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IPEX or IPEX-like Syndromes

Showing 26 - 50 of >10,000

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Lower Risk MDS Per IPSS-R Trial (Luspatercept)

Not yet recruiting
  • Lower Risk MDS Per IPSS-R
  • (no location specified)
Jun 21, 2023

Genetic Predisposition Trial in Philadelphia (Digital Care Plans)

Not yet recruiting
  • Genetic Predisposition
  • Digital Care Plans
  • Philadelphia, Pennsylvania
    Children's Hospital of Philadelphia
Feb 8, 2023

High Grade MDS Trial in Aurora (Omacetaxine, Azacitidine)

Recruiting
  • High Grade Myelodysplastic Syndromes
  • Aurora, Colorado
    Universtiy of Colorado Denver
Nov 17, 2022

Clinical Phenotypes and Outcomes of Ma2 Patient

Completed
  • Autoimmune Encephalitis
  • Paraneoplastic Syndromes
  • Diagnosis test
  • Lyon, France
    Centre de référence des syndromes neurologiques paranéoplasiques
Dec 8, 2022

BRCA1/2-Associated Hereditary Breast and Ovarian Cancer Syndrome, Breast Ductal Carcinoma In Situ, Hematopoietic and Lymphoid

Recruiting
  • BRCA1/2-Associated Hereditary Breast and Ovarian Cancer Syndrome
  • +5 more
  • Biospecimen Collection
  • +3 more
  • Portland, Oregon
  • +1 more
Feb 9, 2022

Iron Deficiency Anemia Trial in Australia, Israel, Romania (KER-047)

Recruiting
  • Iron Deficiency Anemia
  • Adelaide, South Australia, Australia
  • +8 more
Jun 23, 2023

MDS Trial in Japan (Eltrombopag, Placebo)

Recruiting
  • Myelodysplastic Syndromes
  • Narita, Chiba, Japan
  • +21 more
Jan 19, 2023

Acute Myeloid Leukemia, MDS Trial in China (TQB2928 Injection + Azacitidine for injection)

Not yet recruiting
  • Acute Myeloid Leukemia
  • Myelodysplastic Syndromes
  • TQB2928 Injection + Azacitidine for injection
  • Beijing, Beijing, China
  • +8 more
Aug 22, 2023

Frequency, Clinical Phenotype and Genetic Analysis of Heritable

Not yet recruiting
  • Renal Tumor Histology
  • +13 more
  • Gene test
  • Shanghai, Shanghai, China
    Ethics Committee of Shanghai Renji Hospital
Sep 6, 2022

Knowing and Treating Kosaki/Penttinen Syndromes

Not yet recruiting
  • Kosaki Overgrowth Syndrome
  • Penttinen Syndrome
    • Dijon, France
      CHU Dijon Bourgogne
    Jul 18, 2023

    Parkinson Disease, Progressive Supranuclear Palsy Trial in France (7 Tesla MRI)

    Not yet recruiting
    • Parkinson Disease
    • Progressive Supranuclear Palsy
    • 7 Tesla MRI
    • Aix-en-Provence, France
    • +5 more
    Nov 24, 2023

    Post-stroke Cognitive Impairment Trial in Hangzhou (Angong Niuhuang Pill)

    Recruiting
    • Post-stroke Cognitive Impairment
    • Angong Niuhuang Pill
    • Hangzhou, Zhejiang, China
      2nd Affiliated Hospital, School of Medicine
    Feb 7, 2023

    S100A8/A9 and Innate Immunity in Liver Disease

    Recruiting
    • Cirrhosis, Liver
    • +4 more
      • London Borough Of Wandsworth, London, United Kingdom
        Arjuna Singanayagam
      Mar 30, 2023

      Chronic Myelomonocytic Leukemia, Chronic Myelomonocytic Leukemia-1, Chronic Myelomonocytic Leukemia-2 Trial in Canada, United

      Active, not recruiting
      • Chronic Myelomonocytic Leukemia
      • +6 more
      • Birmingham, Alabama
      • +297 more
      Jan 28, 2023

      Stable Angina Pectoris, Coronary Artery Disease, Ischemic Heart Disease Trial in Kyoto (Aspirin, No aspirin)

      Recruiting
      • Stable Angina Pectoris
      • +2 more
      • Kyoto, Japan
        Kyoto University Hospital
      Aug 15, 2022

      Traffic Accident, Whiplash Syndrome Trial in Seoul (Korean herbal medicine treatment, Non-Korean herbal medicine treatment)

      Active, not recruiting
      • Traffic Accident
      • Whiplash Syndrome
      • Korean herbal medicine treatment
      • Non-Korean herbal medicine treatment
      • Seoul, Gangnam-Gu, Korea, Republic of
        Jaseng Hospital of Korean Medicine
      Aug 7, 2022

      Pediatric Cancer Trial in Canada, United States (Registry)

      Recruiting
      • Pediatric Cancer
      • Registry
      • Atlanta, Georgia
      • +6 more
      Aug 23, 2022

      Sensorimotor Integration in Monogenic Parkinson-dystonia

      Recruiting
      • Parkinson
      • +5 more
      • Transcranial magnetic stimulation (TMS)
      • +3 more
      • Lübeck, Schleswig-Holstein, Germany
        Institute of Systems Motor Science Lübeck
      Jan 27, 2023

      Autoimmune Cytopenias Including Autoimmune Hemolytic Anemia,

      Recruiting
      • Autoimmune Hemolytic Anemia
      • +5 more
      • cytokine essays
      • +6 more
      • Milano, Italy
        Fondazione Irccs Ca' Granda Ospedale Maggiore Policlinico
      Jul 3, 2023

      Evaluation of Sarcopenia-Related Malnutrition in Older Adults

      Recruiting
      • Sarcopenia
      • Malnutrition
        • Istanbul, Turkey
          Ümraniye Training and research hospital
        Aug 2, 2022

        Frailty, Dementia, Depression Trial in Balikesir (Comprehensive Geriatric Assessment)

        Enrolling by invitation
        • Frailty
        • +5 more
        • Comprehensive Geriatric Assessment
        • Balikesir, None Selected, Turkey
          Balikesir Ataturk City Hospital
        Aug 8, 2023

        MDS, MDS Trial in Tampa, Boston, Houston (APR-548 + Azacitidine)

        Terminated
        • MDS
        • Myelodysplastic Syndromes
        • APR-548 + Azacitidine
        • Tampa, Florida
        • +3 more
        Jul 20, 2022

        Effect of Sulthiame on EEG in Childhood Epilepsy Syndromes

        Not yet recruiting
        • Importance of Interictal Epileptiform Activity on Sleep EEG
        • (no location specified)
        May 22, 2023

        Diagnostic Score for Encephalitis to Assess Risk of Autoimmune

        Recruiting
        • Autoimmune Encephalitis
        • Autoimmune Encephalitis Caused by N-Methyl D-Aspartate Receptor Antibody (Disorder)
        • Clinical score of Granillo and al.
        • Lyon, France
          Centre de référence des syndromes neurologiques paranéoplasiques
        Jul 12, 2023

        Pathogenesis of Physical Induced Urticarial Syndromes

        Recruiting
        • Hypersensitivity, Immediate
        • +3 more
          • Bethesda, Maryland
            National Institutes of Health Clinical Center
          Jan 18, 2023