Shwachman-Diamond Syndrome
Showing 1 - 25 of >10,000
Shwachman-Diamond Syndrome, Shwachman-Diamond Syndrome-Like Trial in Aurora, Boston, Cincinnati
Recruiting
- Shwachman-Diamond Syndrome
- Shwachman-Diamond Syndrome-Like
-
Aurora, Colorado
- +3 more
Sep 25, 2023
Cancer in Inherited Bone Marrow Failure Syndromes
Recruiting
- Diamond Blackfan Anemia
- +4 more
-
Bethesda, Maryland
- +1 more
Jan 24, 2023
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia
Active, not recruiting
- Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
- +36 more
- Cyclophosphamide
- +4 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Jan 23, 2023
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Bone Marrow Failure Syndrome, Congenital Amegakaryocytic Thrombocytopenia, Congenital Pure Red Cell Aplasia Trial in United
Recruiting
- Bone Marrow Failure Syndrome
- +6 more
- Treosulfan
- +7 more
-
Los Angeles, California
- +23 more
Aug 15, 2022
Bone Marrow Failure Syndrome, Severe Aplastic Anemia, Severe Congenital Neutropenia Trial in New York (CD34 Stem Cell Selection
Active, not recruiting
- Bone Marrow Failure Syndrome
- +15 more
- CD34 Stem Cell Selection Therapy
-
New York, New YorkMorgan Stanley Children's Hospital, New York-Presbyterian, Colum
Jun 17, 2020
Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)
Completed
- Hurler Syndrome
- +14 more
-
Atlanta, GeorgiaChildren's Healthcare of Atlanta
Dec 20, 2019
Familial Investigations of Childhood Cancer Predisposition
Recruiting
- Acute Leukemia
- +45 more
-
Memphis, TennesseeSt. Jude Children's Research Hospital
May 11, 2022
Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human
Completed
- Mucopolysaccharidosis I
- +15 more
- Human Placental Derived Stem Cell
-
Denver, Colorado
- +2 more
Oct 24, 2022
Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,
Recruiting
- Bone Marrow Failure Syndrome
- +15 more
- Thiotepa--single daily dose
- Thiotepa--escalated dose
-
Gainesville, FloridaUF Health Shands Children's Hospital
Jul 8, 2021
Accelerated Phase Chronic Myelogenous Leukemia, Adult Acute Lymphoblastic Leukemia in Remission, Adult Acute Myeloid Leukemia in
Completed
- Accelerated Phase Chronic Myelogenous Leukemia
- +77 more
- fludarabine phosphate
- +8 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Sep 16, 2019
Frail Elderly Syndrome, Chronic Disease Trial in Calgary, Langley, Vancouver (Advance care planning tools)
Completed
- Frail Elderly Syndrome
- Chronic Disease
- Advance care planning tools
-
Calgary, Alberta, Canada
- +3 more
Jan 17, 2022
Hepatorenal Syndrome Trial in Canada, United States (Terlipressin, Placebo)
Steroid-refractory Diamond-Blackfan Anemia (DBA) Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Bitopertin)
Not yet recruiting
- Steroid-refractory Diamond-Blackfan Anemia (DBA)
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Apr 28, 2023
Metabolic Disorders, Hematologic, Immune, or Bone Marrow Disorders, Hemoglobinopathies Trial in Canada, United States (Treatment
Recruiting
- Metabolic Disorders
- +3 more
- Treatment Plan 1: Stratum 1
- +3 more
-
Phoenix, Arizona
- +19 more
Oct 12, 2021
Craniopharyngioma, Hypothalamic Obesity, Metabolic Syndrome Trial in Vancouver (Hypothalamic Deep Brain Stimulation)
Withdrawn
- Craniopharyngioma
- +2 more
- Hypothalamic Deep Brain Stimulation
-
Vancouver, British Columbia, CanadaLeslie and Gordon Diamond Health Center
Oct 29, 2020
DIAMOND AF Post-Approval Study
Recruiting
- Paroxysmal Atrial Fibrillation
- DiamondTemp™ Ablation System
-
Winter Park, Florida
- +1 more
Jan 19, 2023
Persistent Atrial Fibrillation, Atrial Fibrillation Trial in Worldwide (Radiofrequency Ablation)
Recruiting
- Persistent Atrial Fibrillation
- Atrial Fibrillation
- Radiofrequency Ablation
-
Birmingham, Alabama
- +28 more
Jan 17, 2023
Abrasion, Dental, Class I Dental Caries Trial (Bioactive Glass Air Abrasion Particles., Diamond Stone.)
Not yet recruiting
- Abrasion, Dental
- Class I Dental Caries
- Bioactive Glass Air Abrasion Particles.
- Diamond Stone.
- (no location specified)
Oct 24, 2023
Non-Neoplastic Hematologic and Lymphocytic Disorder Trial in United States (procedure, biological, drug, other, radiation)
Completed
- Non-Neoplastic Hematologic and Lymphocytic Disorder
- Allogeneic Bone Marrow Transplantation
- +11 more
-
Aurora, Colorado
- +5 more
Jul 21, 2021
Sars-CoV2 Trial in Paris (blood sample)
Completed
- Sars-CoV2
- blood sample
-
Paris, FranceHopital Pitié Salpetrière
Jul 5, 2022
Angina, Stable Trial in Denmark, Sweden (CADScor®System)
Recruiting
- Angina, Stable
- CADScor®System
-
Copenhagen S, Denmark
- +5 more
Mar 1, 2022
Diamond Blackfan Anemia Trial in Manhasset (Sotatercept, Sotatercept with prednisone boost)
Terminated
- Diamond Blackfan Anemia
- Sotatercept
- Sotatercept with prednisone boost
-
Manhasset, New YorkNorth Shore- LIJ campus of The Feinstein Institute for Medical R
Nov 22, 2021
Anoplasty for Post Hemorroidectomy Anal Stenosis : Diamond
Not yet recruiting
- Anoplasty in Treatment of Post Hemorroidectomy Anal Stenosis
- anoplasty in treatment of post hemorroidectomy anal stenosis
-
Assiut, EgyptAssiut university
May 20, 2022