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miglustat

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STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Glycogen Storage Disease Type II Infantile Onset Trial in Gainesville (Cipaglucosidase alfa (ATB200), Miglustat (AT2221))

Recruiting
  • Glycogen Storage Disease Type II Infantile Onset
  • Cipaglucosidase alfa
  • Miglustat
  • Gainesville, Florida
    University of Florida Clinical Research Center
Jan 18, 2023

GM2 Gangliosidosis, Supportive Care Trial in Kashan, Mashhad, Tehran (Miglustat)

Recruiting
  • GM2 Gangliosidosis
  • Supportive Care
  • Miglustat
  • Kashan, Isfahan, Iran, Islamic Republic of
  • +2 more
Oct 23, 2022

Hereditary Spastic Paraparesis Trial in Pisa (Miglustat 100 MG)

Completed
  • Hereditary Spastic Paraparesis
  • Miglustat 100 MG
  • Pisa, PI, Italy
    IRCCS Fondazione Stella Maris
Apr 1, 2022

Batten Disease Trial in Houston (Miglustat 100Mg Oral Capsule)

Recruiting
  • Batten Disease
  • Miglustat 100Mg Oral Capsule
  • Houston, Texas
    Texas Children Hospital
May 17, 2022

Pompe Disease Trial in New York, Fairfax (biological, drug, other)

Not yet recruiting
  • Pompe Disease
  • Cipaglucosidase alfa
  • +3 more
  • New York, New York
  • +1 more
Nov 2, 2023

GM1 Gangliosidoses, GM2 Gangliosidoses, Tay-Sachs Disease Trial in Minneapolis (miglustat, Ketogenic Diet)

Terminated
  • GM1 Gangliosidoses
  • +3 more
  • miglustat
  • Ketogenic Diet
  • Minneapolis, Minnesota
    University of Minnesota
Mar 18, 2021

Pompe Disease Trial in Worldwide (ATB200, AT2221)

Active, not recruiting
  • Pompe Disease
  • Phoenix, Arizona
  • +18 more
Oct 19, 2021

Pompe Disease Infantile-Onset Trial in Italy, Taiwan, United States (ATB200, AT2221)

Available
  • Pompe Disease Infantile-Onset
  • Oakland, California
  • +3 more
Jul 18, 2022

Gaucher Disease Trial in Taipei (Miglustat, ERT)

Unknown status
  • Gaucher Disease
  • Taipei, Taiwan
    National Taiwan University Hospital
Mar 28, 2019

Niemann-Pick Disease, Type C Trial in Worldwide (arimoclomol, Placebo)

Active, not recruiting
  • Niemann-Pick Disease, Type C
  • Oakland, California
  • +13 more
Apr 14, 2021

Pompe Disease (Late-onset) Trial in Worldwide (AT2221, alglucosidase alfa, ATB200)

Completed
  • Pompe Disease (Late-onset)
  • Phoenix, Arizona
  • +72 more
Oct 7, 2021

Niemann-Pick Disease, Type C1 Trial in Worldwide (Hydroxypropyl-beta-cyclodextrin, Placebo)

Recruiting
  • Niemann-Pick Disease, Type C1
  • Oakland, California
  • +13 more
Jan 9, 2023

Gaucher Disease Type 1 Trial in Worldwide (Miglustat)

Completed
  • Gaucher Disease Type 1
  • Miglustat
  • San Francisco, California
  • +19 more
Oct 24, 2018

Pompe Disease, Hypersensitivity Reaction Trial (Zavesca® Prescription)

Terminated
  • Pompe Disease
  • Hypersensitivity Reaction
  • Zavesca® Prescription
  • (no location specified)
Dec 4, 2018

Cystic Fibrosis Trial in Paris (Miglustat ; , Placebo ; Miglustat)

Completed
  • Cystic Fibrosis
  • Miglustat ; placebo
  • Placebo ; Miglustat
  • Paris, France
    Assistance publique-Hôpitaux de Paris, Hôpital Cochin
Mar 16, 2018

Niemann-Pick Disease, Type C1 Trial in Oakland, Morristown (Hydroxypropyl-beta-cyclodextrin)

Completed
  • Niemann-Pick Disease, Type C1
  • Oakland, California
  • +1 more
Feb 17, 2021

Pompe Disease Undergoing Immune Modulation Therapies

Completed
  • Pompe Disease
  • Gainesville, Florida
    University of Florida
Dec 6, 2017

Gangliosidoses GM2 Trial in Toronto (miglustat)

Completed
  • Gangliosidoses GM2
  • miglustat
  • Toronto, Ontario, Canada
    The Hospital for Sick Children
May 18, 2016

Niemann Pick Diseases Trial in Bethesda, New York, Abingdon (OGT918)

Completed
  • Niemann Pick Diseases
  • Bethesda, Maryland
  • +2 more
Jun 30, 2017

Gaucher Disease Trial in Bethesda, London (OGT 918)

Completed
  • Gaucher Disease
  • OGT 918
  • Bethesda, Maryland
  • +1 more
Jun 30, 2017

Diarrhea Trial in Toronto (Treatment A, Treatment B)

Completed
  • Diarrhea
  • Treatment A
  • Treatment B
  • Toronto, Ontario, Canada
    BioPharma Services Inc.
Mar 9, 2015

Cystic Fibrosis Trial in Brussels (miglustat, )

Completed
  • Cystic Fibrosis
  • miglustat
  • placebo
  • Brussels, Belgium
    Universite Catholique de Louvain
Mar 5, 2014

Gene Therapy for Tay-Sachs Disease

Completed
  • Tay Sachs Disease
  • +2 more
    • Tampa, Florida
    • +1 more
    Dec 3, 2014

    Niemann-Pick Disease, Type C Trial run by the NICHD (N-Acetyl Cysteine)

    Completed
    • Niemann-Pick Disease, Type C
    • N-Acetyl Cysteine
    • Bethesda, Maryland
      National Institutes of Health Clinical Center, 9000 Rockville Pi
    Apr 30, 2013