Sarcoglycan
Showing 1 - 11 of 11
Limb Girdle Muscular Dystrophy Trial in Columbus (SRP-9003)
Enrolling by invitation
- Limb Girdle Muscular Dystrophy
- SRP-9003
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Columbus, OhioNationwide Children's Hospital
May 17, 2023
Limb-Girdle Muscular Dystrophy, Type 2E Trial in Columbus (SRP-9003)
Active, not recruiting
- Limb-Girdle Muscular Dystrophy, Type 2E
- SRP-9003
-
Columbus, OhioNationwide Children's Hospital
Sep 28, 2022
LGMD2C Trial (ATA-200)
Not yet recruiting
- LGMD2C
- ATA-200
- (no location specified)
Aug 1, 2023
LGMD2E/R4, LGMD2D/R3, and LGMD2C/R5, = 4 Years of Age, Who Are
Recruiting
- Limb-girdle Muscular Dystrophy
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Phoenix, Arizona
- +14 more
Aug 23, 2022
Long-Term Development of Muscular Dystrophy Outcome Assessments
Not yet recruiting
- LGMD1A
- +33 more
-
Richmond, VirginiaVirginia Commonwealth University
Aug 3, 2023
Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy
Recruiting
- Limb Girdle Muscular Dystrophy
- Muscular Dystrophies
-
Irvine, California
- +10 more
Sep 13, 2021
Duchenne Muscular Dystrophy Trial in Columbus (rAAVrh74.MCK.GALGT2)
Active, not recruiting
- Duchenne Muscular Dystrophy
- rAAVrh74.MCK.GALGT2
-
Columbus, OhioNationwide Children's Hospital
Jul 26, 2022
Pilot Study of Cardiac MR in Patients With Muscular Dystrophy
Recruiting
- Muscular Dystrophies
- +3 more
-
Washington, District of ColumbiaChildren's National Health System
Mar 1, 2022
Genetics of Cardiovascular and Neuromuscular Disease
Recruiting
- Cardiomyopathy
- +2 more
- Blood draw (genetic testing)
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Chicago, IllinoisUniversity of Chicago
Aug 23, 2016
Muscular Dystrophies Trial in Columbus (rAAV1.tMCK.human-alpha-sarcoglycan- First cohort, Genetic:
Completed
- Muscular Dystrophies
- rAAV1.tMCK.human-alpha-sarcoglycan- First cohort
- Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Second cohort
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Columbus, OhioThe Research Institute at Nationwide Children's Hospital
Feb 4, 2013
Limb Girdle Muscular Dystrophy Type 2C, Gamma-sarcoglycanopathy Trial in Paris (AAV1-gamma-sarcoglycan vector injection)
Completed
- Limb Girdle Muscular Dystrophy Type 2C
- Gamma-sarcoglycanopathy
- AAV1-gamma-sarcoglycan vector injection
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Paris, FranceHôpital Pitié-Salpêtrière
Apr 28, 2011