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Myopathies, Nemaline

Showing 1 - 25 of 88

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Muscle Fatigability of Patients With Congenital Myopathies.

Not yet recruiting
  • Central Core Disease
  • +3 more
  • Natural history and non therapeutical therapy
  • Nijmegen, Gelderland, Netherlands
  • +1 more
Nov 27, 2023

Congenital Myopathy, Neuromuscular Diseases, Musculoskeletal Diseases Trial in Gothenburg (Salbutamol (as Salbutamol Sulfate) 2

Enrolling by invitation
  • Congenital Myopathy
  • +5 more
  • Salbutamol (as Salbutamol Sulfate) 2 Mg Oral Tablet
  • Salbutamol Only Product in Oral Dose Form
  • Gothenburg, Västra Götaland, Sweden
    Sahlgrenska university hospital
Jan 10, 2022

Molecular and Genetic Studies of Congenital Myopathies

Recruiting
  • Central Core Disease
  • +7 more
    • Boston, Massachusetts
      Genetics Division, Boston Children's Hospital
    Sep 7, 2021

    Nemaline Myopathy, Inspiratory Muscle Training Trial in Nijmegen (Threshold IMT, Philips Respironics, Murrysville, PA, USA)

    Completed
    • Nemaline Myopathy
    • Inspiratory Muscle Training
    • Threshold IMT, Philips Respironics, Murrysville, PA, USA
    • Nijmegen, Netherlands
      Radboud university medical center
    Jul 4, 2021

    Muscle Relaxation in Myopathies With Positive Muscle Phenomena

    Unknown status
    • Nemaline Myopathy Type 6
    • +2 more
    • Transcranial magnetic stimulation (TMS)
    • (no location specified)
    Sep 30, 2019

    Myositis, Idiopathic Inflammatory Myopathies Trial in Xiamen (68Ga-FAPI)

    Recruiting
    • Myositis
    • Idiopathic Inflammatory Myopathies
    • Xiamen, Fujian, China
      The first affiliated hospital of Xiamen University
    Jul 12, 2023

    Myositis Trial in Worldwide (Nipocalimab, Placebo, Glucocorticoids)

    Recruiting
    • Myositis
    • Scottsdale, Arizona
    • +50 more
    Jan 17, 2023

    Dermatomyositis, Polymyositis Trial in Orlando (M5049 high dose, Placebo)

    Recruiting
    • Dermatomyositis
    • Polymyositis
    • M5049 high dose
    • Placebo
    • Orlando, Florida
      HMD Research LLC
    Jan 30, 2023

    Idiopathic Inflammatory Myopathies Trial in Beijing (tofacitinib)

    Recruiting
    • Idiopathic Inflammatory Myopathies
    • Beijing, Beijing, China
      Department of Rheumatology and Immunology, Peking University Peo
    Oct 9, 2022

    Myopathy Trial in São Paulo (Chronic transcranial direct current stimulation)

    Recruiting
    • Myopathy
    • Chronic transcranial direct current stimulation
    • São Paulo, Sao Paulo, Brazil
      Samuel K Shinjo
    May 31, 2022

    Primary Mitochondrial Myopathies Trial in Madrid

    Not yet recruiting
    • Primary Mitochondrial Myopathies
      • Madrid, Spain
        Hospital Universitario 12 Octubre
      Dec 7, 2022

      Bullying in Youth With Muscular Dystrophy and Congenital

      Completed
      • Muscular Dystrophies
      • Congenital Myopathy
        • Ottawa, Ontario, Canada
        • +1 more
        Nov 4, 2022

        Idiopathic Inflammatory Myopathies Trial in Brest (description of adult autoimmune myopathies)

        Recruiting
        • Idiopathic Inflammatory Myopathies
        • description of adult autoimmune myopathies
        • Brest, France
          CHU de BREST
        May 20, 2022

        Treatment Side Effects Trial in Sao Paulo (Lipid-lowering agents (Artovastatin))

        Terminated
        • Treatment Side Effects
        • Lipid-lowering agents (Artovastatin)
        • Sao Paulo, Brazil
          Samuel Katsuyuki Shinjo
        May 31, 2022

        Optimizing Treatment on Idiopathic Inflammatory Myopathies

        Recruiting
        • Idiopathic Inflammatory Myopathies
        • Intravenous Infusion
        • Sao Paulo, Brazil
          Samuel Katsuyuki Shinjo
        May 31, 2022

        Study of Inherited Neurological Disorders

        Recruiting
        • Motor Neuron Disease
        • +3 more
          • Bethesda, Maryland
            National Institutes of Health Clinical Center
          Jan 26, 2023

          Natural History Study of Patients With Centronuclear Myopathies

          Withdrawn
          • Centronuclear Myopathy
            • (no location specified)
            Jul 7, 2022

            MItochondrial Myopathies Trial in Denmark, United States (Omaveloxolone capsules, 2.5 mg, omaveloxolone capsules, 5 mg,

            Completed
            • MItochondrial Myopathies
            • Omaveloxolone capsules, 2.5 mg
            • +7 more
            • Los Angeles, California
            • +8 more
            Sep 15, 2021

            Evaluation of Peripheral Neutrophils in Antisynthetase Syndrome

            Not yet recruiting
            • Antisynthetase Syndrome
              • Vandœuvre-lès-Nancy, France
                CHU Nancy
              Jan 11, 2023

              Patients With Inflammatory Myopathies Associated With a Biobank

              Not yet recruiting
              • Inflammatory Myositis
              • +2 more
                • (no location specified)
                Jul 7, 2022

                Systemic Sclerosis, Inflammatory Myopathies Trial in Strasbourg (Collection of biological samples)

                Recruiting
                • Systemic Sclerosis
                • Inflammatory Myopathies
                • Collection of biological samples
                • Strasbourg, Bas-Rhin, France
                  University Hospital of Hautepierre
                Dec 14, 2021

                Electrical Remodeling, Rheumatic Diseases, Myopathy Trial in Sao Paulo (Electrical stimulation)

                Completed
                • Electrical Remodeling
                • +2 more
                • Electrical stimulation
                • Sao Paulo, Brazil
                  Samuel K Shinjo
                Apr 29, 2021

                Idiopathic Inflammatory Myopathies, Physical Activity Trial in Sao Paulo (Physical exercises)

                Completed
                • Idiopathic Inflammatory Myopathies
                • Physical Activity
                • Physical exercises
                • Sao Paulo, Brazil
                  Samuel Katsuyuki Shinjo
                Apr 29, 2021

                Idiopathic Inflammatory Myopathies Trial in New Haven (electrical impedance myography, healthy control group)

                Completed
                • Idiopathic Inflammatory Myopathies
                • electrical impedance myography
                • healthy control group
                • New Haven, Connecticut
                  Bhaskar Roy
                Sep 2, 2021

                Mitochondrial Myopathies Trial in Nice (Personalized and mixed training program)

                Recruiting
                • Mitochondrial Myopathies
                • Personalized and mixed training program
                • Nice, Alpes Maritimes, France
                  CHU de Nice
                Jul 1, 2022