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NTD beta-thalassemia PRO

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ß-thalassemia, Ineffective Erythropoiesis Trial in Worldwide (PTG-300)

Completed
  • β-thalassemia
  • Ineffective Erythropoiesis
  • Oakland, California
  • +15 more
Jul 12, 2021

ß-thalassemia, Ineffective Erythropoiesis, Chronic Anemia Trial in Worldwide (PTG-300)

Completed
  • β-thalassemia
  • +2 more
  • Oakland, California
  • +32 more
Jul 13, 2021

Thalassemia Trial in Worldwide (Luspatercept, Placebo, Best Supportive Care (BSC))

Active, not recruiting
  • Thalassemia
  • Los Angeles, California
  • +16 more
Aug 16, 2022

Sickle Cell Disease, Sickle Cell Hemoglobin C, Sickle Beta Zero Thalassemia Trial in Chicago (PROs assessment using sickle cell

Completed
  • Sickle Cell Disease
  • +3 more
  • PROs assessment using sickle cell disease mobile app (SCD-app)
  • Chicago, Illinois
    Ann & Robert H. Lurie Children's Hospital of Chicago
Dec 17, 2020

Anemia Trial in Worldwide (biological, drug, other)

Recruiting
  • Anemia
  • Luspatercept
  • +2 more
  • Halifax, Nova Scotia, Canada
  • +11 more
Jan 3, 2023

Quality of Life in Thalassemic Patients at Assiut University

Not yet recruiting
  • Thalassemia
  • Abdominal ultrasound
  • (no location specified)
Mar 17, 2023

Bone Denisty Change in Children With Beta Thalassemia Major

Not yet recruiting
  • Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
  • Dexa scan
  • (no location specified)
Sep 29, 2023

Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Worldwide (CTX001)

Active, not recruiting
  • Beta-Thalassemia
  • +4 more
  • CTX001
  • Stanford, California
  • +11 more
Nov 30, 2022

Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)

Completed
  • Thalassemia, Beta
  • Hydroxyurea and Thalidomide
  • Karachi, Sindh, Pakistan
    Children's Hospital Karachi
Nov 23, 2023

Cognitive Function, Fatigue and Health Related Quality of Life

Recruiting
  • Cognitive Change
  • +3 more
    • Giza, Egypt
      Abo El-Rish Pediatric Hospital
    Jul 20, 2022

    A Long-term Follow-up Study in Subjects Who Received CTX001

    Enrolling by invitation
    • Beta-Thalassemia
    • +6 more
    • CTX001
    • New York, New York
    • +12 more
    Nov 18, 2022

    Beta-Thalassemia Trial in Greece, Italy (ACE-536)

    Completed
    • Beta-Thalassemia
    • Athens, Greece
    • +6 more
    May 17, 2021

    Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia

    Not yet recruiting
    • Myelodysplastic Syndrome
    • Beta Thalassemia
    • Seoul, Korea, Republic of
      Bristol-Myers Squibb YH
    Oct 3, 2023

    Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)

    Completed
    • Transfusion-dependent Beta-Thalassemia
    • Peshawar, Khyber Pakhtunkhwa, Pakistan
      Blood Care Clinic
    Nov 19, 2023

    Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

    Recruiting
    • Transfusion Dependent Beta Thalassemia
    • +3 more
    • EDIT-301
    • Oakland, California
    • +3 more
    Jan 3, 2023

    Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))

    Completed
    • Beta Thalassemia Major
    • Beta Thalassemia Intermedia
    • SOTATERCEPT (ACE-011)
    • Créteil, France
    • +14 more
    Aug 18, 2022

    Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity Trial in Tanta (L_carnitine, Sildenafil)

    Recruiting
    • Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity
    • Tanta, Gharbia, Egypt
      Tanta University Hospital
    Oct 14, 2022

    Atrial Fibrillation in Beta-Thalassemia

    Not yet recruiting
    • Atrial Fibrillation
    • Thalassemia
      • Ferrara, Italy
        Matteo Bertini
      Aug 18, 2022

      Transfusion-dependent Beta-thalassemia After Gene Therapy

      Recruiting
      • Transfusion-dependent Beta-Thalassemia
      • Gene Therapy
      • Gene therapy
      • Tianjin, Tianjin, China
        Regenerative Medicine Center
      Aug 6, 2023

      ß-thalassemia Trial (BD211)

      Not yet recruiting
      • β-thalassemia
      • BD211
      • (no location specified)
      Mar 15, 2023

      Anemia Trial (Luspatercept)

      Not yet recruiting
      • Anemia
      • Luspatercept
      • (no location specified)
      May 26, 2023

      Thalassemia, Beta Trial in Karachi (hydroxyurea and thalidomide)

      Completed
      • Thalassemia, Beta
      • hydroxyurea and thalidomide
      • Karachi, Sindh, Pakistan
        Children's Hospital Karachi
      Nov 11, 2021

      Beta-thalassemia Trial in Nanning (Luspatercept, Placebo)

      Recruiting
      • Beta-thalassemia
      • Nanning, China
      • +1 more
      Jan 13, 2023

      MDS Trial in Worldwide (Luspatercept, Epoetin Alfa)

      Not yet recruiting
      • Myelodysplastic Syndromes
      • Luspatercept
      • Epoetin Alfa
      • Concord, California
      • +100 more
      Jul 20, 2023

      Beta Thalassaemia Trial in Milan (Safety and Efficacy assessments)

      Active, not recruiting
      • Beta Thalassaemia
      • Safety and Efficacy assessments
      • Milan, Italy
        Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
      Nov 22, 2022