Mucopolysaccharidosis
Showing 1 - 25 of 205
Mucopolysaccharidosis III-A Trial in Hamburg (JR-441)
Recruiting
- Mucopolysaccharidosis III-A
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Hamburg, GermanyUniversitätsklinikum Hamburg-Eppendorf
Oct 18, 2023
Set for Head, Neck and Respiratory Disease in
Completed
- Mucopolysaccharidosis Type II
-
Manchester, Lancashire, United KingdomManchester University NHS Foundation Trust
Aug 31, 2023
MPS (RaDiCo Cohort) (RaDiCo-MPS)
Recruiting
- Mucopolysaccharidosis I
- +7 more
-
Angers, France
- +22 more
Sep 12, 2023
Mucopolysaccharidosis IH/S, Mucopolysaccharidosis IS Trial in Minneapolis (Autologous Plasmablasts (B cells))
Not yet recruiting
- Mucopolysaccharidosis IH/S
- Mucopolysaccharidosis IS
- Autologous Plasmablasts (B cells)
-
Minneapolis, MinnesotaUniversity of Minnesota
Jan 20, 2023
Mucopolysaccharidosis II Trial in Cincinnati (DNL310)
Enrolling by invitation
- Mucopolysaccharidosis II
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Oct 10, 2023
Before and After Hematopoietic Cell Transplantation in
Enrolling by invitation
- Hematopoietic Cell Transplantation
- Mucopolysaccharidosis Type I
- Laronidase therapy and a stem cell transplant
-
Minneapolis, MinnesotaUniversity of Minnesota Masonic Cancer Center
Nov 22, 2022
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],
Recruiting
- Mucopolysaccharidosis I
- +2 more
- Adalimumab Injection [Humira]
- Saline Solution for Injection
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Torrance, CaliforniaThe Lundquist Institute at Harbor-UCLA Medical Center
Aug 9, 2022
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)
Recruiting
- Mucopolysaccharidosis I
- +7 more
- There is no intervention
-
San Francisco, CaliforniaUniversity of California San Francisco
Nov 9, 2022
Mucopolysaccharidosis II Trial in Oakland (JR-141)
Not yet recruiting
- Mucopolysaccharidosis II
-
Oakland, CaliforniaUCSF Benioff Children's Hospital Oakland
Oct 21, 2022
Mucopolysaccharidosis Type II Observational
Withdrawn
- Mucopolysaccharidosis II
- Observational
-
Oakland, California
- +2 more
Oct 6, 2022
Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)
Active, not recruiting
- Mucopolysaccharidosis Type IIIB
- MPS III B
- AX 250
-
Oakland, California
- +7 more
Jan 16, 2023
Mucopolysaccharidosis I Trial in Wuhan (Laronidase)
Recruiting
- Mucopolysaccharidosis I
-
Wuhan, ChinaInvestigational Site Number :1560001
Jan 15, 2023
Long Term Follow-Up for RGX-111
Enrolling by invitation
- Mucopolysaccharidosis I
- No Intervention
-
Orange, California
- +2 more
Oct 25, 2023
Mucopolysaccharidosis Type II Natural History
Completed
- Mucopolysaccharidosis II
-
Pittsburgh, Pennsylvania
- +2 more
Apr 22, 2022
Mucopolysaccharidosis (MPS), Hunter Syndrome Trial (ELAPRASE, Rituximab, Methotrexate)
Not yet recruiting
- Mucopolysaccharidosis (MPS)
- Hunter Syndrome
- ELAPRASE
- +3 more
- (no location specified)
Aug 8, 2022
Participants With Sanfilippo Syndrome Type IIIC
Not yet recruiting
- Sanfilippo Syndrome Type C
-
Bron, FranceHospices Civils De Lyon
Apr 20, 2023
(LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX
Active, not recruiting
- Hemophilia B
- +2 more
- SB-318
- +2 more
-
Oakland, California
- +4 more
Jan 30, 2023
Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome), Mucopolysaccharidosis Type IH, MPS IH, Hurler Syndrome Trial
Withdrawn
- Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome)
- +2 more
- Autologous Plasmablasts
- (no location specified)
Oct 5, 2022