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Severe Combined Immune Deficiency (SCID) with NK cell activity

Showing 1 - 25 of >10,000

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Severe Combined Immune Deficiency (SCID) Trial run by the National Institute of Allergy and Infectious Diseases (NIAID)

Enrolling by invitation
  • Severe Combined Immune Deficiency (SCID)
  • Bethesda, Maryland
    National Institutes of Health Clinical Center
Aug 24, 2022

Adenosine Deaminase Severe Combined Immune Deficiency Trial (A cryopreserved formulation of autologous mPB CD34+ hematopoietic

Not yet recruiting
  • Adenosine Deaminase Severe Combined Immune Deficiency
  • A cryopreserved formulation of autologous mPB CD34+ hematopoietic stem and progenitor cells transduced ex vivo with the EFS-ADA lentiviral vector encoding the human ADA enzyme
  • (no location specified)
Jun 20, 2022

Severe Combined Immunodeficiency Trial in Memphis (drug, device, other)

Recruiting
  • Severe Combined Immunodeficiency
  • Anti-thymocyte globulin (rabbit)
  • +5 more
  • Memphis, Tennessee
    St. Jude Children's Research Hospital
Oct 6, 2021

Severe Combined Immunodeficiency Trial in San Francisco (AProArt, CliniMACS® CD34 Reagent System cell sorter device, Busulfan)

Recruiting
  • Severe Combined Immunodeficiency
  • San Francisco, California
    University of California, San Francisco (UCSF) Children's Hospit
Feb 4, 2022

Severe Combined Immunodeficiency (SCID), Immunodeficiency With Predominant T-cell Defect, Unspecified, Severe Chronic

Enrolling by invitation
  • Severe Combined Immunodeficiency (SCID)
  • +8 more
  • CD3/CD19 negative allogeneic hematopoietic stem cells
  • Pittsburgh, Pennsylvania
    Children's Hospital of Pittsburgh of UPMC
Dec 6, 2021

Severe Combined Immunodeficiency Due to RAG1 Deficiency Trial in Leiden (Gene therapy)

Recruiting
  • Severe Combined Immunodeficiency Due to RAG1 Deficiency
  • Gene therapy
  • Leiden, Netherlands
    Leiden University Medical Center
Dec 3, 2021

SCID Trial in United States (Humanized anti-CD117 Monoclonal Antibody (JSP191))

Recruiting
  • SCID
  • Humanized anti-CD117 Monoclonal Antibody (JSP191)
  • Los Angeles, California
  • +7 more
Nov 16, 2021

Immune Deficiency Disorders, Severe Combined Immunodeficiency, Chronic Granulomatous Disease Trial in Saint Louis (Transplant

Recruiting
  • Immune Deficiency Disorders
  • +13 more
  • Transplant preparative regimen of alemtuzumab, fludarabine, thiotepa, and melphalan
  • Saint Louis, Missouri
    Washington University
Apr 25, 2022

Adenosine Deaminase Deficiency, Severe Combined Immunodeficiencies (SCID) Trial in London (genetic, other, drug)

Completed
  • Adenosine Deaminase Deficiency
  • Severe Combined Immunodeficiencies (SCID)
  • Infusion of autologous EFS-ADA LV CD34+ cells
  • +3 more
  • London, United Kingdom
    Great Ormond Street Hospital for Children NHS Foundation Trust
Aug 20, 2021

Pediatric Patients, Any Type of Severe Combined Immunodeficiency (SCID), Partial HLA Incompatible Allogeneic Hematopoietic Stem

Recruiting
  • Pediatric Patients
  • +2 more
  • Human T Lymphoid Progenitor (HTLP) injection
  • Paris, Ile De France, France
    Unité d'Immunologie Hématologie Rhumatologie Pédiatrique (UIHR),
Apr 13, 2021

Genetic Basis of Immunodeficiency

Recruiting
  • Severe Combined Immunodeficiency
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jan 21, 2023

    Baby Detect : Genomic Newborn Screening

    Recruiting
    • Congenital Adrenal Hyperplasia
    • +126 more
      • Liege, Wallonia, Belgium
        CRMN, Hôpital La Citadelle
      Jan 24, 2023

      Severe Combined Immunodeficiency Disease, X-linked Trial in San Francisco, Memphis, Seattle (genetic, drug, device)

      Recruiting
      • Severe Combined Immunodeficiency Disease, X-linked
      • CL20-i4-EF1α-hγc-OPT
      • +2 more
      • San Francisco, California
      • +2 more
      Jan 9, 2023

      X-linked Severe Combined Immunodeficiency (XSCID) Trial run by the National Institute of Allergy and Infectious Diseases (NIAID)

      Suspended
      • X-linked Severe Combined Immunodeficiency (XSCID)
      • Bethesda, Maryland
        National Institutes of Health Clinical Center, 9000 Rockville Pi
      Aug 24, 2022

      Investigation of ADA Enzyme Deficiency

      Enrolling by invitation
      • Adenosine Deaminase Deficiency
      • adenosine deaminase test
      • Ankara, Mamak, Turkey
        Ankara Üniversitesi Tıp Fakültesi
      Mar 18, 2022

      Enzyme Deficiency in Pulmonology Clinics (ADA)

      Active, not recruiting
      • Bronchiectasis
      • +2 more
      • adenosine deaminase enzyme deficiency test
      • Ankara, Mamak, Turkey
        Ankara University Medical Faculty
      Mar 18, 2022

      Adenosine Deaminase Enzyme Deficiency in Lymphopenia and/or

      Enrolling by invitation
      • Adenosine Deaminase Deficiency
      • ADENOSINE DEAMINASE TEST
      • Konya, Meram, Turkey
        Konya Necmettin Erbakan University
      Mar 18, 2022

      Adenosine Deaminase Enzyme Deficiency Disease in Adult Pulmonary

      Enrolling by invitation
      • Pulmonary Alveolar Proteinosis
      • adenosine deaminase test
      • Istanbul, Maltepe, Turkey
        Istanbul Yedikule Chest Diseases and Thoracic Surgery Training a
      Mar 18, 2022

      Natural History Study of SCID Disorders

      Enrolling by invitation
      • Severe Combined Immunodeficiency (SCID)
      • +5 more
        • Birmingham, Alabama
        • +43 more
        Nov 9, 2020

        Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

        Recruiting
        • Primary Immunodeficiency (PID)
        • +4 more
        • data collection
        • Pittsburgh, Pennsylvania
          UPMC Children's Hospital of Pittsburgh
        Feb 9, 2022

        Severe Combined Immunodeficiency, X-Linked Trial in London (Lentiviral vector transduced CD34+ cells)

        Recruiting
        • Severe Combined Immunodeficiency, X-Linked
        • Lentiviral vector transduced CD34+ cells
        • London, Greater London, United Kingdom
          Great Ormond Street Hospital for Children NHS Foundation Trust
        Mar 15, 2022

        Neonatal Screening of Severe Combined Immunodeficiencies

        Completed
        • Severe Combined Immunodeficiency
        • Neonatal Screening
          • Shanghai, Shanghai, China
            Children's Hospital of Fudan University
          Jan 3, 2022

          The Experience of Screening for SCID

          Recruiting
          • Severe Combined Immunodeficiency
          • SCID Screening
          • London, United Kingdom
            King's College London
          Dec 6, 2022

          Patients Treated for SCID (1968-Present)

          Enrolling by invitation
          • SCID
          • +5 more
            • Birmingham, Alabama
            • +35 more
            Nov 9, 2020

            Lymphoma Trial (Tislelizumab)

            Not yet recruiting
            • Lymphoma
            • (no location specified)
            Jul 28, 2022