Severe congenital protein C deficiency
Showing 1 - 25 of >10,000
Protein C Deficiency Trial in United States (Protein C Concentrate (Human) Vapor Heated)
Completed
- Protein C Deficiency
- Protein C Concentrate (Human) Vapor Heated
-
Los Angeles, California
- +11 more
May 3, 2021
Data in Severe Congenital Protein C Deficiency Who Were Treated
Completed
- Protein C Deficiency
- Protein C Concentrate (Human) Vapor Heated
-
Los Angeles, California
- +9 more
Apr 7, 2021
Congenital Protein C Deficiency Trial in Kashihara, Chiba, Saitama (TAK-662)
Active, not recruiting
- Congenital Protein C Deficiency
-
Kashihara, Nara, Japan
- +3 more
Apr 7, 2022
Crohn's Disease, Glycogen Metabolism, Inflammatory Bowel Disease (IBD) Trial run by the National Institute of Allergy and
Recruiting
- Crohn's Disease
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Aug 20, 2022
IBD, Colitis, Ulcerative, Magnesium Deficiency Trial in Aarhus N (Magnesium acetate mixture (30 mmol/ml), High-protein diet (2
Recruiting
- Inflammatory Bowel Diseases
- +4 more
- Magnesium acetate mixture (30 mmol/ml)
- High-protein diet (2 g/kg/day)
-
Aarhus N, DenmarkAarhus University Hospital
Feb 27, 2022
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Energy Supply; Deficiency, Severe, Energy Supply; Deficiency, Stress, Physiological Trial (Energy Deficit)
Not yet recruiting
- Energy Supply; Deficiency, Severe
- +2 more
- Energy Deficit
- (no location specified)
Feb 28, 2022
Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD
Recruiting
- Mucopolysaccharidosis Disorders
- +28 more
- Stem Cell Transplantation
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Nov 1, 2022
Clinical Associates of Iron Deficiency in Atrial Fibrillation
Recruiting
- Iron-deficiency
- Atrial Fibrillation
- Ferritin, iron and iron binding capacity, high sensitive C-reactive protein (CRP) measurement
-
Istanbul, TurkeyKoc University
Mar 11, 2022
Hypovitaminosis D and "Metabolic" Inflammatory Status in Obesity
Completed
- Hypovitaminosis D
- Obesity
- Vitamin D Plasma Level
- +5 more
-
Trieste, ItalySilvia Palmisano
Nov 3, 2023
Artemis (DCLRE1C ) Deficient Severe Combined Immunodeficiency Trial in Paris (ARTEGENE drug product)
Not yet recruiting
- Artemis (DCLRE1C ) Deficient Severe Combined Immunodeficiency
- ARTEGENE drug product
-
Paris, FranceDepartment of Pediatric Immunology, Hematology and Rheumatology
Sep 26, 2022
Epilepsy, GLUT1DS1, Glut1 Deficiency Syndrome 1, Autosomal Recessive Trial in Dallas (Triheptanoin)
Active, not recruiting
- Epilepsy
- +6 more
-
Dallas, TexasUT Southwestern Medical Center
Feb 1, 2022
Critical Illness, Energy Supply; Deficiency, Severe, Protein Deficiency Trial in Geneva (GLUCOSAFE 2, Local protocol control
Not yet recruiting
- Critical Illness
- +4 more
- GLUCOSAFE 2
- +2 more
-
Geneva, SwitzerlandService of Intensive Care, Geneva University Hospital,
Jan 12, 2022
Leber Congenital Amaurosis 10, Inherited Retinal Dystrophies, Eye Diseases, Hereditary Trial in United States (EDIT-101)
Active, not recruiting
- Leber Congenital Amaurosis 10
- +6 more
-
Miami, Florida
- +4 more
Dec 2, 2022
Severe Congenital Neutropenia, GATA2 Deficiency Trial in Moscow (conditioning with TLI)
Not yet recruiting
- Severe Congenital Neutropenia
- GATA2 Deficiency
- conditioning with TLI
-
Moscow, Russian FederationHSCT department
Apr 9, 2021
Ceprotin Treatment Registry
Completed
- Protein C Deficiency
- Protein C Concentrate (Human)
-
Phoenix, Arizona
- +27 more
Mar 15, 2021
Ischemic Stroke Trial (3K3A-APC, Placebo)
Not yet recruiting
- Ischemic Stroke
- 3K3A-APC
- Placebo
- (no location specified)
Jul 29, 2022
Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency, Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2),
No longer available
- Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency
- +7 more
-
Pittsburgh, PennsylvaniaUniversity of Pittsburgh Division of Medical Genetics, Children'
Dec 8, 2021
Evaluation of Risk Factors and Outcome of Thrombosis in Children
Not yet recruiting
- Thrombosis in Children
- complete blood count
-
Sohag, EgyptSohag University hospitals
Apr 30, 2023
COVID-19 Vaccine Trial in Ciudad Autónoma de Buenos Aires (ARVAC-CG vaccine (recombinant protein vaccine against SARS-CoV-2))
Active, not recruiting
- COVID-19 Vaccine
- ARVAC-CG vaccine (recombinant protein vaccine against SARS-CoV-2)
-
Ciudad Autónoma de Buenos Aires, ArgentinaUnidad de Investigación Clínica Farmacocinética FP Clinical Phar
Dec 21, 2022
Human Immunodeficiency Virus Trial in Boston (Ad26.Mos4.HIV, MVA-Mosaic, Clade C gp140 + Mosaic gp140)
Completed
- Human Immunodeficiency Virus
- Ad26.Mos4.HIV
- +3 more
-
Boston, MassachusettsBeth Israel Deaconess Medical Center
Feb 7, 2022
Congenital Afibrinogenemia, Hypofibrinogenemia Trial in Worldwide (FIB Grifols)
Suspended
- Congenital Afibrinogenemia
- Hypofibrinogenemia
- FIB Grifols
-
New Hyde Park, New York
- +9 more
May 11, 2021
Reference Ranges and Optimal Cut-offs for Sucrose Challenge Test
Completed
- Congenital Sucrase-Isomaltase Deficiency
- Sucrose Hydrogen Methane Breath Test
-
Culver City, CaliforniaScience 37-Recruiting Nationally
May 17, 2022
GLUT1DS1, Epilepsy, Glut1 Deficiency Syndrome 1, Autosomal Recessive Trial in Dallas (Triheptanoin)
Active, not recruiting
- GLUT1DS1
- +6 more
-
Dallas, TexasUniversity of Texas Southwestern Medical Center
Jul 30, 2021