Thalassaemia
Showing 1 - 25 of 106
Transfusion Dependent Beta-Thalassaemia Trial in Nanning (ET-01)
Recruiting
- Transfusion Dependent Beta-Thalassaemia
- ET-01
-
Nanning, Guangxi, ChinaPLA 923 Hospital
Mar 2, 2023
Transfusion Dependent Beta-Thalassaemia Trial in Guangzhou, Shenzhen, Tianjin (ET-01)
Active, not recruiting
- Transfusion Dependent Beta-Thalassaemia
- ET-01
-
Guangzhou, Guangdong, China
- +3 more
May 9, 2022
Transfusion Dependent Beta-Thalassaemia Trial in Tianjin (ET-01)
Active, not recruiting
- Transfusion Dependent Beta-Thalassaemia
- ET-01
-
Tianjin, Tianjin, ChinaInstitute of Hematology & Blood Diseases Hospital
Dec 9, 2021
Thalassemia Major Trial in Ferrara (Blood component A, Blood component B)
Completed
- Thalassemia Major
- Blood component A
- Blood component B
-
Ferrara, ItalyDay Hospital Thalassaemia and Haemoglobinopathies (DHTE)
Nov 11, 2021
Beta Thalassaemia Trial in Milan (Safety and Efficacy assessments)
Active, not recruiting
- Beta Thalassaemia
- Safety and Efficacy assessments
-
Milan, ItalyOspedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 22, 2022
Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in
Recruiting
- Non-transfusion-dependent Thalassemia
- +2 more
- SLN124
- Placebo
-
Düsseldorf, Germany
- +19 more
Mar 18, 2022
Beta-Thalassemia Trial in Bulgaria, Israel, United States (VIT-2763 60 mg QD, VIT-2763 60 mg BID, VIT-2763 120 mg BID)
Withdrawn
- Beta-Thalassemia
- VIT-2763 60 mg QD
- +3 more
-
Whittier, California
- +6 more
Nov 7, 2022
Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)
Recruiting
- Beta-Thalassemia
- Sirolimus 0.5 mg
-
Ferrara, FE, Italy
- +3 more
Nov 11, 2021
Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (AG-348)
Completed
- Pyruvate Kinase Deficiency
- Anemia, Hemolytic
-
Oakland, California
- +18 more
Dec 14, 2021
Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome Trial in Bulgaria, United Kingdom (SLN124 is a GalNAc
Withdrawn
- Non-transfusion-dependent Thalassemia
- Low Risk Myelodysplastic Syndrome
- SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as Placebo
-
Kyustendil, Bulgaria
- +4 more
Apr 23, 2020
Sickle Cell Disease, Sickle Cell Trait, Beta-Thalassemia Trial (High performance liquid chromatography, Automated sickling test,
Not yet recruiting
- Sickle Cell Disease
- +4 more
- High performance liquid chromatography
- +5 more
- (no location specified)
Aug 17, 2022
Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (Placebo, AG-348)
Completed
- Pyruvate Kinase Deficiency
- Anemia, Hemolytic
- Placebo
- AG-348
-
Little Rock, Arkansas
- +45 more
May 20, 2022
Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)
Recruiting
- Thalassemia Major
- Transfusion-dependent Anemia
- Luspatercept Injectable Product
-
Guangzhou, Guangdong, ChinaThe second affiliated hospital of Sun Yat-sen University
Jul 15, 2022
Type 3 Von Willebrand International Registries Inhibitor
Active, not recruiting
- Type 3 Von Willebrand's Disease
- Von Willebrand Factor
-
Helsinki, Finland
- +24 more
Mar 21, 2022
Transfusion-dependent Thalassemia Trial in Dhaka (Thalidomide Capsules, Placebo)
Recruiting
- Transfusion-dependent Thalassemia
- Thalidomide Capsules
- Placebo
-
Dhaka, BangladeshBangabandhu Sheikh Mujib Medical University
Oct 18, 2023
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen Children's Hospital
Feb 24, 2023
Hemoglobinopathies and Rare Inherited Anemia and Covid 19
Recruiting
- Haemoglobinopathies
-
Genova, Italy
- +1 more
May 4, 2022
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen University General Hospital
May 8, 2023
Transfusion-dependent ß-thalassemia Patients, Cardiac Iron Overload Trial in Athens, Patras (Deferasirox, Deferoxamine (DFO))
Terminated
- Transfusion-dependent β-thalassemia Patients
- Cardiac Iron Overload
- Deferasirox
- Deferoxamine (DFO)
-
Athens, GR, Greece
- +3 more
Oct 21, 2019
Thalassemia, Iron Overload Trial in Nanning (CN128 Tablets)
Active, not recruiting
- Thalassemia
- Iron Overload
- CN128 Tablets
-
Nanning, Guangxi, ChinaThe First Affiliated Hospital Of Guangxi Medical University
Aug 3, 2022
Thalassemia Trial in Peshawar (Thalidomide and Hydroxyurea)
Completed
- Thalassemia
- Thalidomide and Hydroxyurea
-
Peshawar, Khyber Pakhtukhwa, PakistanBlood Diseases Clinic
Mar 10, 2022
Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)
Not yet recruiting
- Transfusion-dependent Beta-Thalassemia
- KL003 cell injection Drug Product
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
May 8, 2023
Atrial Fibrillation in Beta-Thalassemia
Not yet recruiting
- Atrial Fibrillation
- Thalassemia
-
Ferrara, ItalyMatteo Bertini
Aug 18, 2022
Clinical Presentation of Genetic Disorders in Patients Attending
Not yet recruiting
- Genetic Disease Clinical Presentation in Patients Attending Genetics Outpatient Clinic of Assiut University Children Hospital
- (no location specified)
Jun 2, 2023
Beta Thalassemia Intermedia Trial in Worldwide (IONIS TMPRSS6-LRx)
Active, not recruiting
- Beta Thalassemia Intermedia
-
Camperdown, New South Wales, Australia
- +18 more
Sep 23, 2022