Fanconi Anemia

Showing 26 - 50 of 53

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy

Enrolling by invitation
  • Fanconi Anemia Complementation Group A
  • Fanconi Anemia
  • Safety and efficacy assessments
  • Madrid, Spain
    Hospital Infantil Universitario Niño Jesús (HIUNJ)
Jun 18, 2020

Fanconi Anemia Trial in Barcelona, Madrid (filgrastim, plerixafor)

Completed
  • Fanconi Anemia
  • Barcelona, Spain
  • +1 more
May 25, 2020

Chronic Myeloproliferative Disorders, Leukemia, Lymphoma Trial in Buffalo (biological, drug, procedure)

Completed
  • Chronic Myeloproliferative Disorders
  • +7 more
  • anti-thymocyte globulin
  • +11 more
  • Buffalo, New York
    Roswell Park Cancer Institute
Jan 29, 2020

Acute Myeloid Leukemia in Remission, de Novo Myelodysplastic Syndrome, Fanconi Anemia Trial in Brazil, United States (procedure,

Completed
  • Acute Myeloid Leukemia in Remission
  • +3 more
  • Allogeneic Bone Marrow Transplantation
  • +7 more
  • Oakland, California
  • +4 more
Jan 17, 2020

Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)

Completed
  • Hurler Syndrome
  • +14 more
  • Atlanta, Georgia
    Children's Healthcare of Atlanta
Dec 20, 2019

Accelerated Phase Chronic Myelogenous Leukemia, Acute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic

Completed
  • Accelerated Phase Chronic Myelogenous Leukemia
  • +99 more
  • fludarabine phosphate
  • +4 more
  • Buffalo, New York
    Roswell Park Cancer Institute
Oct 30, 2019

Fanconi Anemia Trial in Beijing, Shenzhen (Gene-modified autologous stem cells)

Unknown status
  • Fanconi Anemia
  • Gene-modified autologous stem cells
  • Beijing, Beijing, China
  • +2 more
Sep 18, 2019

Fanconi Anemia Trial in Milwaukee (CliniMACs device, Busulfan, Fludarabine)

Completed
  • Fanconi Anemia
  • CliniMACs device
  • +4 more
  • Milwaukee, Wisconsin
    Medical College of Wisconsin
Sep 3, 2019

Fanconi Anemia, Dyskeratosis Congenita Trial in Boston (danazol)

Terminated
  • Fanconi Anemia
  • Dyskeratosis Congenita
  • Boston, Massachusetts
    Children's Hospital Boston
Jan 31, 2019

Fanconi Anemia, Severe Aplastic Anemia Trial in Houston (biological, drug, procedure)

Terminated
  • Fanconi Anemia
  • Severe Aplastic Anemia
  • CAMPATH-1H
  • +3 more
  • Houston, Texas
  • +1 more
Apr 26, 2018

Tissue Sample Collection From Patients With Fanconi Anemia

Completed
  • Fanconi Anemia
  • +2 more
  • biologic sample preservation procedure
  • biopsy
  • Portland, Oregon
    Knight Cancer Institute at Oregon Health and Science University
Nov 30, 2017

Gene Function in Bone Marrow Cells From Fanconi Anemia and From

Terminated
  • Fanconi Anemia
  • microarray analysis
  • biopsy
  • Portland, Oregon
    Knight Cancer Institute at Oregon Health and Science University
Nov 30, 2017

Chronic Myeloproliferative Disorders, Diamond-blackfan Anemia, Fanconi Anemia Trial in Minneapolis (anti-thymocyte globulin,

Terminated
  • Chronic Myeloproliferative Disorders
  • +8 more
  • anti-thymocyte globulin
  • +9 more
  • Minneapolis, Minnesota
    University of Minnesota Cancer Center
Nov 27, 2017

Fanconi Anemia Trial in Los Angeles (CD34+ selected cells)

Withdrawn
  • Fanconi Anemia
  • CD34+ selected cells
  • Los Angeles, California
    Children's Hospital Los Angeles
Jul 6, 2017

Fanconi Anemia Trial in Cincinnati (Retrovirus Construct)

Completed
  • Fanconi Anemia
  • Retrovirus Construct
  • Cincinnati, Ohio
    Cincinnati Children's Hospital Medical Center
Jun 21, 2017

Adult Acute Myeloid Leukemia in Remission, Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities, Adult Acute Myeloid

Completed
  • Adult Acute Myeloid Leukemia in Remission
  • +10 more
  • fludarabine phosphate
  • +6 more
  • Chicago, Illinois
  • +4 more
Feb 16, 2017

Fanconi Anemia Trial in New York (Cyclophosphamide, Fludarabine, Total body irradiation (TBI))

Completed
  • Fanconi Anemia
  • New York, New York
    Memorial Sloan Kettering Cancer Center
Jun 29, 2016

Fanconi Anemia Trial in Cincinnati (PBSC Collection, Bone Marrow Harvest, CliniMacs Cell Selection System)

Completed
  • Fanconi Anemia
  • PBSC Collection
  • +2 more
  • Cincinnati, Ohio
    Cincinnati Children's Hospital Medical Center
Jul 11, 2016

de Novo Fanconi Anemia in Younger Newly Diagnosed Acute Myeloid

Completed
  • Childhood Acute Erythroleukemia (M6)
  • +17 more
  • laboratory biomarker analysis
  • Monrovia, California
    Children's Oncology Group
May 13, 2016

Anemia, Aplastic, Fanconi Anemia, Hematologic Diseases Trial (stem cell transplantation)

Completed
  • Anemia, Aplastic
  • +7 more
  • stem cell transplantation
  • (no location specified)
Apr 12, 2016

Immune Function in Young Cytopenia That Did Not Respond to

Completed
  • Dyskeratosis Congenita
  • +4 more
  • polymerase chain reaction
  • +3 more
  • Vienna, Austria
  • +9 more
Jan 15, 2015

FANCONI ANEMIA Trial in Houston (procedure, drug, biological)

Terminated
  • FANCONI ANEMIA
  • CD34 selected haploidentical PBSCT
  • +4 more
  • Houston, Texas
  • +1 more
Mar 3, 2014

Childhood Langerhans Cell Histiocytosis, Fanconi Anemia, Leukemia Trial in Hershey (biological, drug, radiation)

Unknown status
  • Childhood Langerhans Cell Histiocytosis
  • +7 more
  • anti-thymocyte globulin
  • +6 more
  • Hershey, Pennsylvania
    Penn State Hershey Cancer Institute at Milton S. Hershey Medical
Jan 9, 2014

Fanconi Anemia, Autosomal or Sex Linked Recessive Genetic Disease, Bone Marrow Hematopoiesis Failure, Multiple Congenital

Available
  • Fanconi Anemia
  • +3 more
  • human whole exome
  • whole genomic
  • Tianjin, Tianjin, China
    Institute of Hematology & Blood Diseases Hospital
Nov 21, 2013

Congenital Amegakaryocytic Thrombocytopenia, Diamond-blackfan Anemia, Fanconi Anemia Trial in San Francisco (biological, drug,

Completed
  • Congenital Amegakaryocytic Thrombocytopenia
  • +5 more
  • anti-thymocyte globulin
  • +6 more
  • San Francisco, California
    UCSF Comprehensive Cancer Center
Nov 8, 2012