severe congenital neutropenia

Showing 1 - 8 of 8

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Baby Detect : Genomic Newborn Screening

Recruiting
  • Congenital Adrenal Hyperplasia
  • +126 more
    • Liege, Wallonia, Belgium
      CRMN, Hôpital La Citadelle
    Jan 24, 2023

    Severe Congenital Neutropenia, GATA2 Deficiency Trial in Moscow (conditioning with TLI)

    Not yet recruiting
    • Severe Congenital Neutropenia
    • GATA2 Deficiency
    • conditioning with TLI
    • Moscow, Russian Federation
      HSCT department
    Apr 9, 2021

    Bone Marrow Failure Syndrome, Severe Aplastic Anemia, Severe Congenital Neutropenia Trial in New York (CD34 Stem Cell Selection

    Active, not recruiting
    • Bone Marrow Failure Syndrome
    • +15 more
    • CD34 Stem Cell Selection Therapy
    • New York, New York
      Morgan Stanley Children's Hospital, New York-Presbyterian, Colum
    Jun 17, 2020

    Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)

    Completed
    • Hurler Syndrome
    • +14 more
    • Atlanta, Georgia
      Children's Healthcare of Atlanta
    Dec 20, 2019

    Accelerated Phase Chronic Myelogenous Leukemia, Adult Acute Lymphoblastic Leukemia in Remission, Adult Acute Myeloid Leukemia in

    Completed
    • Accelerated Phase Chronic Myelogenous Leukemia
    • +77 more
    • fludarabine phosphate
    • +8 more
    • Buffalo, New York
      Roswell Park Cancer Institute
    Sep 16, 2019

    Congenital Amegakaryocytic Thrombocytopenia, Diamond-blackfan Anemia, Leukemia Trial in San Francisco, Madison (biological,

    Completed
    • Congenital Amegakaryocytic Thrombocytopenia
    • +4 more
    • alemtuzumab
    • +9 more
    • San Francisco, California
    • +1 more
    Aug 30, 2017

    Congenital Amegakaryocytic Thrombocytopenia, Leukemia, MDS Trial in San Francisco, Chapel Hill (biological, drug, procedure,

    Completed
    • Congenital Amegakaryocytic Thrombocytopenia
    • +3 more
    • anti-thymocyte globulin
    • +7 more
    • San Francisco, California
    • +1 more
    Nov 8, 2012

    Congenital Amegakaryocytic Thrombocytopenia, Diamond-blackfan Anemia, Fanconi Anemia Trial in San Francisco (biological, drug,

    Completed
    • Congenital Amegakaryocytic Thrombocytopenia
    • +5 more
    • anti-thymocyte globulin
    • +6 more
    • San Francisco, California
      UCSF Comprehensive Cancer Center
    Nov 8, 2012