gene therapy

Showing 1 - 11 of 11

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Transfusion-dependent Beta-thalassemia After Gene Therapy

Recruiting
  • Transfusion-dependent Beta-Thalassemia
  • Gene Therapy
  • Gene therapy
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Aug 6, 2023

CIBMTR Research Database

Recruiting
  • Autologous Stem Cell Transplantation
  • +6 more
    • Minneapolis, Minnesota
    • +1 more
    Jan 20, 2023

    Hemophilia A, Gene Therapy, Clotting Disorders Trial in Johannesburg, London, Southampton (Valoctocogene Roxaparvovec)

    Recruiting
    • Hemophilia A
    • +3 more
    • Valoctocogene Roxaparvovec
    • Seoul, Korea, Republic of
    • +8 more
    Jan 6, 2023

    Hemophilia A, Gene Therapy Trial in Tianjin (Injection of GS001)

    Recruiting
    • Hemophilia A
    • Gene Therapy
    • Injection of GS001
    • Tianjin, Tianjin, China
      Chinese Academy of Medical Science and Blood Disease Hospital
    Sep 19, 2022

    Severe Combined Immunodeficiency, X Linked, Gene Therapy Trial in United Kingdom, United States (autologous CD34+ cell

    Recruiting
    • Severe Combined Immunodeficiency, X Linked
    • Gene Therapy
    • autologous CD34+ cell transduced with G2SCID vector
    • Los Angeles, California
    • +4 more
    Jul 19, 2022

    Knowledge, Beliefs, and Attitudes of Hemophilia B About Gene

    Recruiting
    • Gene Therapy
    • Hemophilia B
    • Interview
    • Memphis, Tennessee
      St. Jude Children's Research Hospital
    May 25, 2022

    Adeno-Associated Virus (AAV), Blood Coagulation Disorder, Blood Coagulation Disorders, Inherited Trial in United States

    Recruiting
    • Adeno-Associated Virus (AAV)
    • +16 more
    • SPK-8016
    • Los Angeles, California
    • +13 more
    Feb 3, 2022

    RGX-314 Administered in the Suprachoroidal Space for nAMD

    Enrolling by invitation
    • Neovascular Age-Related Macular Degeneration (nAMD)
    • +5 more
    • No intervention.
    • Phoenix, Arizona
    • +14 more
    Jan 14, 2022

    Dry Age-related Macular Degeneration, Geographic Atrophy, Gene Therapy Trial (Intravitreal AAVCAGsCD59, Intravitreal Sham

    Withdrawn
    • Dry Age-related Macular Degeneration
    • +3 more
    • Intravitreal AAVCAGsCD59
    • Intravitreal Sham Injection
    • (no location specified)
    May 6, 2021

    Gene Therapy Trial in Chongqing (Lentiviral Vector Gene Therapy)

    Recruiting
    • Gene Therapy
    • Lentiviral Vector Gene Therapy
    • Chongqing, Chongqing, China
      Children's Hospital of Chongqing Medical University
    Mar 26, 2020

    Macular Degeneration, Age-Related Maculopathies, Age-Related Maculopathy Trial in United States (AAV2-sFLT01)

    Completed
    • Macular Degeneration
    • +9 more
    • AAV2-sFLT01
    • Baltimore, Maryland
    • +3 more
    Aug 21, 2018