PhaseOut DMD
Showing 1 - 25 of 238
Duchenne Muscular Dystrophy Trial in United Kingdom, United States (Ezutromid)
Terminated
- Duchenne Muscular Dystrophy
-
Los Angeles, California
- +15 more
Dec 13, 2019
Wearable Technology to Evaluate Hyperglycemia and HRV in DMD
Not yet recruiting
- Duchenne Muscular Dystrophy
- wearable technology
-
Nashville, TennesseeVanderbilt University Medical Center
Nov 3, 2023
Hyperglycemia and HRV in DMD - Longitudinal Aim
Not yet recruiting
- Duchenne Muscular Dystrophy
- wearable technology
-
Nashville, TennesseeVanderbilt University Medical Center
Oct 16, 2023
Duchenne Muscular Dystrophy Trial (NS-050/NCNP-03, Placebo)
Not yet recruiting
- Duchenne Muscular Dystrophy
- NS-050/NCNP-03
- Placebo
- (no location specified)
Sep 19, 2023
Duchenne Muscular Dystrophy Trial (Givinostat, Placebo)
Not yet recruiting
- Duchenne Muscular Dystrophy
- Givinostat
- Placebo
- (no location specified)
Jun 27, 2023
Duchenne Muscular Dystrophy Trial in Ankara (Telerehabilitation)
Completed
- Duchenne Muscular Dystrophy
- Telerehabilitation
-
Ankara, TurkeyLokman Hekim University
Oct 26, 2023
Quality and Independence of Gait Classification Scale for DMD
Completed
- Duchenne Muscular Dystrophy
- Gait Disorders in Children
- Quality and Independence of Gait Classification Scale for Duchenne Muscular Dystrophy (QIGS-DMD)
-
Isparta, TurkeyGüllü Aydın Yağcıoğlu
Sep 29, 2022
Duchenne Muscular Dystrophy With Small Mutations
Recruiting
- Muscular Dystrophy, Duchenne
- MUSCLE MAGNETIC RESONANCE IMAGING (MRI)
-
Rome, ItalyClaudia Brogna
Apr 17, 2023
Brain Involvement in Dystrophinopathies Part 1
Recruiting
- Duchenne Muscular Dystrophy
- Becker Muscular Dystrophy
-
Copenhagen, Denmark
- +6 more
Oct 27, 2022
Peabody Developmental Motor Scaling In Period Duchenne Muscular
Completed
- Duchenne Muscular Dystrophy (DMD)
- Peabody Developmental Motor Scales-2, PDMS
-
Samsun, TurkeyOndokuz Mayıs University
Aug 6, 2023
Duchenne Muscular Dystrophy Trial (delandistrogene moxeparvovec)
Not yet recruiting
- Duchenne Muscular Dystrophy
- delandistrogene moxeparvovec
- (no location specified)
Nov 8, 2023
Duchenne Muscular Dystrophy Trial in Altindag (PAQ-C (Physical activitiy questionare for children), MoCA (Montreal Cognitive
Recruiting
- Duchenne Muscular Dystrophy
- PAQ-C (Physical activitiy questionare for children), MoCA (Montreal Cognitive Assessment), PBS (Pediatric Balance Scale), Modified Mini Mental State Examination, BMI (Body Mass Index)
-
Altındağ, Ankara, TurkeyHacettepe University
Nov 29, 2022
Duchenne Muscular Dystrophy Trial in Chengdu (JWK007 Single intravenous infusion administration)
Recruiting
- Duchenne Muscular Dystrophy
- JWK007 Single intravenous infusion administration
-
Chengdu, Sichuan, ChinaWest China Hospital, Sichuan University
Oct 29, 2023
Duchenne Muscular Dystrophy Trial in Ankara (telerehabilitation-based motor imagery training, telerehabilitation-based
Not yet recruiting
- Duchenne Muscular Dystrophy
- telerehabilitation-based motor imagery training
- telerehabilitation-based physiotheraphy training
-
Ankara, TurkeyHacettepe University
Oct 27, 2023
Cerebral Palsy, Spinal Muscular Atrophy, Spinal Cord Injuries Trial in Grand Rapids (Power Wheelchair Standing Device)
Active, not recruiting
- Cerebral Palsy
- +5 more
- Power Wheelchair Standing Device
-
Grand Rapids, MichiganGrand Valley State University
Oct 14, 2022
NSAA NON-Interventional Study Protocol
Not yet recruiting
- Duchenne Muscular Dystrophy
- Remote Administration of NSAA
- (no location specified)
Sep 19, 2023
AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Boys
Recruiting
- Duchenne Muscular Dystrophy
- AAV8 DetectCDx
-
Atlanta, GeorgiaRare Disease Research
Jan 12, 2023
Duchenne Muscular Dystrophy Trial in Columbus (rAAVrh74.MCK.GALGT2)
Active, not recruiting
- Duchenne Muscular Dystrophy
- rAAVrh74.MCK.GALGT2
-
Columbus, OhioNationwide Children's Hospital
Jul 26, 2022
Evaluation of Home Based Assessments on Participants With DMD
Recruiting
- Duchenne Muscular Dystrophy
- Wearable Device
- Duchenne Video Assessment (DVA)
-
Charlestown, MassachusettsSolid Biosciences
Dec 12, 2022
Duchenne Muscular Dystrophy, Ambulation Difficulty, Posture Disorders in Children Trial in Isparta (foot posture index, north
Recruiting
- Duchenne Muscular Dystrophy
- +3 more
- foot posture index, north star ambulation assessment, timed performance tests, 6 minute walk test
-
Isparta, TurkeyGüllü Aydın Yağcıoğlu
Jul 24, 2022
Duchenne Muscular Dystrophy Video Assessment Registry
Recruiting
- Duchenne Muscular Dystrophy
-
Plymouth, MassachusettsCasimir
Feb 1, 2023
Muscular Dystrophy, Duchenne Trial in United States (SRP-9001)
Enrolling by invitation
- Muscular Dystrophy, Duchenne
- SRP-9001
-
Palo Alto, California
- +4 more
Sep 28, 2022
Duchenne Muscular Dystrophy Trial in Worldwide (SRP-4045, SRP-4053, Placebo)
Active, not recruiting
- Duchenne Muscular Dystrophy
- SRP-4045
- +2 more
-
Phoenix, Arizona
- +74 more
Jan 17, 2023