Fanconi Anemia
Showing 26 - 50 of 53
Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
Enrolling by invitation
- Fanconi Anemia Complementation Group A
- Fanconi Anemia
- Safety and efficacy assessments
-
Madrid, SpainHospital Infantil Universitario Niño Jesús (HIUNJ)
Jun 18, 2020
Chronic Myeloproliferative Disorders, Leukemia, Lymphoma Trial in Buffalo (biological, drug, procedure)
Completed
- Chronic Myeloproliferative Disorders
- +7 more
- anti-thymocyte globulin
- +11 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Jan 29, 2020
Acute Myeloid Leukemia in Remission, de Novo Myelodysplastic Syndrome, Fanconi Anemia Trial in Brazil, United States (procedure,
Completed
- Acute Myeloid Leukemia in Remission
- +3 more
- Allogeneic Bone Marrow Transplantation
- +7 more
-
Oakland, California
- +4 more
Jan 17, 2020
Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)
Completed
- Hurler Syndrome
- +14 more
-
Atlanta, GeorgiaChildren's Healthcare of Atlanta
Dec 20, 2019
Accelerated Phase Chronic Myelogenous Leukemia, Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic
Completed
- Accelerated Phase Chronic Myelogenous Leukemia
- +99 more
- fludarabine phosphate
- +4 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Oct 30, 2019
Fanconi Anemia Trial in Beijing, Shenzhen (Gene-modified autologous stem cells)
Unknown status
- Fanconi Anemia
- Gene-modified autologous stem cells
-
Beijing, Beijing, China
- +2 more
Sep 18, 2019
Fanconi Anemia Trial in Milwaukee (CliniMACs device, Busulfan, Fludarabine)
Completed
- Fanconi Anemia
- CliniMACs device
- +4 more
-
Milwaukee, WisconsinMedical College of Wisconsin
Sep 3, 2019
Fanconi Anemia, Dyskeratosis Congenita Trial in Boston (danazol)
Terminated
- Fanconi Anemia
- Dyskeratosis Congenita
-
Boston, MassachusettsChildren's Hospital Boston
Jan 31, 2019
Fanconi Anemia, Severe Aplastic Anemia Trial in Houston (biological, drug, procedure)
Terminated
- Fanconi Anemia
- Severe Aplastic Anemia
- CAMPATH-1H
- +3 more
-
Houston, Texas
- +1 more
Apr 26, 2018
Tissue Sample Collection From Patients With Fanconi Anemia
Completed
- Fanconi Anemia
- +2 more
- biologic sample preservation procedure
- biopsy
-
Portland, OregonKnight Cancer Institute at Oregon Health and Science University
Nov 30, 2017
Gene Function in Bone Marrow Cells From Fanconi Anemia and From
Terminated
- Fanconi Anemia
- microarray analysis
- biopsy
-
Portland, OregonKnight Cancer Institute at Oregon Health and Science University
Nov 30, 2017
Chronic Myeloproliferative Disorders, Diamond-blackfan Anemia, Fanconi Anemia Trial in Minneapolis (anti-thymocyte globulin,
Terminated
- Chronic Myeloproliferative Disorders
- +8 more
- anti-thymocyte globulin
- +9 more
-
Minneapolis, MinnesotaUniversity of Minnesota Cancer Center
Nov 27, 2017
Fanconi Anemia Trial in Los Angeles (CD34+ selected cells)
Withdrawn
- Fanconi Anemia
- CD34+ selected cells
-
Los Angeles, CaliforniaChildren's Hospital Los Angeles
Jul 6, 2017
Fanconi Anemia Trial in Cincinnati (Retrovirus Construct)
Completed
- Fanconi Anemia
- Retrovirus Construct
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Jun 21, 2017
Adult Acute Myeloid Leukemia in Remission, Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities, Adult Acute Myeloid
Completed
- Adult Acute Myeloid Leukemia in Remission
- +10 more
- fludarabine phosphate
- +6 more
-
Chicago, Illinois
- +4 more
Feb 16, 2017
Fanconi Anemia Trial in New York (Cyclophosphamide, Fludarabine, Total body irradiation (TBI))
Completed
- Fanconi Anemia
- Cyclophosphamide
- +2 more
-
New York, New YorkMemorial Sloan Kettering Cancer Center
Jun 29, 2016
Fanconi Anemia Trial in Cincinnati (PBSC Collection, Bone Marrow Harvest, CliniMacs Cell Selection System)
Completed
- Fanconi Anemia
- PBSC Collection
- +2 more
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Jul 11, 2016
de Novo Fanconi Anemia in Younger Newly Diagnosed Acute Myeloid
Completed
- Childhood Acute Erythroleukemia (M6)
- +17 more
- laboratory biomarker analysis
-
Monrovia, CaliforniaChildren's Oncology Group
May 13, 2016
Anemia, Aplastic, Fanconi Anemia, Hematologic Diseases Trial (stem cell transplantation)
Completed
- Anemia, Aplastic
- +7 more
- stem cell transplantation
- (no location specified)
Apr 12, 2016
Immune Function in Young Cytopenia That Did Not Respond to
Completed
- Dyskeratosis Congenita
- +4 more
- polymerase chain reaction
- +3 more
-
Vienna, Austria
- +9 more
Jan 15, 2015
FANCONI ANEMIA Trial in Houston (procedure, drug, biological)
Terminated
- FANCONI ANEMIA
- CD34 selected haploidentical PBSCT
- +4 more
-
Houston, Texas
- +1 more
Mar 3, 2014
Childhood Langerhans Cell Histiocytosis, Fanconi Anemia, Leukemia Trial in Hershey (biological, drug, radiation)
Unknown status
- Childhood Langerhans Cell Histiocytosis
- +7 more
- anti-thymocyte globulin
- +6 more
-
Hershey, PennsylvaniaPenn State Hershey Cancer Institute at Milton S. Hershey Medical
Jan 9, 2014
Fanconi Anemia, Autosomal or Sex Linked Recessive Genetic Disease, Bone Marrow Hematopoiesis Failure, Multiple Congenital
Available
- Fanconi Anemia
- +3 more
- human whole exome
- whole genomic
-
Tianjin, Tianjin, ChinaInstitute of Hematology & Blood Diseases Hospital
Nov 21, 2013
Congenital Amegakaryocytic Thrombocytopenia, Diamond-blackfan Anemia, Fanconi Anemia Trial in San Francisco (biological, drug,
Completed
- Congenital Amegakaryocytic Thrombocytopenia
- +5 more
- anti-thymocyte globulin
- +6 more
-
San Francisco, CaliforniaUCSF Comprehensive Cancer Center
Nov 8, 2012