24, 2015

    Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Germany, United Kingdom, United States (BMN 110)

    Terminated
    • Mucopolysaccharidosis IVA
    • +2 more
    • BMN 110
    • Oakland, California
    • +6 more
    Dec 8, 2015

    Children With Mucopolysaccharidosis Type IVa

    Withdrawn
    • Mucopolysaccharidosis IV
    • Morquio A Disease
      • Birmingham, West Midlands, United Kingdom
        Birmingham Children's Hospital NHS Foundation Trust
      Jul 27, 2016

      Mucopolysaccharidosis Disorders in Patients Presenting With

      Completed
      • Mucopolysaccharidosis IV A
      • Mucopolysaccharidosis VI
      • Enzyme testing
      • Minneapolis, Minnesota
      • +1 more
      Jul 31, 2015

      MPS IV A, Mucopolysaccharidosis IVA, Morquio A Syndrome Trial in United Kingdom (BMN 110)

      Terminated
      • MPS IV A
      • +2 more
      • BMN 110
      • Birmingham, United Kingdom
      • +3 more
      Aug 28, 2015

      Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)

      Terminated
      • MPS IV A
      • +2 more
        • Oakland, California
        • +14 more
        Dec 5, 2014

        MPS IV A Trial in Worldwide (BMN 110 Weekly, Placebo, BMN 110 Every Other Week)

        Completed
        • MPS IV A
        • BMN 110 Weekly
        • +2 more
        • Oakland, California
        • +27 more
        Jun 6, 2014

        MPS IV A Trial in Birmingham, London, Manchester (BMN 110)

        Completed
        • MPS IV A
        • BMN 110
        • Birmingham, United Kingdom
        • +2 more
        May 28, 2014

        Detect Unrecognized Mucopolysaccharidosis in Children Visiting

        Terminated
        • Mucopolysaccharidoses
        • +4 more
        • Dried blood spot test for MPS
        • New Brunswick, New Jersey
        • +1 more
        May 23, 2013