City

Minneapolis (3)

Montreal (1)

Tampa (1)

Overall Status

Completed (4)

Phase

n/a (1)

phase 2 (1)

phase 2/phase 3 (1)

Sponsor

Masonic Cancer Center, University of Minnesota (2)

McGill University Health Centre/Research Institute of the McGill University Health Centre (1)

University of Minnesota (1)

Collaborator

National Center for Advancing Translational Sciences (NCATS) (1)

National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) (1)

National Institute of Neurological Disorders and Stroke (NINDS) (1)

Rare Diseases Clinical Research Network (1)

Study Documents

Intervention Type

drug (2)

procedure (2)

biological (1)

device (1)

other (1)

Funder Type

Other (4)

Study Type

Interventional (3)

Observational (1)

tay sachs disease

Showing 1 - 4 of 4

Trials per page:

STUDY

CONDITIONS

INTERVENTIONS

LOCATIONS

LAST UPDATED

Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (drug, procedure,

Completed

Has Results

Adrenoleukodystrophy
+8 more

Clofarabine
+7 more

Minneapolis, Minnesota

Masonic Cancer Center, University of Minnesota

Jul 10, 2019

Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (Stem Cell Transplant,

Completed

Has Results

Adrenoleukodystrophy
+10 more

Stem Cell Transplant
Busulfan, Cyclophosphamide, Antithymocyte Globulin

Minneapolis, Minnesota

Masonic Cancer Center, University of Minnesota

Dec 3, 2017

Tay Sachs Disease, Canavan Disease, Familial Dysautonomia Trial in Montreal (Online pre-test genetic education tool)

Completed

Tay Sachs Disease
+2 more

Online pre-test genetic education tool

Montreal, Quebec, Canada

Montreal General Hospital (MUHC)

Aug 14, 2017

Gene Therapy for Tay-Sachs Disease

Completed

Tay Sachs Disease
+2 more

Tampa, Florida
+1 more

Dec 3, 2014