sapropterin
Showing 1 - 25 of 58
Claudication, Intermittent, Peripheral Artery Disease, Peripheral Vascular Diseases Trial in Worcester (Tetrahydrobiopterin 10
Recruiting
- Claudication, Intermittent
- +2 more
- Tetrahydrobiopterin 10 mg/kg
- +3 more
-
Worcester, MassachusettsUMASS Memorial Healthcare - University Campus
Nov 2, 2022
Head and Neck Squamous Cell Carcinoma Trial (Sapropterin diHCl tablets)
Not yet recruiting
- Head and Neck Squamous Cell Carcinoma
- Sapropterin dihydrochloride tablets
- (no location specified)
Mar 17, 2022
Phenylketonuria Trial in Fargo (sapropterin diHCl, Moxifloxacin, Moxifloxacin )
Completed
- Phenylketonuria
- sapropterin dihydrochloride
- +2 more
-
Fargo, North DakotaPRACS Institute, Ltd.
Jul 19, 2021
Schizo Affective Disorder, Schizophrenia Trial in Worcester (L-arginine, Sapropterin DiHCl)
Withdrawn
- Schizo Affective Disorder
- Schizophrenia
- L-arginine
- Sapropterin Dihydrochloride
-
Worcester, MassachusettsUMass Medical School
Jan 4, 2022
Endothelial Dysfunction Trial in Hackensack (Sapropterin DiHCl, Sapropterin DiHCl and Vitamin C)
Completed
- Endothelial Dysfunction
- Sapropterin Dihydrochloride
- Sapropterin Dihydrochloride and Vitamin C
-
Hackensack, New Jersey(unnamed)
Apr 22, 2021
Intermittent Claudication Trial in Argentina, United States (Placebo, Sapropterin DiHCl)
Completed
- Intermittent Claudication
- Placebo
- Sapropterin Dihydrochloride
-
Scottsdale, Arizona
- +19 more
Dec 14, 2020
COPD (COPD) Trial in Augusta (Tetrahydrobiopterin (BH4), Antioxidant Cocktail)
Completed
- Chronic Obstructive Pulmonary Disease (COPD)
- Tetrahydrobiopterin (BH4)
- Antioxidant Cocktail
-
Augusta, GeorgiaGeorgia Prevention Institute
Feb 5, 2021
Sickle Cell Disease Trial in United States (Sapropterin DiHCl)
Completed
- Sickle Cell Disease
- Sapropterin Dihydrochloride
-
Washington, District of Columbia
- +11 more
Feb 3, 2021
Peripheral Artery Disease, Peripheral Arterial Disease Trial (Sapropterin DiHCl (BH4, tetrahydrobiopterin), Placebo)
Withdrawn
- Peripheral Artery Disease
- Peripheral Arterial Disease
- Sapropterin Dihydrochloride (BH4, tetrahydrobiopterin)
- Placebo
- (no location specified)
Nov 24, 2020
Phenylketonuria Trial in Canada, United States (sapropterin diHCl)
Completed
- Phenylketonuria
- sapropterin dihydrochloride
-
La Jolla, California
- +18 more
Dec 1, 2020
PKUDOS: Phenylketonuria Demographic, Outcomes, and Safety
Completed
- Phenylketonuria
- Hyperphenylalaninaemia
-
Los Angeles, California
- +44 more
Oct 11, 2022
Gastroparesis Trial in Stanford (sapropterin diHCl)
Completed
- Gastroparesis
- sapropterin dihydrochloride
-
Stanford, CaliforniaStanford University School of Medicine
Sep 6, 2019
Behavioral Manifestations of Lesch-Nyhan Disease Trial in San Diego (sapropterin)
Withdrawn
- Behavioral Manifestations of Lesch-Nyhan Disease
- sapropterin
-
San Diego, CaliforniaUCSD Mitochondrial and Metabolic Disease Center
Jul 31, 2019
Phenylketonuria Trial in Miami (Kuvan, Diet)
Completed
- Phenylketonuria
- Kuvan
- Diet
-
Miami, FloridaDepartment of Biochemistry & Molecular Biology
Nov 19, 2019
Nutritional Status in Phenylketonuria
Completed
- Phenylketonurias
- Diet
- Sapropterin
-
Porto, PortugalCentro Hospitalar Universitário do Porto
Sep 9, 2019
Alzheimer's Disease Trial in Worcester (Simvastatin, L-Arginine, Tetrahydrobiopterin)
Completed
- Alzheimer's Disease
- Simvastatin
- +2 more
-
Worcester, MassachusettsUMass Medical School/ UMass Memorial Medical Center
Jul 11, 2019
Simple Breath Test to Examine Phenylalanine Metabolism
Completed
- Phenylketonuria (PKU)
-
Vancouver, British Columbia, CanadaChild & Family Research Institute
Sep 22, 2020
Heart Failure, Cardiovascular Disease Trial in Providence (Kuvan)
Completed
- Heart Failure
- Cardiovascular Disease
-
Providence, Rhode IslandProvidence VAMC
Jan 28, 2019
Executive Function, Neurotransmitter Function and Genomic
Completed
- Phenylketonuria
- +2 more
- sapropterin dihydrochloride
-
New Orleans, LouisianaTulane University Health Science Center
Sep 13, 2018
Sapropterin in Individuals With Phenylketonuria
Completed
- Phenylketonuria
- Sapropterin (Kuvan)
-
Saint Louis, MissouriWashington University
Jun 15, 2018
Radiation Enteritis Trial in Chengdu (Tetrahydrobiopterin)
Recruiting
- Radiation Enteritis
-
Chengdu, Sichuan, Chinaest China Second Hospital of Sichuan University
Feb 25, 2022
Radiation-Induced Dermatitis Trial in Chengdu (Tetrahydrobiopterin)
Not yet recruiting
- Radiation-Induced Dermatitis
-
Chengdu, Sichuan, Chinaest China Second Hospital of Sichuan University
Feb 25, 2022
Phenylketonuria Trial in Pittsburgh (radiation, procedure, drug, other, behavioral, diagnostic test)
Recruiting
- Phenylketonuria
- Preparative Radiation Therapy
- +6 more
-
Pittsburgh, Pennsylvania
- +1 more
Jan 9, 2023
Autistic Disorder Trial in Palo Alto (sapropterin, Placebo)
Completed
- Autistic Disorder
- sapropterin
- Placebo
-
Palo Alto, CaliforniaThe Children's Health Council
Apr 27, 2018