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MPS 7

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Mucopolysaccharidosis II Trial in Salt Lake City, Fairfax (Genetic HMI-203)

Recruiting
  • Mucopolysaccharidosis II
  • Genetic HMI-203
  • Oakland, California
  • +5 more
Jan 26, 2023

MPS 7, Sly Syndrome, Mucopolysaccharidosis Trial in United States (UX003, Placebo)

Completed
  • MPS 7
  • +3 more
  • Oakland, California
  • +3 more
Jul 16, 2020

Sly Syndrome, MPS VII, Mucopolysaccharidosis Trial in Worldwide (UX003)

Completed
  • Sly Syndrome
  • +3 more
  • Oakland, California
  • +6 more
Jul 16, 2020

Sleep, Inadequate Trial in Natick (Protein Nutrition During Recovery)

Not yet recruiting
  • Sleep, Inadequate
  • Protein Nutrition During Recovery
  • Natick, Massachusetts
    US Army Research Institute of Environmental Medicine
Oct 4, 2023

Set for Head, Neck and Respiratory Disease in

Completed
  • Mucopolysaccharidosis Type II
    • Manchester, Lancashire, United Kingdom
      Manchester University NHS Foundation Trust
    Aug 31, 2023

    Mucopolysaccharidosis IV Type A, Morquio A Syndrome, MPS IVA Trial in Worldwide (Vimizim® (elosulfase alfa))

    Active, not recruiting
    • Mucopolysaccharidosis IV Type A
    • +2 more
    • Vimizim® (elosulfase alfa)
    • Phoenix, Arizona
    • +78 more
    Dec 23, 2022

    Mucopolysaccharidosis Type I (MPS I), Hurler Syndrome, Hurler-Scheie Syndrome Trial in Orange, Philadelphia, Porto Alegre

    Active, not recruiting
    • Mucopolysaccharidosis Type I (MPS I)
    • +2 more
    • RGX-111
    • Orange, California
    • +3 more
    Jan 9, 2023

    Mucopolysaccharidosis II Trial in Cincinnati (DNL310)

    Enrolling by invitation
    • Mucopolysaccharidosis II
    • Cincinnati, Ohio
      Cincinnati Children's Hospital Medical Center
    Oct 10, 2023

    Mucopolysaccharidosis IH/S, Mucopolysaccharidosis IS Trial in Minneapolis (Autologous Plasmablasts (B cells))

    Not yet recruiting
    • Mucopolysaccharidosis IH/S
    • Mucopolysaccharidosis IS
    • Autologous Plasmablasts (B cells)
    • Minneapolis, Minnesota
      University of Minnesota
    Jan 20, 2023

    Kinesio Taping, Dry Needling and Lidocain Injection Methods in

    Completed
    • Myofascial Pain Syndrome
    • kinesiotherapy
    • (no location specified)
    Aug 26, 2023

    Myofascial Pain Syndrome of Neck Trial in Riyadh (Radial shockwave therapy)

    Recruiting
    • Myofascial Pain Syndrome of Neck
    • Radial shockwave therapy
    • Riyadh, Saudi Arabia
      Physical Rehabilitation Department, King Faisal Specialist Hospi
    May 19, 2022

    Myofascial Pain Syndrome, Trigger Point Pain, Myofascial Trial (conventional therapy, Experimental group 1 : pressure release

    Not yet recruiting
    • Myofascial Pain Syndrome
    • Trigger Point Pain, Myofascial
    • conventional therapy
    • +2 more
    • (no location specified)
    Jan 9, 2023

    Mucopolysaccharidosis IV A, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110 - Weekly, BMN 110 - Every Other Week)

    Completed
    • Mucopolysaccharidosis IV A
    • +2 more
    • BMN 110 - Weekly
    • BMN 110 - Every Other Week
    • Phoenix, Arizona
    • +42 more
    Jul 19, 2021

    Mucopolysaccharidosis Type II, Metabolic Diseases Trial in Russian Federation (GNR-055 1.0-2.0-3.0 mg/kg, GNR-055 2.0 mg/kg,

    Recruiting
    • Mucopolysaccharidosis Type II
    • Metabolic Diseases
    • GNR-055 1.0-2.0-3.0 mg/kg
    • +2 more
    • Ekaterinburg, Russian Federation
    • +4 more
    Jan 13, 2022

    MPS I Trial in Oakland (SB-318)

    Terminated
    • MPS I
    • SB-318
    • Oakland, California
      UCSF Benioff Children's Hospital Oakland
    Jan 6, 2023

    Myofascial Pain Syndromes, Myofascial Trigger Point Pain Trial in Istanbul (dry needling, cold spray and stretching)

    Completed
    • Myofascial Pain Syndromes
    • Myofascial Trigger Point Pain
    • dry needling
    • cold spray and stretching
    • Istanbul, Turkey
      Haydarpaşa Numune Education and Research Hospital
    Dec 16, 2022

    Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)

    Terminated
    • Mucopolysaccharidosis Type 3 B
    • rAAV9.CMV.hNAGLU
    • Columbus, Ohio
    • +3 more
    Apr 29, 2022

    Myofascial Pain Syndrome Trial in Ankara (ultrasound guided rhomboid intercostal block)

    Completed
    • Myofascial Pain Syndrome
    • ultrasound guided rhomboid intercostal block
    • Ankara, Turkey
      Diskapi Yildirim Beyazit Training and Research Hospital
    Nov 7, 2021

    Mucopolysaccharidosis Type 7 Trial in Manchester (UX003)

    Completed
    • Mucopolysaccharidosis Type 7
    • Manchester, United Kingdom
      Manchester Academic Health Science Centre
    Dec 12, 2018

    Sanfilippo Syndrome Type A (MPS IIIA) Trial in Germany, Turkey, United States (SOBI003)

    Completed
    • Sanfilippo Syndrome Type A (MPS IIIA)
    • Oakland, California
    • +3 more
    Nov 18, 2021

    Sanfilippo Syndrome Type A (MPS IIIA) Trial in Oakland, Chapel Hill, Ankara (SOBI003)

    Completed
    • Sanfilippo Syndrome Type A (MPS IIIA)
    • Oakland, California
    • +2 more
    Feb 2, 2022

    Temporomandibular Joint Dysfunction Syndrome, Autonomic Nervous System Imbalance Trial in Istanbul (Auricular Non-Invazive Vagus

    Not yet recruiting
    • Temporomandibular Joint Dysfunction Syndrome
    • Autonomic Nervous System Imbalance
    • Auricular Non-Invazive Vagus Nerve Stimulation + Traditional Rehabilitation Program for TMD
    • Traditional Rehabilitation Program
    • Istanbul, Beşiktaş, Turkey
      Bahçeşehir University
    Aug 15, 2022

    Carotid Structure and Function in MPS Syndromes: A Multicenter

    Completed
    • Mucopolysaccharidoses
      • Orange, California
      • +1 more
      Feb 5, 2021

      Mucopolysaccharidosis II, MPS II Trial in United States (SB-913)

      Terminated
      • Mucopolysaccharidosis II
      • MPS II
      • SB-913
      • Oakland, California
      • +4 more
      Oct 21, 2022

      A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)

      Completed
      • Sanfilippo Syndrome Type A
      • assessment
      • Minneapolis, Minnesota
        University of Minnesota
      May 19, 2021