miglustat
Showing 1 - 25 of 33
Glycogen Storage Disease Type II Infantile Onset Trial in Gainesville (Cipaglucosidase alfa (ATB200), Miglustat (AT2221))
Recruiting
- Glycogen Storage Disease Type II Infantile Onset
- Cipaglucosidase alfa
- Miglustat
-
Gainesville, FloridaUniversity of Florida Clinical Research Center
Jan 18, 2023
GM2 Gangliosidosis, Supportive Care Trial in Kashan, Mashhad, Tehran (Miglustat)
Recruiting
- GM2 Gangliosidosis
- Supportive Care
- Miglustat
-
Kashan, Isfahan, Iran, Islamic Republic of
- +2 more
Oct 23, 2022
Hereditary Spastic Paraparesis Trial in Pisa (Miglustat 100 MG)
Completed
- Hereditary Spastic Paraparesis
- Miglustat 100 MG
-
Pisa, PI, ItalyIRCCS Fondazione Stella Maris
Apr 1, 2022
Batten Disease Trial in Houston (Miglustat 100Mg Oral Capsule)
Recruiting
- Batten Disease
- Miglustat 100Mg Oral Capsule
-
Houston, TexasTexas Children Hospital
May 17, 2022
Pompe Disease Trial in New York, Fairfax (biological, drug, other)
Not yet recruiting
- Pompe Disease
- Cipaglucosidase alfa
- +3 more
-
New York, New York
- +1 more
Nov 2, 2023
GM1 Gangliosidoses, GM2 Gangliosidoses, Tay-Sachs Disease Trial in Minneapolis (miglustat, Ketogenic Diet)
Terminated
- GM1 Gangliosidoses
- +3 more
- miglustat
- Ketogenic Diet
-
Minneapolis, MinnesotaUniversity of Minnesota
Mar 18, 2021
Gaucher Disease Trial in Taipei (Miglustat, ERT)
Unknown status
- Gaucher Disease
- Miglustat
- ERT
-
Taipei, TaiwanNational Taiwan University Hospital
Mar 28, 2019
Niemann-Pick Disease, Type C Trial in Worldwide (arimoclomol, Placebo)
Active, not recruiting
- Niemann-Pick Disease, Type C
- arimoclomol
- Placebo
-
Oakland, California
- +13 more
Apr 14, 2021
Niemann-Pick Disease, Type C1 Trial in Worldwide (Hydroxypropyl-beta-cyclodextrin, Placebo)
Recruiting
- Niemann-Pick Disease, Type C1
- Hydroxypropyl-beta-cyclodextrin
- Placebo
-
Oakland, California
- +13 more
Jan 9, 2023
Gaucher Disease Type 1 Trial in Worldwide (Miglustat)
Completed
- Gaucher Disease Type 1
- Miglustat
-
San Francisco, California
- +19 more
Oct 24, 2018
Pompe Disease, Hypersensitivity Reaction Trial (Zavesca® Prescription)
Terminated
- Pompe Disease
- Hypersensitivity Reaction
- Zavesca® Prescription
- (no location specified)
Dec 4, 2018
Cystic Fibrosis Trial in Paris (Miglustat ; , Placebo ; Miglustat)
Completed
- Cystic Fibrosis
- Miglustat ; placebo
- Placebo ; Miglustat
-
Paris, FranceAssistance publique-Hôpitaux de Paris, Hôpital Cochin
Mar 16, 2018
Niemann-Pick Disease, Type C1 Trial in Oakland, Morristown (Hydroxypropyl-beta-cyclodextrin)
Completed
- Niemann-Pick Disease, Type C1
-
Oakland, California
- +1 more
Feb 17, 2021
Gangliosidoses GM2 Trial in Toronto (miglustat)
Completed
- Gangliosidoses GM2
- miglustat
-
Toronto, Ontario, CanadaThe Hospital for Sick Children
May 18, 2016
Gaucher Disease Trial in Bethesda, London (OGT 918)
Completed
- Gaucher Disease
- OGT 918
-
Bethesda, Maryland
- +1 more
Jun 30, 2017
Diarrhea Trial in Toronto (Treatment A, Treatment B)
Completed
- Diarrhea
- Treatment A
- Treatment B
-
Toronto, Ontario, CanadaBioPharma Services Inc.
Mar 9, 2015
Cystic Fibrosis Trial in Brussels (miglustat, )
Completed
- Cystic Fibrosis
- miglustat
- placebo
-
Brussels, BelgiumUniversite Catholique de Louvain
Mar 5, 2014
Gene Therapy for Tay-Sachs Disease
Completed
- Tay Sachs Disease
- +2 more
-
Tampa, Florida
- +1 more
Dec 3, 2014
Niemann-Pick Disease, Type C Trial run by the NICHD (N-Acetyl Cysteine)
Completed
- Niemann-Pick Disease, Type C
- N-Acetyl Cysteine
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Apr 30, 2013