NTD beta-thalassemia PRO
Showing 1 - 25 of 5,363
ß-thalassemia, Ineffective Erythropoiesis Trial in Worldwide (PTG-300)
Completed
- β-thalassemia
- Ineffective Erythropoiesis
-
Oakland, California
- +15 more
Jul 12, 2021
Thalassemia Trial in Worldwide (Luspatercept, Placebo, Best Supportive Care (BSC))
Active, not recruiting
- Thalassemia
- Luspatercept
- +2 more
-
Los Angeles, California
- +16 more
Aug 16, 2022
Sickle Cell Disease, Sickle Cell Hemoglobin C, Sickle Beta Zero Thalassemia Trial in Chicago (PROs assessment using sickle cell
Completed
- Sickle Cell Disease
- +3 more
- PROs assessment using sickle cell disease mobile app (SCD-app)
-
Chicago, IllinoisAnn & Robert H. Lurie Children's Hospital of Chicago
Dec 17, 2020
Anemia Trial in Worldwide (biological, drug, other)
Recruiting
- Anemia
- Luspatercept
- +2 more
-
Halifax, Nova Scotia, Canada
- +11 more
Jan 3, 2023
Quality of Life in Thalassemic Patients at Assiut University
Not yet recruiting
- Thalassemia
- Abdominal ultrasound
- (no location specified)
Mar 17, 2023
Bone Denisty Change in Children With Beta Thalassemia Major
Not yet recruiting
- Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
- Dexa scan
- (no location specified)
Sep 29, 2023
Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Worldwide (CTX001)
Active, not recruiting
- Beta-Thalassemia
- +4 more
- CTX001
-
Stanford, California
- +11 more
Nov 30, 2022
Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)
Completed
- Thalassemia, Beta
- Hydroxyurea and Thalidomide
-
Karachi, Sindh, PakistanChildren's Hospital Karachi
Nov 23, 2023
Cognitive Function, Fatigue and Health Related Quality of Life
Recruiting
- Cognitive Change
- +3 more
-
Giza, EgyptAbo El-Rish Pediatric Hospital
Jul 20, 2022
A Long-term Follow-up Study in Subjects Who Received CTX001
Enrolling by invitation
- Beta-Thalassemia
- +6 more
- CTX001
-
New York, New York
- +12 more
Nov 18, 2022
Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia
Not yet recruiting
- Myelodysplastic Syndrome
- Beta Thalassemia
-
Seoul, Korea, Republic ofBristol-Myers Squibb YH
Oct 3, 2023
Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)
Completed
- Transfusion-dependent Beta-Thalassemia
-
Peshawar, Khyber Pakhtunkhwa, PakistanBlood Care Clinic
Nov 19, 2023
Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)
Recruiting
- Transfusion Dependent Beta Thalassemia
- +3 more
- EDIT-301
-
Oakland, California
- +3 more
Jan 3, 2023
Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))
Completed
- Beta Thalassemia Major
- Beta Thalassemia Intermedia
- SOTATERCEPT (ACE-011)
-
Créteil, France
- +14 more
Aug 18, 2022
Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity Trial in Tanta (L_carnitine, Sildenafil)
Recruiting
- Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity
-
Tanta, Gharbia, EgyptTanta University Hospital
Oct 14, 2022
Atrial Fibrillation in Beta-Thalassemia
Not yet recruiting
- Atrial Fibrillation
- Thalassemia
-
Ferrara, ItalyMatteo Bertini
Aug 18, 2022
Transfusion-dependent Beta-thalassemia After Gene Therapy
Recruiting
- Transfusion-dependent Beta-Thalassemia
- Gene Therapy
- Gene therapy
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Aug 6, 2023
ß-thalassemia Trial (BD211)
Not yet recruiting
- β-thalassemia
- BD211
- (no location specified)
Mar 15, 2023
Anemia Trial (Luspatercept)
Not yet recruiting
- Anemia
- Luspatercept
- (no location specified)
May 26, 2023
Thalassemia, Beta Trial in Karachi (hydroxyurea and thalidomide)
Completed
- Thalassemia, Beta
- hydroxyurea and thalidomide
-
Karachi, Sindh, PakistanChildren's Hospital Karachi
Nov 11, 2021
MDS Trial in Worldwide (Luspatercept, Epoetin Alfa)
Not yet recruiting
- Myelodysplastic Syndromes
- Luspatercept
- Epoetin Alfa
-
Concord, California
- +100 more
Jul 20, 2023
Beta Thalassaemia Trial in Milan (Safety and Efficacy assessments)
Active, not recruiting
- Beta Thalassaemia
- Safety and Efficacy assessments
-
Milan, ItalyOspedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 22, 2022