Sanfilippo
Showing 1 - 25 of 89
Participants With Sanfilippo Syndrome Type IIIC
Not yet recruiting
- Sanfilippo Syndrome Type C
-
Bron, FranceHospices Civils De Lyon
Apr 20, 2023
Patients With Sanfilippo Disease(s) (MPS3)
Not yet recruiting
- Sanfilippo Syndrome
- MPS3
-
Fairfax, VirginiaLDRTC
Jan 20, 2023
A Natural History Study of Sanfilippo Syndrome Type D
Recruiting
- Sanfilippo Syndrome Type D
-
New York, New YorkColumbia University Irving Medical Center
Jan 11, 2023
MPS IIIA, Sanfilippo Syndrome, Sanfilippo A Trial in Australia, Spain, United States (ABO-102)
Active, not recruiting
- MPS IIIA
- +3 more
- ABO-102
-
Columbus, Ohio
- +4 more
Nov 8, 2022
A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)
Completed
- Sanfilippo Syndrome Type A
- assessment
-
Minneapolis, MinnesotaUniversity of Minnesota
May 19, 2021
Sanfilippo Syndrome A Trial (assessment)
Not yet recruiting
- Sanfilippo Syndrome A
- assessment
- (no location specified)
Jun 6, 2021
Biomarker for Sanfilippo Type A-B-C-D Disease (BioSanfilippo)
Active, not recruiting
- Mental Retardation
- Developmental Delay
-
Cairo, Egypt
- +4 more
May 12, 2021
Sanfilippo Syndrome Type A (MPS IIIA) Trial in Oakland, Chapel Hill, Ankara (SOBI003)
Completed
- Sanfilippo Syndrome Type A (MPS IIIA)
-
Oakland, California
- +2 more
Feb 2, 2022
Mucopolysaccharidosis Type IIIB
Completed
- Sanfilippo Syndrome Type B
-
Oakland, California
- +3 more
Mar 15, 2021
Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)
Active, not recruiting
- Mucopolysaccharidosis Type IIIB
- MPS III B
- AX 250
-
Oakland, California
- +7 more
Jan 16, 2023
MPS III B Trial in Worldwide (AX 250)
Not yet recruiting
- MPS III B
- AX 250
-
Oakland, California
- +4 more
Aug 8, 2022
Sanfilippo Syndrome Type A (MPS IIIA) Trial in Germany, Turkey, United States (SOBI003)
Completed
- Sanfilippo Syndrome Type A (MPS IIIA)
-
Oakland, California
- +3 more
Nov 18, 2021
Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)
Recruiting
- Adrenoleukodystrophy
- +11 more
- DUOC-01
-
Durham, North CarolinaDuke University Medical Center
Oct 24, 2022
Mucopolysaccharidosis Type IIIA Trial in Manchester (Autologous CD34+ cells transduced with a lentiviral vector containing the
Active, not recruiting
- Mucopolysaccharidosis Type IIIA
- Autologous CD34+ cells transduced with a lentiviral vector containing the human SGSH gene
-
Manchester, United KingdomManchester University NHS Foundation Trust
Jul 2, 2021
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn
Enrolling by invitation
- Acid Sphingomyelinase Deficiency
- +13 more
- Confirmatory Testing
-
Bronx, New York
- +9 more
May 9, 2022
Sanfilippo Syndrome B Trial in Paris (rAAV2/5-hNAGLU)
Completed
- Sanfilippo Syndrome B
-
Paris, Le Kremlin-Bicetre Cedex, FranceHopitaux Universitaires Paris-Sud
Nov 28, 2019
Neurobehavioral Phenotypes in MPS III
Completed
- Sanfilippo Syndrome Type A
- +2 more
-
Minneapolis, MinnesotaUniversity of Minnesota
Oct 30, 2019
MPS III B, Mucopolysaccharidosis Type IIIB Trial in Worldwide (AX 250)
Completed
- MPS III B
- Mucopolysaccharidosis Type IIIB
- AX 250
-
Oakland, California
- +6 more
Aug 4, 2020
Study of Patients With MPS IIIA Treated With ABO-102
Enrolling by invitation
- Mucopolysaccharidosis III-A
- ABO-102
-
Columbus, Ohio
- +2 more
Nov 8, 2022
Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)
Terminated
- Mucopolysaccharidosis Type 3 B
- rAAV9.CMV.hNAGLU
-
Columbus, Ohio
- +3 more
Apr 29, 2022
Study of Patients With MPS IIIB Treated With ABO-101
Terminated
- Mucopolysaccharidosis III-B
- ABO-101
-
Columbus, Ohio
- +2 more
May 25, 2022
Right Ventricle Dysfunction in Critically Ill Patients
Not yet recruiting
- Right Ventricular Dysfunction
- (no location specified)
Jul 27, 2023
Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (drug, procedure,
Completed
- Adrenoleukodystrophy
- +8 more
- Clofarabine
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Jul 10, 2019
Advanced Soft Tissue Sarcoma Trial in Italy (Standard arm: Trabectedin in monotherapy, Experimental arm: Trabectedin + Olaparib)
Recruiting
- Advanced Soft Tissue Sarcoma
- Standard arm: Trabectedin in monotherapy
- Experimental arm: Trabectedin + Olaparib
-
Bologna, BO, Italy
- +13 more
Oct 29, 2021