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Severe congenital protein C deficiency

Showing 1 - 25 of >10,000

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Protein C Deficiency Trial in United States (Protein C Concentrate (Human) Vapor Heated)

Completed
  • Protein C Deficiency
  • Protein C Concentrate (Human) Vapor Heated
  • Los Angeles, California
  • +11 more
May 3, 2021

Data in Severe Congenital Protein C Deficiency Who Were Treated

Completed
  • Protein C Deficiency
  • Protein C Concentrate (Human) Vapor Heated
  • Los Angeles, California
  • +9 more
Apr 7, 2021

Congenital Protein C Deficiency Trial in Kashihara, Chiba, Saitama (TAK-662)

Active, not recruiting
  • Congenital Protein C Deficiency
  • Kashihara, Nara, Japan
  • +3 more
Apr 7, 2022

Crohn's Disease, Glycogen Metabolism, Inflammatory Bowel Disease (IBD) Trial run by the National Institute of Allergy and

Recruiting
  • Crohn's Disease
  • +2 more
  • Bethesda, Maryland
    National Institutes of Health Clinical Center
Aug 20, 2022

IBD, Colitis, Ulcerative, Magnesium Deficiency Trial in Aarhus N (Magnesium acetate mixture (30 mmol/ml), High-protein diet (2

Recruiting
  • Inflammatory Bowel Diseases
  • +4 more
  • Magnesium acetate mixture (30 mmol/ml)
  • High-protein diet (2 g/kg/day)
  • Aarhus N, Denmark
    Aarhus University Hospital
Feb 27, 2022

Baby Detect : Genomic Newborn Screening

Recruiting
  • Congenital Adrenal Hyperplasia
  • +126 more
    • Liege, Wallonia, Belgium
      CRMN, Hôpital La Citadelle
    Jan 24, 2023

    Hemophilia A, Hemophilia B Trial (SerpinPC)

    Not yet recruiting
    • Hemophilia A
    • Hemophilia B
    • (no location specified)
    Mar 16, 2023

    Energy Supply; Deficiency, Severe, Energy Supply; Deficiency, Stress, Physiological Trial (Energy Deficit)

    Not yet recruiting
    • Energy Supply; Deficiency, Severe
    • +2 more
    • Energy Deficit
    • (no location specified)
    Feb 28, 2022

    Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

    Recruiting
    • Mucopolysaccharidosis Disorders
    • +28 more
    • Stem Cell Transplantation
    • +7 more
    • Minneapolis, Minnesota
      Masonic Cancer Center, University of Minnesota
    Nov 1, 2022

    Clinical Associates of Iron Deficiency in Atrial Fibrillation

    Recruiting
    • Iron-deficiency
    • Atrial Fibrillation
    • Ferritin, iron and iron binding capacity, high sensitive C-reactive protein (CRP) measurement
    • Istanbul, Turkey
      Koc University
    Mar 11, 2022

    Hypovitaminosis D and "Metabolic" Inflammatory Status in Obesity

    Completed
    • Hypovitaminosis D
    • Obesity
    • Vitamin D Plasma Level
    • +5 more
    • Trieste, Italy
      Silvia Palmisano
    Nov 3, 2023

    Artemis (DCLRE1C ) Deficient Severe Combined Immunodeficiency Trial in Paris (ARTEGENE drug product)

    Not yet recruiting
    • Artemis (DCLRE1C ) Deficient Severe Combined Immunodeficiency
    • ARTEGENE drug product
    • Paris, France
      Department of Pediatric Immunology, Hematology and Rheumatology
    Sep 26, 2022

    Epilepsy, GLUT1DS1, Glut1 Deficiency Syndrome 1, Autosomal Recessive Trial in Dallas (Triheptanoin)

    Active, not recruiting
    • Epilepsy
    • +6 more
    • Dallas, Texas
      UT Southwestern Medical Center
    Feb 1, 2022

    Critical Illness, Energy Supply; Deficiency, Severe, Protein Deficiency Trial in Geneva (GLUCOSAFE 2, Local protocol control

    Not yet recruiting
    • Critical Illness
    • +4 more
    • GLUCOSAFE 2
    • +2 more
    • Geneva, Switzerland
      Service of Intensive Care, Geneva University Hospital,
    Jan 12, 2022

    Leber Congenital Amaurosis 10, Inherited Retinal Dystrophies, Eye Diseases, Hereditary Trial in United States (EDIT-101)

    Active, not recruiting
    • Leber Congenital Amaurosis 10
    • +6 more
    • Miami, Florida
    • +4 more
    Dec 2, 2022

    Severe Congenital Neutropenia, GATA2 Deficiency Trial in Moscow (conditioning with TLI)

    Not yet recruiting
    • Severe Congenital Neutropenia
    • GATA2 Deficiency
    • conditioning with TLI
    • Moscow, Russian Federation
      HSCT department
    Apr 9, 2021

    Ceprotin Treatment Registry

    Completed
    • Protein C Deficiency
    • Protein C Concentrate (Human)
    • Phoenix, Arizona
    • +27 more
    Mar 15, 2021

    Ischemic Stroke Trial (3K3A-APC, Placebo)

    Not yet recruiting
    • Ischemic Stroke
    • 3K3A-APC
    • Placebo
    • (no location specified)
    Jul 29, 2022

    Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency, Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2),

    No longer available
    • Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency
    • +7 more
    • Pittsburgh, Pennsylvania
      University of Pittsburgh Division of Medical Genetics, Children'
    Dec 8, 2021

    Evaluation of Risk Factors and Outcome of Thrombosis in Children

    Not yet recruiting
    • Thrombosis in Children
    • complete blood count
    • Sohag, Egypt
      Sohag University hospitals
    Apr 30, 2023

    COVID-19 Vaccine Trial in Ciudad Autónoma de Buenos Aires (ARVAC-CG vaccine (recombinant protein vaccine against SARS-CoV-2))

    Active, not recruiting
    • COVID-19 Vaccine
    • ARVAC-CG vaccine (recombinant protein vaccine against SARS-CoV-2)
    • Ciudad Autónoma de Buenos Aires, Argentina
      Unidad de Investigación Clínica Farmacocinética FP Clinical Phar
    Dec 21, 2022

    Human Immunodeficiency Virus Trial in Boston (Ad26.Mos4.HIV, MVA-Mosaic, Clade C gp140 + Mosaic gp140)

    Completed
    • Human Immunodeficiency Virus
    • Ad26.Mos4.HIV
    • +3 more
    • Boston, Massachusetts
      Beth Israel Deaconess Medical Center
    Feb 7, 2022

    Congenital Afibrinogenemia, Hypofibrinogenemia Trial in Worldwide (FIB Grifols)

    Suspended
    • Congenital Afibrinogenemia
    • Hypofibrinogenemia
    • FIB Grifols
    • New Hyde Park, New York
    • +9 more
    May 11, 2021

    Reference Ranges and Optimal Cut-offs for Sucrose Challenge Test

    Completed
    • Congenital Sucrase-Isomaltase Deficiency
    • Sucrose Hydrogen Methane Breath Test
    • Culver City, California
      Science 37-Recruiting Nationally
    May 17, 2022

    GLUT1DS1, Epilepsy, Glut1 Deficiency Syndrome 1, Autosomal Recessive Trial in Dallas (Triheptanoin)

    Active, not recruiting
    • GLUT1DS1
    • +6 more
    • Dallas, Texas
      University of Texas Southwestern Medical Center
    Jul 30, 2021