sphingolipidoses
Showing 1 - 6 of 6
Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD
Recruiting
- Mucopolysaccharidosis Disorders
- +28 more
- Stem Cell Transplantation
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Nov 1, 2022
Sphingolipidoses, Enzyme Deficiency Trial in San Francisco (no intervention)
Recruiting
- Sphingolipidoses
- Enzyme Deficiency
- no intervention
-
San Francisco, CaliforniaUniversity of California San Francisco
Jul 1, 2022
Lyso-Gb1 as a Long-term Prognostic Biomarker in Gaucher Disease
Completed
- Lysosomal Storage Diseases
- +2 more
-
Tirana, Albania
- +7 more
May 27, 2021
Children With Metachromatic Leukodystrophy
Terminated
- Lipid Metabolism Disorders
- +13 more
-
Torrance, California
- +13 more
Mar 16, 2021
Mucopolysaccharidosis, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Campath-1H, Cyclophosphamide, Busulfan)
Completed
- Mucopolysaccharidosis
- +12 more
- Campath-1H
- +5 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Jan 9, 2018
Hurler's Syndrome, Maroteaux-Lamy Syndrome, Sly Syndrome Trial in Minneapolis (Stem Cell Transplantation, Cyclophosphamide,
Terminated
- Hurler's Syndrome
- +10 more
- Stem Cell Transplantation
- +3 more
-
Minneapolis, MinnesotaUniversity of Minnesota, Fairview
Dec 3, 2017