You have 9 free searches left this month | for more free features.
Clincosm LogoSign in Get a demo

Leukodystrophy

Showing 1 - 25 of 87
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED

Lysosomal Storage Disease, Metachromatic Leukodystrophy Trial in Milan (OTL-200 Gene Therapy)

Active, not recruiting
  • Lysosomal Storage Disease
  • Metachromatic Leukodystrophy
  • OTL-200 Gene Therapy
  • Milan, Italy
    Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 4, 2022

Lysosomal Storage Diseases, Metachromatic Leukodystrophy Trial in Milan (OTL-200)

Recruiting
  • Lysosomal Storage Diseases
  • Metachromatic Leukodystrophy
  • OTL-200
  • Milan, Italy
    Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 16, 2022

Learn About Metachromatic Leukodystrophy (MLD) in Spain

Not yet recruiting
  • Metachromatic Leukodystrophy (MLD)
  • No Intervention
  • Santiago de Compostela, A Coruna, Spain
  • +9 more
Mar 9, 2023

Macrophages Activation Pattern in X-linked Adrenoleukodystrophy,

Recruiting
  • Adrenoleukodystrophy
  • +3 more
  • Blood sample collection
  • Le Kremlin-Bicêtre, France
  • +1 more
Oct 10, 2022

Metachromatic Leukodystrophy, Adrenoleukodystrophy Trial in Shenzhen (transduced CD34+ hematopoietic stem cell)

Recruiting
  • Metachromatic Leukodystrophy
  • Adrenoleukodystrophy
  • transduced CD34+ hematopoietic stem cell
  • Shenzhen, Guangdong, China
    Shenzhen Second People's Hospital, The First Affiliated Hospital
May 25, 2022

X-linked Adrenoleukodystrophy Trial in Leipzig (SMART-ALD, Waiting list)

Recruiting
  • X-linked Adrenoleukodystrophy
  • SMART-ALD
  • Waiting list
  • Leipzig, Saxony, Germany
  • +1 more
Aug 16, 2022

Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)

Recruiting
  • Adrenoleukodystrophy
  • +11 more
  • DUOC-01
  • Durham, North Carolina
    Duke University Medical Center
Oct 24, 2022

Metachromatic Leukodystrophy Trial in Le Kremlin-Bicêtre (intracerebral administration of AAVrh.10cuARSA)

Active, not recruiting
  • Metachromatic Leukodystrophy
  • intracerebral administration of AAVrh.10cuARSA
  • Le Kremlin-Bicêtre, France
    Bicêtre Hospital - Paris Sud
Jan 10, 2022

Leukodystrophy, Globoid Cell Trial in Worldwide (PBKR03)

Recruiting
  • Leukodystrophy, Globoid Cell
  • PBKR03
  • Chicago, Illinois
  • +8 more
Aug 17, 2022

Metachromatic Leukodystrophy Trial in Durham (Enriched Hematopoetic Stem Cell Infusion)

No longer available
  • Metachromatic Leukodystrophy
  • Enriched Hematopoetic Stem Cell Infusion
  • Durham, North Carolina
    Duke University
Jul 15, 2022

Metachromatic Leukodystrophy Study (HOME Study)

Recruiting
  • Metachromatic Leukodystrophy
    • Danbury, Connecticut
      National Organization for Rare Disorders
    Oct 28, 2021

    Leukodystrophy, White Matter Disease, Leukoencephalopathies Trial in United States

    Recruiting
    • Leukodystrophy
    • +21 more
      • Palo Alto, California
      • +8 more
      Dec 21, 2021

      Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

      Recruiting
      • Mucopolysaccharidosis Disorders
      • +28 more
      • Stem Cell Transplantation
      • +7 more
      • Minneapolis, Minnesota
        Masonic Cancer Center, University of Minnesota
      Nov 1, 2022

      Leukodystrophy Trial in Salt Lake City

      Recruiting
      • Leukodystrophy
        • Salt Lake City, Utah
          Primary Children's Hospital
        Nov 2, 2022

        Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human

        Completed
        • Mucopolysaccharidosis I
        • +15 more
        • Human Placental Derived Stem Cell
        • Denver, Colorado
        • +2 more
        Oct 24, 2022

        Metachromatic Leukodystrophy (MLD) Trial in Worldwide (SHP611)

        Active, not recruiting
        • Metachromatic Leukodystrophy (MLD)
        • Torrance, California
        • +29 more
        Dec 13, 2022

        Lysosomal Storage Disease, Metachromatic Leukodystrophy Trial in Milan (OTL-200)

        Active, not recruiting
        • Lysosomal Storage Disease
        • Metachromatic Leukodystrophy
        • OTL-200
        • Milan, Italy
          Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
        Sep 29, 2021

        Neurodegenerative Diseases, Leukodystrophy, Ataxia Trial (Home exercise)

        Recruiting
        • Neurodegenerative Diseases
        • +2 more
        • Home exercise
        • Baltimore, Maryland
          Kennedy Krieger Institute
        Jan 5, 2023

        Pediatric Subjects With Globoid Cell Leukodystrophy (GLD)

        Withdrawn
        • Leukodystrophy, Globoid Cell
          • (no location specified)
          May 30, 2021

          Metachromatic Leukodystrophy (MLD) Trial in Hvidovre (rhASA - Dose Level 1, rhASA - Dose Level 2, rhASA - Dose Level 3)

          Completed
          Has Results
          • Metachromatic Leukodystrophy (MLD)
          • rhASA - Dose Level 1
          • +2 more
          • Hvidovre, Denmark
            Rigshospitalet
          Jun 23, 2021

          LeukoSEQ: Whole Genome Sequencing asFirst-Line Diagnostic Tool

          Recruiting
          • Leukodystrophy
          • White Matter Disease
            • Philadelphia, Pennsylvania
              The Children's Hospital of Philadelphia
            Sep 13, 2022

            Krabbe Disease Trial in Ann Arbor (FBX-101)

            Recruiting
            • Krabbe Disease
            • FBX-101
            • Ann Arbor, Michigan
              University of Michigan Hospitals - Michigan Medicine
            Feb 13, 2023

            Krabbe Disease Trial in Ann Arbor (FBX-101)

            Recruiting
            • Krabbe Disease
            • FBX-101
            • Ann Arbor, Michigan
              University of Michigan Hospitals - Michigan Medicine
            Aug 24, 2022

            Quality of Life in Women With X-linked Adrenoleukodystrophy

            Recruiting
            • X-linked Adrenoleukodystrophy
              • Leipzig, Saxony, Germany
                Leipzig University Medical Center, Leukodystrophy Outpatient Cli
              Apr 4, 2022

              Leukodystrophy: An Observational Study at Sohag University

              Not yet recruiting
              • Children With Leukodystrophy
              • MRI
              • (no location specified)
              Mar 2, 2021