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Sickle Beta Thalassemia

Showing 26 - 50 of 4,085

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Bone Denisty Change in Children With Beta Thalassemia Major

Not yet recruiting
  • Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
  • Dexa scan
  • (no location specified)
Sep 29, 2023

Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)

Completed
  • Thalassemia, Beta
  • Hydroxyurea and Thalidomide
  • Karachi, Sindh, Pakistan
    Children's Hospital Karachi
Nov 23, 2023

Sickle Cell Disease, Sickle Cell-Beta0-Thalassemia Trial (Isoquercetin)

Withdrawn
  • Sickle Cell Disease
  • Sickle Cell-Beta0-Thalassemia
  • (no location specified)
Jan 7, 2021

Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)

Completed
  • Transfusion-dependent Beta-Thalassemia
  • Peshawar, Khyber Pakhtunkhwa, Pakistan
    Blood Care Clinic
Nov 19, 2023

Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia

Not yet recruiting
  • Myelodysplastic Syndrome
  • Beta Thalassemia
  • Seoul, Korea, Republic of
    Bristol-Myers Squibb YH
Oct 3, 2023

Transfusion-dependent Beta-thalassemia After Gene Therapy

Recruiting
  • Transfusion-dependent Beta-Thalassemia
  • Gene Therapy
  • Gene therapy
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Aug 6, 2023

Thalassemia Major Trial (n-acetylcystine)

Not yet recruiting
  • Thalassemia Major
  • (no location specified)
Mar 9, 2023

Sickle Cell Disease, Sickle Cell Hemoglobin C, Sickle Beta Zero Thalassemia Trial in Chicago (PROs assessment using sickle cell

Completed
  • Sickle Cell Disease
  • +3 more
  • PROs assessment using sickle cell disease mobile app (SCD-app)
  • Chicago, Illinois
    Ann & Robert H. Lurie Children's Hospital of Chicago
Dec 17, 2020

Cognitive Function, Fatigue and Health Related Quality of Life

Recruiting
  • Cognitive Change
  • +3 more
    • Giza, Egypt
      Abo El-Rish Pediatric Hospital
    Jul 20, 2022

    ß-thalassemia Trial (BD211)

    Not yet recruiting
    • β-thalassemia
    • BD211
    • (no location specified)
    Mar 15, 2023

    Atrial Fibrillation in Beta-Thalassemia

    Not yet recruiting
    • Atrial Fibrillation
    • Thalassemia
      • Ferrara, Italy
        Matteo Bertini
      Aug 18, 2022

      Beta-Thalassemia Trial (CS-101 injection)

      Not yet recruiting
      • Beta-Thalassemia
      • CS-101 injection
      • (no location specified)
      Sep 27, 2023

      Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

      Recruiting
      • Transfusion Dependent Beta Thalassemia
      • +3 more
      • EDIT-301
      • Oakland, California
      • +3 more
      Jan 3, 2023

      Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity Trial in Tanta (L_carnitine, Sildenafil)

      Recruiting
      • Beta Thalassemia With Increased Tricuspid Regurgitant Jet Velocity
      • Tanta, Gharbia, Egypt
        Tanta University Hospital
      Oct 14, 2022

      Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

      Not yet recruiting
      • Thalassemia, Beta
      • Thalassemia Major
      • VGB-Ex01
      • Tianjin, Tianjin, China
        Regenerative Medicine Center
      Sep 11, 2023

      Beta-thalassemia Trial in Nanning (Luspatercept, Placebo)

      Recruiting
      • Beta-thalassemia
      • Nanning, China
      • +1 more
      Jan 13, 2023

      Beta-Thalassemia Trial in Nanning (CS-101)

      Recruiting
      • Beta-Thalassemia
      • CS-101
      • Nanning, China
        The First Affiliated Hospital of Guangxi Medical University
      Sep 9, 2023

      Anemia Trial (Luspatercept)

      Not yet recruiting
      • Anemia
      • Luspatercept
      • (no location specified)
      May 26, 2023

      Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)

      Not yet recruiting
      • Transfusion-dependent Beta-Thalassemia
      • KL003 cell injection Drug Product
      • Tianjin, Tianjin, China
        Regenerative Medicine Center
      May 8, 2023

      Beta Thalassaemia Trial in Milan (Safety and Efficacy assessments)

      Active, not recruiting
      • Beta Thalassaemia
      • Safety and Efficacy assessments
      • Milan, Italy
        Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
      Nov 22, 2022

      Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia

      Active, not recruiting
      • Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
      • +36 more
      • Buffalo, New York
        Roswell Park Cancer Institute
      Jan 23, 2023

      "Iron Overload and Endocrinological Diseases"

      Recruiting
      • Iron Overload
      • +4 more
        • Modena, Italy
          Unit of Endocrinology of Azienza Ospedaliero-Universitaria di Mo
        Nov 13, 2023

        Beta Thalassemia Major Anemia Trial (SP-420)

        Not yet recruiting
        • Beta Thalassemia Major Anemia
        • (no location specified)
        Jan 20, 2023

        Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))

        Completed
        • Beta Thalassemia Major
        • Beta Thalassemia Intermedia
        • SOTATERCEPT (ACE-011)
        • Créteil, France
        • +14 more
        Aug 18, 2022

        ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

        Recruiting
        • β-thalassemia
        • β-globin restored autologous hematopoietic stem cells
        • Shenzhen, Guangdong, China
          Shenzhen University General Hospital
        May 8, 2023