Spinal Muscular Atrophy, Motor Function Measure,Nusinersen
Showing 1 - 25 of >10,000
Spinal Muscular Atrophy Trial in Reims (Monthly assessments of functional motor abilities by a trained therapist, Nusinersen)
Recruiting
- Spinal Muscular Atrophy
- Monthly assessments of functional motor abilities by a trained therapist
- Nusinersen
-
Reims, FranceDamien JOLLY
Mar 16, 2022
Muscular Atrophy, Spinal Trial (No Intervention)
Not yet recruiting
- Muscular Atrophy, Spinal
- No Intervention
- (no location specified)
Mar 16, 2023
Motor Function and Activity of Daily Life in Spinal Muscular
Not yet recruiting
- Spinal Muscular Atrophy
-
Taipei, TaiwanNational Taiwan University Hospital
Jul 5, 2023
SMN Circular RNAs as Potential Biomarkers for Therapeutic
Recruiting
- Spinal Muscular Atrophy
-
Rome, Italy/rome, Italyethics committee of IRCCS Fondazione Policlinico Gemelli
Mar 10, 2023
Muscular Atrophy, Spinal Trial in Worldwide (Nusinersen)
Enrolling by invitation
- Muscular Atrophy, Spinal
-
Sacramento, California
- +27 more
Jan 25, 2023
Ultrasound-assisted or Landmark-based Intrathecal Administration
Not yet recruiting
- Anesthesia, Spinal
- +3 more
- Interlaminar ultrasound-assisted intrathecal administration of nusinersen
- Landmark-based intrathecal administration of nusinersen
-
Roma, RM, ItalyFondazione Policlinico Gemelli
Dec 12, 2022
Effect of Nusinersen on Adults With Spinal Muscular Atrophy
Active, not recruiting
- Adult Spinal Muscular Atrophy
-
Great Neck, New YorkNorthwell Health Neuroscience
Nov 18, 2021
Spinal Muscular Atrophy, Spinal Muscular Atrophy Type 3, Spinal Muscular Atrophy Type 2 Trial in United States (Apitegromab,
Recruiting
- Spinal Muscular Atrophy
- +9 more
- Apitegromab
- Placebo
-
Phoenix, Arizona
- +9 more
Jul 11, 2022
Spinal Muscular Atrophy Trial in France (Spinraza intrathecal injection)
Recruiting
- Spinal Muscular Atrophy
- Spinraza intrathecal injection
-
Lyon, Auvergne Rhone Alpes, France
- +6 more
Jul 1, 2022
Hepatic Function in Spinal and Bulbar Muscular Atrophy
Completed
- Spinal and Bulbar Muscular Atrophy (SBMA)
- Motor Neuron Disease
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Aug 17, 2022
Clinical, Molecular and Imaging Biomarkers in Spinal and Bulbar
Recruiting
- Spinal and Bulbar Muscular Atrophy
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 27, 2023
Spinal Muscular Atrophy Type 3, Spinal Muscular Atrophy Type 4 Trial in Pittsburgh (Spinal Cord Stimulator (octopolar Medtronic
Recruiting
- Spinal Muscular Atrophy Type 3
- Spinal Muscular Atrophy Type 4
- Spinal Cord Stimulator (octopolar Medtronic Vectris Leads)
-
Pittsburgh, PennsylvaniaUniversity of Pittsburgh
Jul 11, 2022
MFM-32 in SMA Patients Treated With Nusinersen
Recruiting
- Spinal Muscular Atrophy
-
Angers, France
- +9 more
Dec 8, 2021
Spinal Muscular Atrophy Trial (OAV101)
Recruiting
- Spinal Muscular Atrophy
- OAV101
-
Montreal, Quebec, Canada
- +1 more
Jan 31, 2023
Spinal Muscular Atrophy Trial in New York (Nusinersen Treatments)
Withdrawn
- Spinal Muscular Atrophy
- Nusinersen Treatments
-
New York, New YorkNYU Langone Health
Jun 25, 2021
Turkish Version of PedsQL 3.0 Neuromuscular Module for 2-to 4-
Enrolling by invitation
- Spinal Muscular Atrophy
- +3 more
-
Istanbul, Kavacık, TurkeySeval Kutlutürk Yıkılmaz
Sep 15, 2022
Neurologic Diseases, Hemiparesis, Quadriplegia Trial in Wilmington, Philadelphia (Neurosleeve)
Recruiting
- Neurologic Diseases
- +13 more
- Neurosleeve
-
Wilmington, Delaware
- +1 more
Dec 2, 2022
Muscular Atrophy, Spinal, Type II, Muscular Atrophy, Spinal, Type III Trial in France (Strength force measurment, Time tests,
Not yet recruiting
- Muscular Atrophy, Spinal, Type II
- Muscular Atrophy, Spinal, Type III
- Strength force measurment
- +6 more
-
Angers, France
- +5 more
Apr 20, 2023
Impairments of Neuro-muscular Communication in Motor-Neuron
Recruiting
- ALS (Amyotrophic Lateral Sclerosis)
- +2 more
- 128 electrode electroencephalography (EEG), Bipolar surface electromyography (sEMG), High-density electromyography (HD-EMG)
-
Dublin, Leinster, IrelandAcademic Unit of Neurology, Trinity College Dublin, The Universi
Dec 21, 2022