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sapropterin

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STUDY
CONDITIONS
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Claudication, Intermittent, Peripheral Artery Disease, Peripheral Vascular Diseases Trial in Worcester (Tetrahydrobiopterin 10

Recruiting
  • Claudication, Intermittent
  • +2 more
  • Tetrahydrobiopterin 10 mg/kg
  • +3 more
  • Worcester, Massachusetts
    UMASS Memorial Healthcare - University Campus
Nov 2, 2022

Head and Neck Squamous Cell Carcinoma Trial (Sapropterin diHCl tablets)

Not yet recruiting
  • Head and Neck Squamous Cell Carcinoma
  • Sapropterin dihydrochloride tablets
  • (no location specified)
Mar 17, 2022

Phenylketonuria Trial in Fargo (sapropterin diHCl, Moxifloxacin, Moxifloxacin )

Completed
  • Phenylketonuria
  • sapropterin dihydrochloride
  • +2 more
  • Fargo, North Dakota
    PRACS Institute, Ltd.
Jul 19, 2021

Schizo Affective Disorder, Schizophrenia Trial in Worcester (L-arginine, Sapropterin DiHCl)

Withdrawn
  • Schizo Affective Disorder
  • Schizophrenia
  • Worcester, Massachusetts
    UMass Medical School
Jan 4, 2022

Endothelial Dysfunction Trial in Hackensack (Sapropterin DiHCl, Sapropterin DiHCl and Vitamin C)

Completed
  • Endothelial Dysfunction
  • Sapropterin Dihydrochloride
  • Sapropterin Dihydrochloride and Vitamin C
  • Hackensack, New Jersey
    (unnamed)
Apr 22, 2021

Intermittent Claudication Trial in Argentina, United States (Placebo, Sapropterin DiHCl)

Completed
  • Intermittent Claudication
  • Placebo
  • Sapropterin Dihydrochloride
  • Scottsdale, Arizona
  • +19 more
Dec 14, 2020

Renal Insufficiency, Chronic Trial in Atlanta, Decatur (drug, other, dietary supplement)

Recruiting
  • Renal Insufficiency, Chronic
  • Atlanta, Georgia
  • +2 more
Jan 20, 2022

COPD (COPD) Trial in Augusta (Tetrahydrobiopterin (BH4), Antioxidant Cocktail)

Completed
  • Chronic Obstructive Pulmonary Disease (COPD)
  • Tetrahydrobiopterin (BH4)
  • Antioxidant Cocktail
  • Augusta, Georgia
    Georgia Prevention Institute
Feb 5, 2021

Sickle Cell Disease Trial in United States (Sapropterin DiHCl)

Completed
  • Sickle Cell Disease
  • Sapropterin Dihydrochloride
  • Washington, District of Columbia
  • +11 more
Feb 3, 2021

Peripheral Artery Disease, Peripheral Arterial Disease Trial (Sapropterin DiHCl (BH4, tetrahydrobiopterin), Placebo)

Withdrawn
  • Peripheral Artery Disease
  • Peripheral Arterial Disease
  • Sapropterin Dihydrochloride (BH4, tetrahydrobiopterin)
  • Placebo
  • (no location specified)
Nov 24, 2020

Phenylketonuria Trial in Canada, United States (sapropterin diHCl)

Completed
  • Phenylketonuria
  • sapropterin dihydrochloride
  • La Jolla, California
  • +18 more
Dec 1, 2020

PKUDOS: Phenylketonuria Demographic, Outcomes, and Safety

Completed
  • Phenylketonuria
  • Hyperphenylalaninaemia
  • Los Angeles, California
  • +44 more
Oct 11, 2022

Gastroparesis Trial in Stanford (sapropterin diHCl)

Completed
  • Gastroparesis
  • sapropterin dihydrochloride
  • Stanford, California
    Stanford University School of Medicine
Sep 6, 2019

Behavioral Manifestations of Lesch-Nyhan Disease Trial in San Diego (sapropterin)

Withdrawn
  • Behavioral Manifestations of Lesch-Nyhan Disease
  • sapropterin
  • San Diego, California
    UCSD Mitochondrial and Metabolic Disease Center
Jul 31, 2019

Phenylketonuria Trial in Miami (Kuvan, Diet)

Completed
  • Phenylketonuria
  • Miami, Florida
    Department of Biochemistry & Molecular Biology
Nov 19, 2019

Nutritional Status in Phenylketonuria

Completed
  • Phenylketonurias
  • Diet
  • Sapropterin
  • Porto, Portugal
    Centro Hospitalar Universitário do Porto
Sep 9, 2019

Alzheimer's Disease Trial in Worcester (Simvastatin, L-Arginine, Tetrahydrobiopterin)

Completed
  • Alzheimer's Disease
  • Worcester, Massachusetts
    UMass Medical School/ UMass Memorial Medical Center
Jul 11, 2019

Simple Breath Test to Examine Phenylalanine Metabolism

Completed
  • Phenylketonuria (PKU)
    • Vancouver, British Columbia, Canada
      Child & Family Research Institute
    Sep 22, 2020

    Heart Failure, Cardiovascular Disease Trial in Providence (Kuvan)

    Completed
    • Heart Failure
    • Cardiovascular Disease
    • Providence, Rhode Island
      Providence VAMC
    Jan 28, 2019

    Executive Function, Neurotransmitter Function and Genomic

    Completed
    • Phenylketonuria
    • +2 more
    • sapropterin dihydrochloride
    • New Orleans, Louisiana
      Tulane University Health Science Center
    Sep 13, 2018

    Sapropterin in Individuals With Phenylketonuria

    Completed
    • Phenylketonuria
    • Sapropterin (Kuvan)
    • Saint Louis, Missouri
      Washington University
    Jun 15, 2018

    Radiation Enteritis Trial in Chengdu (Tetrahydrobiopterin)

    Recruiting
    • Radiation Enteritis
    • Chengdu, Sichuan, China
      est China Second Hospital of Sichuan University
    Feb 25, 2022

    Radiation-Induced Dermatitis Trial in Chengdu (Tetrahydrobiopterin)

    Not yet recruiting
    • Radiation-Induced Dermatitis
    • Chengdu, Sichuan, China
      est China Second Hospital of Sichuan University
    Feb 25, 2022

    Phenylketonuria Trial in Pittsburgh (radiation, procedure, drug, other, behavioral, diagnostic test)

    Recruiting
    • Phenylketonuria
    • Preparative Radiation Therapy
    • +6 more
    • Pittsburgh, Pennsylvania
    • +1 more
    Jan 9, 2023

    Autistic Disorder Trial in Palo Alto (sapropterin, Placebo)

    Completed
    • Autistic Disorder
    • sapropterin
    • Placebo
    • Palo Alto, California
      The Children's Health Council
    Apr 27, 2018