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TPP1

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Cerliponase Alfa Observational Study in the US

Recruiting
  • Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2
  • Cerliponase Alfa
  • Administration Kit
  • Little Rock, Arkansas
  • +13 more
Jun 2, 2022

Neuronal Ceroid Lipofuscinosis Type 2 Trial in London (RGX-381)

Not yet recruiting
  • Neuronal Ceroid Lipofuscinosis Type 2
  • RGX-381
  • London, United Kingdom
    Greater Ormond Street Hospital
Mar 17, 2023

Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients

Active, not recruiting
  • Neuronal Ceroid-Lipofuscinoses
  • +2 more
    • Orange, California
      Children's Hospital of Orange County
    Jul 18, 2022

    Children Diagnosed With CLN2 Disease

    Recruiting
    • Batten Disease
    • +2 more
    • CLN2 Treatment
    • Columbus, Ohio
      Nationwide Children's Hospital
    Aug 2, 2021

    Neuronal Ceroid Lipofuscinosis Type 2 Trial in Columbus (Cerliponase Alfa)

    Enrolling by invitation
    • Neuronal Ceroid Lipofuscinosis Type 2
    • Cerliponase Alfa
    • Columbus, Ohio
      Nationwide Children's Hospital
    Nov 29, 2021

    Obesity, Surgery, Anesthesia Trial in Burlington (Individualized lung-protective ventilation, Standard lung-protective

    Not yet recruiting
    • Obesity
    • +4 more
    • Individualized lung-protective ventilation
    • Standard lung-protective ventilation
    • Burlington, Vermont
      University of Vemont Medical Center
    Jan 23, 2023

    Neuronal Ceroid Lipofuscinosis, Batten Disease, CLN1 Disease Trial in Hamburg (Natural History)

    Recruiting
    • Neuronal Ceroid Lipofuscinosis
    • +14 more
    • Natural History
    • Hamburg, Germany
      University Medical Center Hamburg-Eppendorf
    Oct 22, 2021

    Cough Audio Classification as a TB Triage Test

    Recruiting
    • Tuberculosis
    • Cough sounds
    • Cape Town, Western Cape, South Africa
    • +1 more
    Jul 21, 2022

    Study Will Examine the Impact of Project With Trial in Alhambra (Project With)

    Recruiting
    • Study Will Examine the Impact of Project With
    • Project With
    • Alhambra, California
      Urban Strategies
    Apr 27, 2022

    Covid19 Trial in Nottingham (Residence-based testing participation pilot (SARS-CoV-2 testing with relaxed social distancing

    Completed
    • Covid19
    • Residence-based testing participation pilot (SARS-CoV-2 testing with relaxed social distancing restrictions)
    • Nottingham, United Kingdom
      University of Nottingham
    Sep 15, 2021

    Clinical Evaluation of tNGS for Diagnosis of DR-TB

    Active, not recruiting
    • Tuberculosis, Multidrug-Resistant
    • targeted Next Generation Sequencing (tNGS)
    • Tbilisi, Georgia
    • +2 more
    Jan 23, 2023

    Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190,

    Completed
    • Jansky-Bielschowsky Disease
    • +4 more
    • BMN 190
    • Intracerebroventricular (ICV) access device
    • Columbus, Ohio
    • +3 more
    Jul 28, 2022

    Knee Osteoarthritis Trial in Lahore (MULLIGAN ROTATIONAL MOVEMENT, Medial gapping technique)

    Completed
    • Knee Osteoarthritis
    • MULLIGAN ROTATIONAL MOVEMENT
    • Medial gapping technique
    • Lahore, Punjab, Pakistan
      Riphah Rehabilitation Center
    Dec 17, 2022

    Recurrent/Metastatic Carcinosarcoma Trial in Seoul (nivolumab)

    Recruiting
    • Recurrent/Metastatic Carcinosarcoma
    • Seoul, Korea, Republic of
      Severance Hospital, Yonsei University Health System
    Feb 3, 2022

    Tuberculosis Trial in Abuja, Dasmariñas, Lusaka (Tongue swab-based molecular assays)

    Not yet recruiting
    • Tuberculosis
    • Tongue swab-based molecular assays
    • Abuja, Nigeria
    • +2 more
    Jul 11, 2023

    Anterior Cruciate Ligament Tear Trial in Istanbul (Primary anterior cruciate ligament repair, Primary anterior cruciate ligament

    Completed
    • Anterior Cruciate Ligament Tear
    • Primary anterior cruciate ligament repair
    • Primary anterior cruciate ligament repair and lateral extraarticular tenodesis (LET) with iliotibial band
    • Istanbul, Turkey
      SBU Prof. Cemil Tascioglu City Hospital
    Jun 27, 2023

    Hepatocellular Carcinoma Trial in Greece, Israel, Italy (Milciclib maleate)

    Completed
    • Hepatocellular Carcinoma
    • Milciclib maleate
    • Athens, Greece
    • +13 more
    Oct 11, 2021

    Knee Osteoarthritis Trial in Ankara (Baseline, Intrinsic focus, White noise)

    Completed
    • Knee Osteoarthritis
    • Baseline
    • +3 more
    • Ankara, Turkey
      Gazi University Faculty of Medicine
    Oct 2, 2023

    Solid Tumors Trial (ARTS-021, CDK 4/6 inhibitor, Fulvestrant 50 MG/ML Prefilled Syringe)

    Not yet recruiting
    • Solid Tumors
    • (no location specified)
    May 17, 2023

    Soil Transmitted Helminths, Schistosomiasis Mansoni Trial (Artificial Intelligence Digital Pathology)

    Not yet recruiting
    • Soil Transmitted Helminths
    • Schistosomiasis Mansoni
    • Artificial Intelligence Digital Pathology
    • (no location specified)
    Sep 29, 2023

    Lymphoma, B-Cell, Neurotoxicity Trial in Montpellier (Magnetic Resonance Imaging with contrast injection, Blood withdrawal,

    Not yet recruiting
    • Lymphoma, B-Cell
    • Neurotoxicity
    • Magnetic Resonance Imaging with contrast injection
    • +2 more
    • Montpellier, Occitanie, France
      Neurology department, Montpellier University Hospital
    Aug 19, 2022

    Tuberculosis, Diagnostics, Global Health Trial in Maputo, Cape Town, Kampala (Oral swab molecular testing, Automated Cough Sound

    Not yet recruiting
    • Tuberculosis
    • +2 more
    • Oral swab molecular testing
    • +3 more
    • Maputo, Mozambique
    • +2 more
    Aug 9, 2023

    Pregnancy, Sexually Transmitted Infections, Automobile Accidents Trial in Columbus, Pittsburgh, Morgantown (Seventeen Days,

    Completed
    • Pregnancy
    • +2 more
    • Seventeen Days
    • Driving Skills for Life
    • Columbus, Ohio
    • +2 more
    Dec 2, 2021

    Heart Failure, Acidosis, Lactic, Thiamine Deficiency Trial in Vienna (Vitamin B1-ratiopharm, Placebo)

    Completed
    • Heart Failure
    • +2 more
    • Vitamin B1-ratiopharm
    • Placebo
    • Vienna, Austria
      Medical University Vienna
    Feb 23, 2021

    Neurodevelopmental Disorders Trial in Hong Kong (EC Brain After-school Program, conventional intervention)

    Recruiting
    • Neurodevelopmental Disorders
    • EC Brain After-school Program
    • conventional intervention
    • Hong Kong, Hong Kong
      The Chinese University of Hong Kong
    Jun 17, 2022