gene therapy
Showing 1 - 11 of 11
Transfusion-dependent Beta-thalassemia After Gene Therapy
Recruiting
- Transfusion-dependent Beta-Thalassemia
- Gene Therapy
- Gene therapy
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Aug 6, 2023
CIBMTR Research Database
Recruiting
- Autologous Stem Cell Transplantation
- +6 more
-
Minneapolis, Minnesota
- +1 more
Jan 20, 2023
Hemophilia A, Gene Therapy, Clotting Disorders Trial in Johannesburg, London, Southampton (Valoctocogene Roxaparvovec)
Recruiting
- Hemophilia A
- +3 more
- Valoctocogene Roxaparvovec
-
Seoul, Korea, Republic of
- +8 more
Jan 6, 2023
Hemophilia A, Gene Therapy Trial in Tianjin (Injection of GS001)
Recruiting
- Hemophilia A
- Gene Therapy
- Injection of GS001
-
Tianjin, Tianjin, ChinaChinese Academy of Medical Science and Blood Disease Hospital
Sep 19, 2022
Severe Combined Immunodeficiency, X Linked, Gene Therapy Trial in United Kingdom, United States (autologous CD34+ cell
Recruiting
- Severe Combined Immunodeficiency, X Linked
- Gene Therapy
- autologous CD34+ cell transduced with G2SCID vector
-
Los Angeles, California
- +4 more
Jul 19, 2022
Knowledge, Beliefs, and Attitudes of Hemophilia B About Gene
Recruiting
- Gene Therapy
- Hemophilia B
- Interview
-
Memphis, TennesseeSt. Jude Children's Research Hospital
May 25, 2022
Adeno-Associated Virus (AAV), Blood Coagulation Disorder, Blood Coagulation Disorders, Inherited Trial in United States
Recruiting
- Adeno-Associated Virus (AAV)
- +16 more
- SPK-8016
-
Los Angeles, California
- +13 more
Feb 3, 2022
RGX-314 Administered in the Suprachoroidal Space for nAMD
Enrolling by invitation
- Neovascular Age-Related Macular Degeneration (nAMD)
- +5 more
- No intervention.
-
Phoenix, Arizona
- +14 more
Jan 14, 2022
Dry Age-related Macular Degeneration, Geographic Atrophy, Gene Therapy Trial (Intravitreal AAVCAGsCD59, Intravitreal Sham
Withdrawn
- Dry Age-related Macular Degeneration
- +3 more
- Intravitreal AAVCAGsCD59
- Intravitreal Sham Injection
- (no location specified)
May 6, 2021
Gene Therapy Trial in Chongqing (Lentiviral Vector Gene Therapy)
Recruiting
- Gene Therapy
- Lentiviral Vector Gene Therapy
-
Chongqing, Chongqing, ChinaChildren's Hospital of Chongqing Medical University
Mar 26, 2020
Macular Degeneration, Age-Related Maculopathies, Age-Related Maculopathy Trial in United States (AAV2-sFLT01)
Completed
- Macular Degeneration
- +9 more
- AAV2-sFLT01
-
Baltimore, Maryland
- +3 more
Aug 21, 2018