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osteopetrosis

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STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

Recruiting
  • Mucopolysaccharidosis Disorders
  • +28 more
  • Stem Cell Transplantation
  • +7 more
  • Minneapolis, Minnesota
    Masonic Cancer Center, University of Minnesota
Nov 1, 2022

Autosomal Dominant Osteopetrosis Type 2 Trial in Indianapolis (ACTIMMUNE)

Completed
  • Autosomal Dominant Osteopetrosis Type 2
  • Indianapolis, Indiana
    Indiana University School of Medicine
Dec 11, 2020

The Natural History of Metachromatic Leukodystrophy

Recruiting
  • MLD
  • +26 more
  • Palliative Care
  • Hematopoetic Stem Cell Transplantation
  • Pittsburgh, Pennsylvania
    The Program for the Study of Neurodevelopment in Rare Disorders,
Nov 2, 2021

Acute Lymphoblastic Leukemia, Acute Myeloid Leukemia, Chronic Myeloid Leukemia Trial in San Francisco (CD34+ enriched, T Cell

No longer available
  • Acute Lymphoblastic Leukemia
  • +11 more
  • CD34+ enriched, T Cell Depleted donor stem cell product
  • San Francisco, California
    University of California, San Francisco
May 25, 2021

Severe Osteopetrosis Trial in Minneapolis (procedure, drug, radiation)

Completed
  • Severe Osteopetrosis
  • umbilical cord blood transplantation
  • +6 more
  • Minneapolis, Minnesota
    University of MInnesota, Fairview
Jul 10, 2019

Osteopetrosis Trial in Torrance, Minneapolis (Interferon gamma-1b)

Completed
  • Osteopetrosis
  • Interferon gamma-1b
  • Torrance, California
  • +1 more
Jul 1, 2019

Osteopenia, Osteoporosis Trial in Minneapolis, Seattle (Pamidronate, Calcium and vitamin D)

Completed
  • Osteopenia
  • Osteoporosis
  • Minneapolis, Minnesota
  • +1 more
Dec 8, 2022

Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Recruiting
  • Primary Immunodeficiency (PID)
  • +4 more
  • data collection
  • Pittsburgh, Pennsylvania
    UPMC Children's Hospital of Pittsburgh
Feb 9, 2022

Distal Radius Fracture, Wrist Fracture Trial in Istanbul (Exercise, PNF Technique, Mulligan Mobilization)

Not yet recruiting
  • Distal Radius Fracture
  • Wrist Fracture
  • Exercise
  • +2 more
  • Istanbul, Turkey
    Biruni University
May 29, 2023

Mitochondrial Diseases, Bone Remodeling Disorder Trial in Aalborg (Clinical assessment, blood samples, bone marrow and bone

Recruiting
  • Mitochondrial Diseases
  • Bone Remodeling Disorder
  • Clinical assessment, blood samples, bone marrow and bone biopsy
  • Aalborg, Denmark
    Dept. of Clinical Genetics
Aug 16, 2022

Osteopetrosis Trial in Minneapolis (Stem Cell or Umbilical Cord Blood Transplantation, Campath, Busulfan, Clofarabine, Total

Terminated
  • Osteopetrosis
  • Stem Cell or Umbilical Cord Blood Transplantation
  • +2 more
  • Minneapolis, Minnesota
    University of MInnesota, Fairview
Dec 3, 2017

COVID-19 Pneumonia Trial in Naples (Saisei Maf capsules)

Completed
  • COVID-19 Pneumonia
  • Saisei Maf capsules
  • Naples, Italy
    Ospedale del Mare Hospital
Sep 7, 2021

Osteopetrosis Trial in Memphis (procedure, device, drug)

Terminated
  • Osteopetrosis
  • Stem Cell Transplantation
  • +2 more
  • Memphis, Tennessee
    St. Jude Children's Research Hospital
Apr 24, 2017

Friedreich Ataxia Trial (gamma interferon)

Completed
  • Friedreich Ataxia
  • gamma interferon
  • (no location specified)
Feb 25, 2020

Testis, Infertility, Sperm Trial in Copenhagen (Denosumab)

Completed
  • Testis
  • +2 more
  • Copenhagen, Denmark
    Rigshospitalet
Mar 25, 2019

Crohn Disease Trial in Winnipeg (Denosumab)

Completed
  • Crohn Disease
  • Winnipeg, Manitoba, Canada
    University of Manitoba
Oct 10, 2018

Sickle Cell Disease, Thalassemia, Anemia Trial in Los Angeles (Hematopoietic stem cell transplantation)

Completed
  • Sickle Cell Disease
  • +11 more
  • Hematopoietic stem cell transplantation
  • Los Angeles, California
    Children Hospital Los Angeles
Jun 21, 2016

Osteopetrosis Trial in Chicago (rhPTH)

Terminated
  • Osteopetrosis
  • Chicago, Illinois
    University of Chicago
Jan 8, 2016

Osteopetrosis Trial (calcitriol, interferon gamma)

Completed
  • Osteopetrosis
  • (no location specified)
Mar 24, 2015

Exploration of Autonomic Nervous System by Photoplethysmography

Completed
  • Intervention Affecting Autonomic Nervous System
  • autonomic nervous system analysis
  • Milan, Italy
    Luigi Sacco Hospital
Jun 23, 2015

Osteopetrosis Trial in Tehran (Busulfan, Cyclophosphamide, Thymoglobulin, Fludarabine (Conditioning regimen), Stem Cell

Unknown status
  • Osteopetrosis
  • Busulfan, Cyclophosphamide, Thymoglobulin, Fludarabine (Conditioning regimen)
  • +2 more
  • Tehran, Iran, Islamic Republic of
    Hematology-Oncology & SCT Research Center
May 31, 2012

GVHD Trial in Italy (polyclonal antibody, Rituximab, Treosulfan)

Unknown status
  • Graft Versus Host Disease
  • polyclonal antibody
  • +6 more
  • Cagliari, Italy
  • +3 more
Mar 12, 2013

Bone Marrow Failure, Osteopetrosis, Fanconi Anemia Trial in New York (Fludarabine, Cyclophosphamide, Cyclophosphamide 40)

Unknown status
  • Bone Marrow Failure
  • +3 more
  • New York, New York
    Columbia University Medical Center
Oct 18, 2011

Patients With High Bone Mass Due to Mutation in Lrp5

Completed
  • Osteopetrosis
    • Odense, Denmark
      Odense University Hospital, Osteoporosis Clinic
    Sep 9, 2010

    Actimmune in Patients With Severe, Malignant Osteopetrosis

    Completed
    • Osteopetrosis
    • Actimmune Registry
    • Brisbane, California
      InterMune, Inc.
    Oct 30, 2007