sphingolipidoses

Showing 1 - 6 of 6

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

Recruiting
  • Mucopolysaccharidosis Disorders
  • +28 more
  • Stem Cell Transplantation
  • +7 more
  • Minneapolis, Minnesota
    Masonic Cancer Center, University of Minnesota
Nov 1, 2022

Sphingolipidoses, Enzyme Deficiency Trial in San Francisco (no intervention)

Recruiting
  • Sphingolipidoses
  • Enzyme Deficiency
  • no intervention
  • San Francisco, California
    University of California San Francisco
Jul 1, 2022

Lyso-Gb1 as a Long-term Prognostic Biomarker in Gaucher Disease

Completed
  • Lysosomal Storage Diseases
  • +2 more
    • Tirana, Albania
    • +7 more
    May 27, 2021

    Children With Metachromatic Leukodystrophy

    Terminated
    • Lipid Metabolism Disorders
    • +13 more
      • Torrance, California
      • +13 more
      Mar 16, 2021

      Mucopolysaccharidosis, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Campath-1H, Cyclophosphamide, Busulfan)

      Completed
      • Mucopolysaccharidosis
      • +12 more
      • Minneapolis, Minnesota
        Masonic Cancer Center, University of Minnesota
      Jan 9, 2018

      Hurler's Syndrome, Maroteaux-Lamy Syndrome, Sly Syndrome Trial in Minneapolis (Stem Cell Transplantation, Cyclophosphamide,

      Terminated
      • Hurler's Syndrome
      • +10 more
      • Stem Cell Transplantation
      • +3 more
      • Minneapolis, Minnesota
        University of Minnesota, Fairview
      Dec 3, 2017