Sickle Beta Thalassemia
Showing 26 - 50 of 4,085
Bone Denisty Change in Children With Beta Thalassemia Major
Not yet recruiting
- Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
- Dexa scan
- (no location specified)
Sep 29, 2023
Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)
Completed
- Thalassemia, Beta
- Hydroxyurea and Thalidomide
-
Karachi, Sindh, PakistanChildren's Hospital Karachi
Nov 23, 2023
Sickle Cell Disease, Sickle Cell-Beta0-Thalassemia Trial (Isoquercetin)
Withdrawn
- Sickle Cell Disease
- Sickle Cell-Beta0-Thalassemia
- (no location specified)
Jan 7, 2021
Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)
Completed
- Transfusion-dependent Beta-Thalassemia
-
Peshawar, Khyber Pakhtunkhwa, PakistanBlood Care Clinic
Nov 19, 2023
Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia
Not yet recruiting
- Myelodysplastic Syndrome
- Beta Thalassemia
-
Seoul, Korea, Republic ofBristol-Myers Squibb YH
Oct 3, 2023
Transfusion-dependent Beta-thalassemia After Gene Therapy
Recruiting
- Transfusion-dependent Beta-Thalassemia
- Gene Therapy
- Gene therapy
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Aug 6, 2023
Sickle Cell Disease, Sickle Cell Hemoglobin C, Sickle Beta Zero Thalassemia Trial in Chicago (PROs assessment using sickle cell
Completed
- Sickle Cell Disease
- +3 more
- PROs assessment using sickle cell disease mobile app (SCD-app)
-
Chicago, IllinoisAnn & Robert H. Lurie Children's Hospital of Chicago
Dec 17, 2020
Cognitive Function, Fatigue and Health Related Quality of Life
Recruiting
- Cognitive Change
- +3 more
-
Giza, EgyptAbo El-Rish Pediatric Hospital
Jul 20, 2022
ß-thalassemia Trial (BD211)
Not yet recruiting
- β-thalassemia
- BD211
- (no location specified)
Mar 15, 2023
Atrial Fibrillation in Beta-Thalassemia
Not yet recruiting
- Atrial Fibrillation
- Thalassemia
-
Ferrara, ItalyMatteo Bertini
Aug 18, 2022
Beta-Thalassemia Trial (CS-101 injection)
Not yet recruiting
- Beta-Thalassemia
- CS-101 injection
- (no location specified)
Sep 27, 2023
Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)
Recruiting
- Transfusion Dependent Beta Thalassemia
- +3 more
- EDIT-301
-
Oakland, California
- +3 more
Jan 3, 2023
Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity Trial in Tanta (L_carnitine, Sildenafil)
Recruiting
- Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity
-
Tanta, Gharbia, EgyptTanta University Hospital
Oct 14, 2022
Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)
Not yet recruiting
- Thalassemia, Beta
- Thalassemia Major
- VGB-Ex01
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Sep 11, 2023
Beta-Thalassemia Trial in Nanning (CS-101)
Recruiting
- Beta-Thalassemia
- CS-101
-
Nanning, ChinaThe First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023
Anemia Trial (Luspatercept)
Not yet recruiting
- Anemia
- Luspatercept
- (no location specified)
May 26, 2023
Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)
Not yet recruiting
- Transfusion-dependent Beta-Thalassemia
- KL003 cell injection Drug Product
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
May 8, 2023
Beta Thalassaemia Trial in Milan (Safety and Efficacy assessments)
Active, not recruiting
- Beta Thalassaemia
- Safety and Efficacy assessments
-
Milan, ItalyOspedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 22, 2022
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia
Active, not recruiting
- Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
- +36 more
- Cyclophosphamide
- +4 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Jan 23, 2023
"Iron Overload and Endocrinological Diseases"
Recruiting
- Iron Overload
- +4 more
-
Modena, ItalyUnit of Endocrinology of Azienza Ospedaliero-Universitaria di Mo
Nov 13, 2023
Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))
Completed
- Beta Thalassemia Major
- Beta Thalassemia Intermedia
- SOTATERCEPT (ACE-011)
-
Créteil, France
- +14 more
Aug 18, 2022
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen University General Hospital
May 8, 2023