rAAV
Showing 1 - 25 of 79
Hemophilia B Without Inhibitor Trial (Low dose KL001, Middle dose KL001, High dose KL001)
Not yet recruiting
- Hemophilia B Without Inhibitor
- Low dose KL001
- +2 more
- (no location specified)
Nov 5, 2023
Hemophilia B Without Inhibitor Trial (Low dose KL001, Middle dose KL001, High dose KL001)
Not yet recruiting
- Hemophilia B Without Inhibitor
- Low dose KL001
- +2 more
- (no location specified)
Nov 5, 2023
HIV Trial (Low dose KL-HIV-Tri01, Middle dose KL-HIV-Tri01, High dose KL-HIV-Tri01)
Not yet recruiting
- HIV Infections
- Low dose KL-HIV-Tri01
- +2 more
- (no location specified)
Nov 5, 2023
Bietti's Crystalline Dystrophy Trial in Beijing (ZVS101e)
Recruiting
- Bietti's Crystalline Dystrophy
-
Beijing, Beijing, ChinaPeking University Third Hospital
Feb 2, 2023
Achromatopsia Trial in Tuebingen (rAAV.hCNGA3)
Recruiting
- Achromatopsia
-
Tuebingen, GermanyUniversity Hospital Tuebingen, Center for Ophthalmology
Dec 7, 2022
Canavan Disease Trial in Dayton (rAAV-Olig001-ASPA, Levetiracetam, Prednisone)
Enrolling by invitation
- Canavan Disease
- rAAV-Olig001-ASPA
- +2 more
-
Dayton, OhioDayton Children's Hospital
Jun 23, 2022
X-linked Retinoschisis Trial in United States (rAAV2tYF-CB-hRS1)
Active, not recruiting
- X-linked Retinoschisis
- rAAV2tYF-CB-hRS1
-
San Francisco, California
- +8 more
Jul 18, 2022
Retinitis Pigmentosa Trial in Tuebingen (subretinal injection of rAAV.hPDE6A)
Active, not recruiting
- Retinitis Pigmentosa
- subretinal injection of rAAV.hPDE6A
-
Tuebingen, GermanyUniversitätsklinikum Tübingen, Department für Augenheilkunde
Dec 7, 2022
Retinal Disease, Retinitis Pigmentosa Trial in Riyadh (Subretinal administration of rAAV2-VMD2-hMERTKRecombinant
Completed
- Retinal Disease
- Retinitis Pigmentosa
- Subretinal administration of rAAV2-VMD2-hMERTKRecombinant Adeno-Associated Virus
-
Riyadh, Saudi ArabiaKing Khaled Eye Specialist Hospital
Jan 25, 2022
Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)
Terminated
- Mucopolysaccharidosis Type 3 B
- rAAV9.CMV.hNAGLU
-
Columbus, Ohio
- +3 more
Apr 29, 2022
MPS I Trial in Oakland (SB-318)
Terminated
- MPS I
- SB-318
-
Oakland, CaliforniaUCSF Benioff Children's Hospital Oakland
Jan 6, 2023
Danon Disease Trial in La Jolla, Philadelphia (RP-A501)
Recruiting
- Danon Disease
- RP-A501
-
La Jolla, California
- +1 more
Oct 17, 2023
Huntington Disease Trial in Germany, Poland, United Kingdom (intra-striatal rAAV5-miHTT)
Recruiting
- Huntington Disease
- intra-striatal rAAV5-miHTT
-
Düsseldorf, Germany
- +5 more
Feb 17, 2022
Pompe Disease Trial in Gainesville (genetic, drug, other)
Completed
- Pompe Disease
- Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase
- +7 more
-
Gainesville, FloridaClinical and Translational Research Building (CTRB), University
Mar 24, 2022
Osteoarthritis, Knee, Osteo Arthritis Knee, Knee Osteoarthritis Trial (GNSC-001, transient immune-modulation, Placebo)
Not yet recruiting
- Osteoarthritis, Knee
- +9 more
- GNSC-001
- +2 more
- (no location specified)
Apr 19, 2023
Amaurosis of Leber, Retinal Diseases Trial in Gainesville, Philadelphia (rAAV2-CBSB-hRPE65)
Active, not recruiting
- Amaurosis of Leber
- Retinal Diseases
- rAAV2-CBSB-hRPE65
-
Gainesville, Florida
- +1 more
Dec 13, 2021
Bietti's Crystalline Dystrophy Trial in Beijing (Gene Replacement Therapy by rAAV2/8-hCYP4V2)
Recruiting
- Bietti's Crystalline Dystrophy
- Gene Replacement Therapy by rAAV2/8-hCYP4V2
-
Beijing, Beijing, ChinaBeijing Tongren Hospital
May 6, 2021
Study of Patients With MPS IIIB Treated With ABO-101
Terminated
- Mucopolysaccharidosis III-B
- ABO-101
-
Columbus, Ohio
- +2 more
May 25, 2022
Choroideremia Trial in Edmonton (rAAV2.REP1 vector)
Completed
- Choroideremia
- rAAV2.REP1 vector
-
Edmonton, Alberta, CanadaUniversity of Alberta
May 16, 2022
X-Linked Retinitis Pigmentosa Trial in United States (rAAV2tYF-GRK1-RPGR)
Recruiting
- X-Linked Retinitis Pigmentosa
- rAAV2tYF-GRK1-RPGR
-
Jacksonville, Florida
- +6 more
Jul 13, 2021
Mucopolysaccharidosis II, MPS II Trial in United States (SB-913)
Terminated
- Mucopolysaccharidosis II
- MPS II
- SB-913
-
Oakland, California
- +4 more
Oct 21, 2022
Huntington Disease Trial in United States (intra-striatal rAAV5-miHTT, Imitation (sham) surgery)
Recruiting
- Huntington Disease
- intra-striatal rAAV5-miHTT
- Imitation (sham) surgery
-
Birmingham, Alabama
- +11 more
Dec 2, 2021