Myeloablative Autologous Gene Editing
Showing 26 - 50 of 9,686
Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Nashville (CTX001)
Recruiting
- Beta-Thalassemia
- +4 more
- CTX001
-
Nashville, Tennessee
- +5 more
Feb 2, 2023
Mucopolysaccharidosis II, MPS II Trial in United States (SB-913)
Terminated
- Mucopolysaccharidosis II
- MPS II
- SB-913
-
Oakland, California
- +4 more
Oct 21, 2022
Sickle Cell Disease, Hemoglobinopathies Trial in Canada, United States (EDIT-301)
Recruiting
- Sickle Cell Disease
- Hemoglobinopathies
- EDIT-301
-
Oakland, California
- +18 more
Jan 10, 2023
Transfusion Dependent Beta-Thalassemia Trial in Nanning (GMCN-508B (LentiRed))
Recruiting
- Transfusion Dependent Beta-Thalassemia
- GMCN-508B (LentiRed)
-
Nanning, Guangxi, ChinaThe affiliated hospital of guangxi medical university
Feb 28, 2023
Cervical Carcinoma Trial in Worldwide (LN-145, LN-145 + pembrolizumab)
Recruiting
- Cervical Carcinoma
- LN-145
- LN-145 + pembrolizumab
-
Phoenix, Arizona
- +39 more
Aug 16, 2022
Biliary Tract Cancer, Cholangiocarcinoma, Biliary Tract Tumors Trial in Pittsburgh (Tumor Infiltrating Lymphocytes (TIL))
Recruiting
- Biliary Tract Cancer
- +2 more
- Tumor Infiltrating Lymphocytes (TIL)
-
Pittsburgh, PennsylvaniaAllyson Welsch
Jul 21, 2022
Leukocyte Adhesion Defect - Type I Trial in Los Angeles, Madrid, London (RP-L201)
Active, not recruiting
- Leukocyte Adhesion Defect - Type I
- RP-L201
-
Los Angeles, California
- +2 more
Nov 19, 2021
Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)
Recruiting
- Transfusion Dependent Beta Thalassemia
- +3 more
- EDIT-301
-
Oakland, California
- +3 more
Jan 3, 2023
Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Worldwide (CTX001)
Active, not recruiting
- Beta-Thalassemia
- +4 more
- CTX001
-
Stanford, California
- +11 more
Nov 30, 2022
Transfusion Dependent Beta-thalassemia Trial in United States (ST-400 Investigational product)
Active, not recruiting
- Transfusion Dependent Beta-thalassemia
- ST-400 Investigational product
-
Los Angeles, California
- +5 more
Jul 6, 2022
Severe Combined Immunodeficiency Due to ADA Deficiency Trial in London (Infusion of autologous cryopreserved EFS-ADA LV CD34+
Active, not recruiting
- Severe Combined Immunodeficiency Due to ADA Deficiency
- Infusion of autologous cryopreserved EFS-ADA LV CD34+ cells (OTL-101)
- +2 more
-
London, United KingdomGreat Ormond Street Hospital for Children NHS Foundation Trust
Dec 17, 2021
Sickle Cell Disease, Hydroxyurea Failure, Hydroxyurea Intolerance Trial in Nashville (CTX001)
Recruiting
- Sickle Cell Disease
- +4 more
- CTX001
-
Philadelphia, Pennsylvania
- +3 more
Jan 24, 2023
Sickle Cell Disease Trial in Paris (DREPAGLOBE drug product)
Active, not recruiting
- Sickle Cell Disease
- DREPAGLOBE drug product
-
Paris, FranceDepartment of Biotherapy, Necker-Enfants Malades Hospital
Sep 26, 2022
Beta-Thalassemia, Thalassemia, Hematologic Diseases Trial (CTX001)
Not yet recruiting
- Beta-Thalassemia
- +6 more
- CTX001
- (no location specified)
Jul 26, 2022
Sickle Cell Disease Trial in Los Angeles, Boston (single infusion of autologous bone marrow derived CD34+ HSC cells transduced
Active, not recruiting
- Sickle Cell Disease
- single infusion of autologous bone marrow derived CD34+ HSC cells transduced with the lentiviral vector containing a short-hairpin RNA targeting BCL11a
-
Los Angeles, California
- +1 more
Feb 8, 2022
Neovascular Age-related Macular Degeneration(nAMD) Trial in Shanghai, Tianjin (HG202)
Not yet recruiting
- Neovascular Age-related Macular Degeneration(nAMD)
- HG202
-
Shanghai, Shanghai, China
- +1 more
Sep 4, 2023
Heterozygous Familial Hypercholesterolemia, Atherosclerotic Cardiovascular Disease, Hypercholesterolemia Trial in Auckland,
Recruiting
- Heterozygous Familial Hypercholesterolemia
- +2 more
-
Auckland, New Zealand
- +1 more
Aug 4, 2022
Neuroblastoma Trial in Minneapolis (Thiotepa, Cyclophosphamide, Melphalan)
Recruiting
- Neuroblastoma
- Thiotepa
- +6 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Nov 2, 2022
Transfusion-dependent a-Thalassemia Trial (GMCN-508A Drug Product)
Not yet recruiting
- Transfusion-dependent α-Thalassemia
- GMCN-508A Drug Product
- (no location specified)
Feb 24, 2023
Mucopolysaccharidosis II Trial (Autologous CD34+ HSCs transduced ex vivo with CD11B LV encoding human IDS tagged with ApoEII)
Not yet recruiting
- Mucopolysaccharidosis II
- Autologous CD34+ HSCs transduced ex vivo with CD11B LV encoding human IDS tagged with ApoEII
- (no location specified)
Dec 16, 2022
Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)
Not yet recruiting
- Transfusion-dependent Beta-Thalassemia
- KL003 cell injection Drug Product
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
May 8, 2023
Hemophilia B Trial in Washington (SB-FIX)
Terminated
- Hemophilia B
- SB-FIX
-
Washington, District of ColumbiaGeorgetown University Medical Center
Mar 8, 2022
Wiskott-Aldrich Syndrome Trial in Atlanta, Milan (OTL-103)
Active, not recruiting
- Wiskott-Aldrich Syndrome
- OTL-103
-
Atlanta, Georgia
- +1 more
Sep 27, 2022
Non Hodgkin's Lymphoma Trial in Beijing (TRAC and Power3 Genes Knock-out Allogeneic CD19-targeting CAR-T cell (ATHENA CAR-T),
Not yet recruiting
- Non Hodgkin's Lymphoma
- TRAC and Power3 Genes Knock-out Allogeneic CD19-targeting CAR-T cell (ATHENA CAR-T)
- +2 more
-
Beijing, China
- +2 more
Aug 23, 2023