LINCL
Showing 1 - 12 of 12
Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Trial in New York (AAVrh.10CUhCLN2 vector 9.0x10^11 genome copies,
Completed
- Batten Disease
- Late-Infantile Neuronal Ceroid Lipofuscinosis
- AAVrh.10CUhCLN2 vector 9.0x10^11 genome copies
- AAVrh.10CUhCLN2 vector 2.85x10^11 genome copies
-
New York, New YorkWeill Cornell Medical College
Jan 31, 2021
Late Infantile Neuronal Ceroid Lipofuscinosis, Batten Disease Trial in New York (AAVrh.10CUCLN2)
Completed
- Late Infantile Neuronal Ceroid Lipofuscinosis
- Batten Disease
- AAVrh.10CUCLN2
-
New York, New YorkWeill Cornell Medical College
Aug 28, 2020
Late Infantile Neuronal Ceroid Lipofuscinosis
Completed
- Batten Disease
- Late Infantile Neuronal Ceroid Lipofuscinosis
-
New York, New YorkWeill Cornell Medicine
Jul 28, 2020
Batten Disease, Late Infantile Neuronal Ceroid Lipofuscinosis Trial in New York (AAV2CUhCLN2 (3x10^12 particle units))
Completed
- Batten Disease
- Late Infantile Neuronal Ceroid Lipofuscinosis
- AAV2CUhCLN2 (3x10^12 particle units)
-
New York, New YorkNew York Presbyterian Hospital - Weill Medical College of Cornel
Jul 22, 2020
Neuronal Ceroid Lipofuscinosis Type 2 Trial in Columbus (Cerliponase Alfa)
Enrolling by invitation
- Neuronal Ceroid Lipofuscinosis Type 2
- Cerliponase Alfa
-
Columbus, OhioNationwide Children's Hospital
Nov 29, 2021
Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190,
Completed
- Jansky-Bielschowsky Disease
- +4 more
- BMN 190
- Intracerebroventricular (ICV) access device
-
Columbus, Ohio
- +3 more
Jul 28, 2022
Neuronal Ceroid Lipofuscinosis, Batten Disease, CLN1 Disease Trial in Hamburg (Natural History)
Recruiting
- Neuronal Ceroid Lipofuscinosis
- +14 more
- Natural History
-
Hamburg, GermanyUniversity Medical Center Hamburg-Eppendorf
Oct 22, 2021
Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190)
Completed
- Jansky-Bielschowsky Disease
- +3 more
- BMN 190
-
Columbus, Ohio
- +4 more
Mar 6, 2019
Genotype - Phenotype Correlations of LINCL
Completed
- Batten Disease
- Late-Infantile Neuronal Ceroid Lipfuscinosis
- (no location specified)
Jul 28, 2016
Collection of Cerebrospinal Fluid in Healthy Children
Terminated
- Late Infantile Neuronal Ceroid Lipofuscinosis
- Batten Disease
- Group 1
-
New York, New YorkWeill Cornell Medical College / New York Presbyterian Hospital
May 3, 2016
Neuronal Ceroid Lipofuscinosis Trial in Portland (Surgery to implant human CNS stem cells (HuCNS-SC), Medication to suppress the
Completed
- Neuronal Ceroid Lipofuscinosis
- Surgery to implant human CNS stem cells (HuCNS-SC)
- Medication to suppress the immune system
-
Portland, OregonOregon Health and Science University
Jan 13, 2015
Neuronal Ceroid Lipofuscinosis Trial in Portland (HuCNS-SC)
Withdrawn
- Neuronal Ceroid Lipofuscinosis
- HuCNS-SC
-
Portland, OregonOregon Health and Science University
Jan 13, 2015