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Hemophilia A (severe or moderately severe)

Showing 1 - 25 of >10,000

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Hemophilia A, Hemophilia B Trial (SerpinPC)

Not yet recruiting
  • Hemophilia A
  • Hemophilia B
  • (no location specified)
Mar 16, 2023

Hemophilia B Without Inhibitor Trial (Low dose KL001, Middle dose KL001, High dose KL001)

Not yet recruiting
  • Hemophilia B Without Inhibitor
  • Low dose KL001
  • +2 more
  • (no location specified)
Nov 5, 2023

Hemophilia B Trial (CSL222 (AAV5-hFIXco-Padua))

Not yet recruiting
  • Hemophilia B
  • CSL222 (AAV5-hFIXco-Padua)
  • (no location specified)
Aug 14, 2023

Hemophilia A Trial in Little Rock (ASC618)

Recruiting
  • Hemophilia A
  • ASC618
  • Little Rock, Arkansas
    Arkansas Children's Hospital
Jan 30, 2023

Study of AAV5-hFIX in Severe or Moderately Severe Haemophilia B

Active, not recruiting
  • Hemophilia B
  • AAV5-hFIX
  • Berlin, Germany
  • +5 more
Jan 17, 2023

Hemophilia B Trial in Denmark, Germany, Netherlands (AAV5-hFIX)

Completed
  • Hemophilia B
  • AAV5-hFIX
  • Copenhagen, Denmark
  • +6 more
Jun 1, 2022

Hemophilia A, Hemophilia B Trial in Korea, Republic of, South Africa, Taiwan (marstacimab)

Recruiting
  • Hemophilia A
  • Hemophilia B
  • Seoul, Seoul-teukbyeolsi [seoul], Korea, Republic of
  • +3 more
Jan 18, 2023

Hemophilia Trial in Tianjin (KN057 dose?, KN057 dose ?, KN057 dose ?)

Recruiting
  • Hemophilia
  • KN057 doseⅠ
  • +2 more
  • Tianjin, Tianjin, China
  • +1 more
Jul 20, 2022

Hemophilia A Trial in United Kingdom, United States (SIG-001)

Terminated
  • Hemophilia A
  • SIG-001
  • Indianapolis, Indiana
  • +5 more
Nov 7, 2022

Hemophilia B Trial in India (Nonacog alfa)

Completed
  • Hemophilia B
  • Nonacog alfa
  • Surat, Gujarat, India
  • +4 more
Jun 29, 2022

Hemophilia B Trial in Worldwide (AAV5-hFIXco-Padua)

Active, not recruiting
  • Hemophilia B
  • AAV5-hFIXco-Padua
  • Factor IX (FIX)
  • Phoenix, Arizona
  • +32 more
Sep 26, 2022

Hemophilia B Trial in United States (AAV5-hFIXco-Padua (AMT-061))

Active, not recruiting
  • Hemophilia B
  • AAV5-hFIXco-Padua (AMT-061)
  • Los Angeles, California
  • +3 more
May 17, 2022

Hemophilia A, Hemophilia B Trial in Worldwide (PF-06741086)

Recruiting
  • Hemophilia A
  • Hemophilia B
  • Tampa, Florida
  • +62 more
Dec 14, 2022

Hemophilia B Trial in Worldwide (BAX 326, BeneFIX)

Completed
  • Hemophilia B
  • BAX 326
  • BeneFIX
  • Rosario, Argentina
  • +24 more
Apr 30, 2021

Hemophilia A Trial in Worldwide (PF-07055480 (giroctocogene fitelparovec): Recombinant AAV2/6 Human Factor VIII Gene Therapy)

Active, not recruiting
  • Hemophilia A
  • PF-07055480 (giroctocogene fitelparovec): Recombinant AAV2/6 Human Factor VIII Gene Therapy
  • Mountain View, California
  • +34 more
Jan 26, 2022

Hemophilia B, Hemophilia A Trial in Worldwide (Standard of Care FIX Replacement therapy, Standard of Care FVIII Replacement

Recruiting
  • Hemophilia B
  • Hemophilia A
  • Standard of Care FIX Replacement therapy
  • Standard of Care FVIII Replacement therapy
  • Palo Alto, California
  • +77 more
Dec 29, 2022

Hemophilia A Trial in Toronto (Antihemophilic Factor Manufactured and Formulated without Added Human or Animal Proteins

Completed
  • Hemophilia A
  • Antihemophilic Factor Manufactured and Formulated without Added Human or Animal Proteins (rAHF-PFM)
  • Toronto, Ontario, Canada
    Hospital for Sick Children
May 3, 2021

Hemophilia B Without Inhibitor Trial (Low dose KL001, Middle dose KL001, High dose KL001)

Not yet recruiting
  • Hemophilia B Without Inhibitor
  • Low dose KL001
  • +2 more
  • (no location specified)
Nov 5, 2023

Severe Hemophilia A Without Inhibitor, Joint Bleed Trial in Bangkok ("Emicizumab", "HEMLIBRA®")

Recruiting
  • Severe Hemophilia A Without Inhibitor
  • Joint Bleed
  • "Emicizumab", "HEMLIBRA®"
  • Bangkok, Thailand
    King Chulalongkorn Memorial hospital
Nov 25, 2023

Dynamics of Anti-factor VIII Antibody Signature During Treatment

Not yet recruiting
  • Severe Hemophilia A
  • +2 more
  • no interventions
  • (no location specified)
Apr 4, 2023

Hemophilia A Trial (NXT007)

Not yet recruiting
  • Hemophilia A
  • (no location specified)
Aug 4, 2023

Bleeding Rates Among Severe Hemophilia A on Emicizumab

Not yet recruiting
  • Hemophilia A
  • Newark, New Jersey
    Newark Beth Israel Medical Center
Oct 26, 2023

Hemophilia A Trial in Worldwide (Human Plasma-Derived Coagulation Factor VIII Concentrate (Virus Inactivated by Polysorbate 80

Completed
  • Hemophilia A
  • Human Plasma-Derived Coagulation Factor VIII Concentrate (Virus Inactivated by Polysorbate 80 Treatment and Vapor Heat Treatment)
  • Sofia, Bulgaria
  • +4 more
Apr 28, 2021

Hemophilia A Trial in Worldwide (Antihemophilic factor, recombinant, manufactured protein-free)

Completed
  • Hemophilia A
  • Antihemophilic factor, recombinant, manufactured protein-free
  • Los Angeles, California
  • +28 more
Apr 28, 2021

Severe Hemophilia Non-Interventional Study

Not yet recruiting
  • Hemophilia A
  • Hemophilia B
  • No Intervention
  • Rzeszów, Podkarpackie, Poland
  • +2 more
Dec 8, 2022