Severe Combined Immune Deficiency (SCID) with NK cell activity
Showing 1 - 25 of >10,000
Severe Combined Immune Deficiency (SCID) Trial run by the National Institute of Allergy and Infectious Diseases (NIAID)
Enrolling by invitation
- Severe Combined Immune Deficiency (SCID)
- Sirolimus
- +4 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Aug 24, 2022
Adenosine Deaminase Severe Combined Immune Deficiency Trial (A cryopreserved formulation of autologous mPB CD34+ hematopoietic
Not yet recruiting
- Adenosine Deaminase Severe Combined Immune Deficiency
- A cryopreserved formulation of autologous mPB CD34+ hematopoietic stem and progenitor cells transduced ex vivo with the EFS-ADA lentiviral vector encoding the human ADA enzyme
- (no location specified)
Jun 20, 2022
Severe Combined Immunodeficiency Trial in Memphis (drug, device, other)
Recruiting
- Severe Combined Immunodeficiency
- Anti-thymocyte globulin (rabbit)
- +5 more
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Oct 6, 2021
Severe Combined Immunodeficiency Trial in San Francisco (AProArt, CliniMACS® CD34 Reagent System cell sorter device, Busulfan)
Recruiting
- Severe Combined Immunodeficiency
- AProArt
- +2 more
-
San Francisco, CaliforniaUniversity of California, San Francisco (UCSF) Children's Hospit
Feb 4, 2022
Severe Combined Immunodeficiency (SCID), Immunodeficiency With Predominant T-cell Defect, Unspecified, Severe Chronic
Enrolling by invitation
- Severe Combined Immunodeficiency (SCID)
- +8 more
- CD3/CD19 negative allogeneic hematopoietic stem cells
-
Pittsburgh, PennsylvaniaChildren's Hospital of Pittsburgh of UPMC
Dec 6, 2021
Severe Combined Immunodeficiency Due to RAG1 Deficiency Trial in Leiden (Gene therapy)
Recruiting
- Severe Combined Immunodeficiency Due to RAG1 Deficiency
- Gene therapy
-
Leiden, NetherlandsLeiden University Medical Center
Dec 3, 2021
SCID Trial in United States (Humanized anti-CD117 Monoclonal Antibody (JSP191))
Recruiting
- SCID
- Humanized anti-CD117 Monoclonal Antibody (JSP191)
-
Los Angeles, California
- +7 more
Nov 16, 2021
Immune Deficiency Disorders, Severe Combined Immunodeficiency, Chronic Granulomatous Disease Trial in Saint Louis (Transplant
Recruiting
- Immune Deficiency Disorders
- +13 more
- Transplant preparative regimen of alemtuzumab, fludarabine, thiotepa, and melphalan
-
Saint Louis, MissouriWashington University
Apr 25, 2022
Adenosine Deaminase Deficiency, Severe Combined Immunodeficiencies (SCID) Trial in London (genetic, other, drug)
Completed
- Adenosine Deaminase Deficiency
- Severe Combined Immunodeficiencies (SCID)
- Infusion of autologous EFS-ADA LV CD34+ cells
- +3 more
-
London, United KingdomGreat Ormond Street Hospital for Children NHS Foundation Trust
Aug 20, 2021
Pediatric Patients, Any Type of Severe Combined Immunodeficiency (SCID), Partial HLA Incompatible Allogeneic Hematopoietic Stem
Recruiting
- Pediatric Patients
- +2 more
- Human T Lymphoid Progenitor (HTLP) injection
-
Paris, Ile De France, FranceUnité d'Immunologie Hématologie Rhumatologie Pédiatrique (UIHR),
Apr 13, 2021
Genetic Basis of Immunodeficiency
Recruiting
- Severe Combined Immunodeficiency
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 21, 2023
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Severe Combined Immunodeficiency Disease, X-linked Trial in San Francisco, Memphis, Seattle (genetic, drug, device)
Recruiting
- Severe Combined Immunodeficiency Disease, X-linked
- CL20-i4-EF1α-hγc-OPT
- +2 more
-
San Francisco, California
- +2 more
Jan 9, 2023
X-linked Severe Combined Immunodeficiency (XSCID) Trial run by the National Institute of Allergy and Infectious Diseases (NIAID)
Suspended
- X-linked Severe Combined Immunodeficiency (XSCID)
- Palifermin
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Aug 24, 2022
Investigation of ADA Enzyme Deficiency
Enrolling by invitation
- Adenosine Deaminase Deficiency
- adenosine deaminase test
-
Ankara, Mamak, TurkeyAnkara Üniversitesi Tıp Fakültesi
Mar 18, 2022
Enzyme Deficiency in Pulmonology Clinics (ADA)
Active, not recruiting
- Bronchiectasis
- +2 more
- adenosine deaminase enzyme deficiency test
-
Ankara, Mamak, TurkeyAnkara University Medical Faculty
Mar 18, 2022
Adenosine Deaminase Enzyme Deficiency in Lymphopenia and/or
Enrolling by invitation
- Adenosine Deaminase Deficiency
- ADENOSINE DEAMINASE TEST
-
Konya, Meram, TurkeyKonya Necmettin Erbakan University
Mar 18, 2022
Adenosine Deaminase Enzyme Deficiency Disease in Adult Pulmonary
Enrolling by invitation
- Pulmonary Alveolar Proteinosis
- adenosine deaminase test
-
Istanbul, Maltepe, TurkeyIstanbul Yedikule Chest Diseases and Thoracic Surgery Training a
Mar 18, 2022
Natural History Study of SCID Disorders
Enrolling by invitation
- Severe Combined Immunodeficiency (SCID)
- +5 more
-
Birmingham, Alabama
- +43 more
Nov 9, 2020
Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Recruiting
- Primary Immunodeficiency (PID)
- +4 more
- data collection
-
Pittsburgh, PennsylvaniaUPMC Children's Hospital of Pittsburgh
Feb 9, 2022
Severe Combined Immunodeficiency, X-Linked Trial in London (Lentiviral vector transduced CD34+ cells)
Recruiting
- Severe Combined Immunodeficiency, X-Linked
- Lentiviral vector transduced CD34+ cells
-
London, Greater London, United KingdomGreat Ormond Street Hospital for Children NHS Foundation Trust
Mar 15, 2022
Neonatal Screening of Severe Combined Immunodeficiencies
Completed
- Severe Combined Immunodeficiency
- Neonatal Screening
-
Shanghai, Shanghai, ChinaChildren's Hospital of Fudan University
Jan 3, 2022
The Experience of Screening for SCID
Recruiting
- Severe Combined Immunodeficiency
- SCID Screening
-
London, United KingdomKing's College London
Dec 6, 2022
Patients Treated for SCID (1968-Present)
Enrolling by invitation
- SCID
- +5 more
-
Birmingham, Alabama
- +35 more
Nov 9, 2020