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phase 1/phase 2 (1)

phase 2 (1)

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Universitatsklinikum Hamburg-Eppendorf (1)

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Batten Disease Support and Research Assocation (BDSRA) (1)

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at-gtx-502 (1)

liquid placebo (1)

mycophenolate mofetil (1)

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JNCL

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STUDY

CONDITIONS

INTERVENTIONS

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LAST UPDATED

CLN3, Batten Disease Trial in Columbus (AT-GTX-502)

Active, not recruiting

CLN3
Batten Disease

AT-GTX-502

Columbus, Ohio

Nationwide Children's Hospital

Jul 18, 2022

Neuronal Ceroid Lipofuscinosis, Batten Disease, CLN1 Disease Trial in Hamburg (Natural History)

Recruiting

Neuronal Ceroid Lipofuscinosis
+14 more

Natural History

Hamburg, Germany

University Medical Center Hamburg-Eppendorf

Oct 22, 2021

Juvenile Neuronal Ceroid Lipofuscinosis Trial in Rochester (Mycophenolate mofetil, Liquid Placebo)

Completed

Has Results

Juvenile Neuronal Ceroid Lipofuscinosis

Mycophenolate mofetil
Liquid Placebo

Rochester, New York

University of Rochester

May 7, 2019