osteopetrosis
Showing 1 - 25 of 25
Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD
Recruiting
- Mucopolysaccharidosis Disorders
- +28 more
- Stem Cell Transplantation
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Nov 1, 2022
Autosomal Dominant Osteopetrosis Type 2 Trial in Indianapolis (ACTIMMUNE)
Completed
- Autosomal Dominant Osteopetrosis Type 2
-
Indianapolis, IndianaIndiana University School of Medicine
Dec 11, 2020
The Natural History of Metachromatic Leukodystrophy
Recruiting
- MLD
- +26 more
- Palliative Care
- Hematopoetic Stem Cell Transplantation
-
Pittsburgh, PennsylvaniaThe Program for the Study of Neurodevelopment in Rare Disorders,
Nov 2, 2021
Acute Lymphoblastic Leukemia, Acute Myeloid Leukemia, Chronic Myeloid Leukemia Trial in San Francisco (CD34+ enriched, T Cell
No longer available
- Acute Lymphoblastic Leukemia
- +11 more
- CD34+ enriched, T Cell Depleted donor stem cell product
-
San Francisco, CaliforniaUniversity of California, San Francisco
May 25, 2021
Severe Osteopetrosis Trial in Minneapolis (procedure, drug, radiation)
Completed
- Severe Osteopetrosis
- umbilical cord blood transplantation
- +6 more
-
Minneapolis, MinnesotaUniversity of MInnesota, Fairview
Jul 10, 2019
Osteopetrosis Trial in Torrance, Minneapolis (Interferon gamma-1b)
Completed
- Osteopetrosis
- Interferon gamma-1b
-
Torrance, California
- +1 more
Jul 1, 2019
Osteopenia, Osteoporosis Trial in Minneapolis, Seattle (Pamidronate, Calcium and vitamin D)
Completed
- Osteopenia
- Osteoporosis
- Pamidronate
- Calcium and vitamin D
-
Minneapolis, Minnesota
- +1 more
Dec 8, 2022
Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Recruiting
- Primary Immunodeficiency (PID)
- +4 more
- data collection
-
Pittsburgh, PennsylvaniaUPMC Children's Hospital of Pittsburgh
Feb 9, 2022
Distal Radius Fracture, Wrist Fracture Trial in Istanbul (Exercise, PNF Technique, Mulligan Mobilization)
Not yet recruiting
- Distal Radius Fracture
- Wrist Fracture
- Exercise
- +2 more
-
Istanbul, TurkeyBiruni University
May 29, 2023
Mitochondrial Diseases, Bone Remodeling Disorder Trial in Aalborg (Clinical assessment, blood samples, bone marrow and bone
Recruiting
- Mitochondrial Diseases
- Bone Remodeling Disorder
- Clinical assessment, blood samples, bone marrow and bone biopsy
-
Aalborg, DenmarkDept. of Clinical Genetics
Aug 16, 2022
Osteopetrosis Trial in Minneapolis (Stem Cell or Umbilical Cord Blood Transplantation, Campath, Busulfan, Clofarabine, Total
Terminated
- Osteopetrosis
- Stem Cell or Umbilical Cord Blood Transplantation
- +2 more
-
Minneapolis, MinnesotaUniversity of MInnesota, Fairview
Dec 3, 2017
COVID-19 Pneumonia Trial in Naples (Saisei Maf capsules)
Completed
- COVID-19 Pneumonia
- Saisei Maf capsules
-
Naples, ItalyOspedale del Mare Hospital
Sep 7, 2021
Osteopetrosis Trial in Memphis (procedure, device, drug)
Terminated
- Osteopetrosis
- Stem Cell Transplantation
- +2 more
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Apr 24, 2017
Friedreich Ataxia Trial (gamma interferon)
Completed
- Friedreich Ataxia
- gamma interferon
- (no location specified)
Feb 25, 2020
Sickle Cell Disease, Thalassemia, Anemia Trial in Los Angeles (Hematopoietic stem cell transplantation)
Completed
- Sickle Cell Disease
- +11 more
- Hematopoietic stem cell transplantation
-
Los Angeles, CaliforniaChildren Hospital Los Angeles
Jun 21, 2016
Exploration of Autonomic Nervous System by Photoplethysmography
Completed
- Intervention Affecting Autonomic Nervous System
- autonomic nervous system analysis
-
Milan, ItalyLuigi Sacco Hospital
Jun 23, 2015
Osteopetrosis Trial in Tehran (Busulfan, Cyclophosphamide, Thymoglobulin, Fludarabine (Conditioning regimen), Stem Cell
Unknown status
- Osteopetrosis
- Busulfan, Cyclophosphamide, Thymoglobulin, Fludarabine (Conditioning regimen)
- +2 more
-
Tehran, Iran, Islamic Republic ofHematology-Oncology & SCT Research Center
May 31, 2012
GVHD Trial in Italy (polyclonal antibody, Rituximab, Treosulfan)
Unknown status
- Graft Versus Host Disease
- polyclonal antibody
- +6 more
-
Cagliari, Italy
- +3 more
Mar 12, 2013
Bone Marrow Failure, Osteopetrosis, Fanconi Anemia Trial in New York (Fludarabine, Cyclophosphamide, Cyclophosphamide 40)
Unknown status
- Bone Marrow Failure
- +3 more
- Fludarabine
- +3 more
-
New York, New YorkColumbia University Medical Center
Oct 18, 2011
Patients With High Bone Mass Due to Mutation in Lrp5
Completed
- Osteopetrosis
-
Odense, DenmarkOdense University Hospital, Osteoporosis Clinic
Sep 9, 2010
Actimmune in Patients With Severe, Malignant Osteopetrosis
Completed
- Osteopetrosis
- Actimmune Registry
-
Brisbane, CaliforniaInterMune, Inc.
Oct 30, 2007