Severe congenital protein C deficiency
Showing 26 - 50 of >10,000
Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency, Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy
Recruiting
- Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency
- +51 more
-
Lakewood, CaliforniaCongenital Muscle Disease International Registry (www.cmdir.org)
Aug 3, 2021
Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (AG-348)
Completed
- Pyruvate Kinase Deficiency
- Anemia, Hemolytic
-
Oakland, California
- +18 more
Dec 14, 2021
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia
Active, not recruiting
- Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
- +36 more
- Cyclophosphamide
- +4 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Jan 23, 2023
Hypoplasminogenemia, Congenital Plasminogen Deficiency Trial in Indianapolis, Oslo (Plasminogen (Human) intravenous)
Completed
- Hypoplasminogenemia
- Congenital Plasminogen Deficiency
- Plasminogen (Human) intravenous
-
Indianapolis, Indiana
- +1 more
Jul 30, 2021
Plasminogen Deficiency Trial in Saskatoon (Aliquoted allogeneic donor plasma in patient's conjunctiva)
Not yet recruiting
- Plasminogen Deficiency
- Aliquoted allogeneic donor plasma in patient's conjunctiva
-
Saskatoon, Saskatchewan, CanadaUniversity of Saskatchewan
Nov 7, 2022
Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (Placebo, AG-348)
Completed
- Pyruvate Kinase Deficiency
- Anemia, Hemolytic
- Placebo
- AG-348
-
Little Rock, Arkansas
- +45 more
May 20, 2022
Congenital Adrenal Hyperplasia Trial in United States (Abiraterone acetate, Placebo, Hydrocortisone)
Withdrawn
- Congenital Adrenal Hyperplasia
- Abiraterone acetate
- +3 more
-
Los Angeles, California
- +3 more
Jan 30, 2023
Obesity, Iron Deficiency Anemia Trial (Calorie-restricted diet with red meat, Calorie-restricted diet without red meat)
Not yet recruiting
- Obesity
- Iron Deficiency Anemia
- Calorie-restricted diet with red meat
- Calorie-restricted diet without red meat
- (no location specified)
Oct 23, 2023
High Sensitivity C Reactive Protein and Total Leucocytic Count
Not yet recruiting
- Abortion Early
- maternal serum C reactive protein
- +2 more
-
Banī Suwayf, Beni Suef, EgyptBeni-suef university Hospital
Aug 1, 2023
Patterns of Hemophilia Care in Assiut Children Patients
Not yet recruiting
- Hemophilia A
- Hemophilia B
- (no location specified)
Jul 29, 2023
Antithrombin III Deficiency Trial in Brussel (observation)
Not yet recruiting
- Antithrombin III Deficiency
- observation
-
Brussel, BelgiumUZ Brussel
May 26, 2023
Prediction of Renal Parenchymal Damage of CAKUT
Recruiting
- CAKUT
- combined diagnosis of renal parenchymal damage
-
Shanghai, ChinaChildren's Hospital of Fudan University
Nov 30, 2022
Ghrelin Levels in Patients With Protein C Deficiency
Unknown status
- Protein C Deficiency
- Protein C deficiency
- (no location specified)
Nov 25, 2019
Incidence of cCPHD in Denmark - a National Observational Study
Active, not recruiting
- Combined Pituitary Hormone Deficiency Genetic Form
- Combined Pituitary Hormone Deficiency
-
Odense, DenmarkHCA Research, Odense University Hospital
Jul 3, 2022
Pyruvate Dehydrogenase Complex Deficiency Trial in United States (drug, other, genetic)
Recruiting
- Pyruvate Dehydrogenase Complex Deficiency
- Dichloroacetate (DCA)
- +2 more
-
Orange, California
- +8 more
Jul 29, 2021
Hereditary Thrombotic Thrombocytopenic Purpura
Recruiting
- Thrombotic Thrombocytopenic Purpura
- +4 more
- Observation
-
Oklahoma City, Oklahoma
- +6 more
Nov 1, 2022
Nutrition in Congenital Heart Disease
Not yet recruiting
- Congenital Heart Disease
- (no location specified)
May 26, 2023
Iron Deficiencies Trial in Zürich (soy protein concentrate-meat analog, soy protein concentrate-meat analog_dephytinization,
Not yet recruiting
- Iron Deficiencies
- soy protein concentrate-meat analog
- +3 more
-
Zürich, SwitzerlandFernfachhochschule Schweiz (FFHS) - Campus Gleisarena
Sep 12, 2023
Newborns With Congenital Diaphragmatic Hernia
Recruiting
- Congenital Diaphragmatic Hernia
- +4 more
-
Stockholm, SwedenDepartment of Pediatric Anesthesia and Intensive Care. Karolinsk
Sep 21, 2023
Balloon Pulmonary Valvuloplasty in Congenital Pulmonary Stenosis
Recruiting
- Congenital Heart Disease
- Pulmonary Valve Stenoses
-
Assiut, EgyptFaculty of medicine Assiut university
Apr 12, 2023
Lung Diseases, Respiratory Distress Syndrome, Newborn, Pulmonary Surfactant Trial in Saint Louis
Recruiting
- Lung Diseases
- +3 more
-
Saint Louis, MissouriWashington University School of Medicine
Nov 22, 2022
Idiopathic Pulmonary Fibrosis Trial in Shanghai (Cell Free Fat Extract(CEFFE))
Recruiting
- Idiopathic Pulmonary Fibrosis
- Cell Free Fat Extract(CEFFE)
-
Shanghai, Shanghai, ChinaThe Ninth People's Hospital Affiliated to Shanghai Jiao Tong Uni
May 22, 2023
Long-chain Fatty Acid Oxidation Disorders (LC-FAOD), Carnitine Palmitoyltransferase (CPT II) Deficiency, Very Long Chain
Completed
- Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
- +4 more
-
Washington, District of Columbia
- +9 more
Jan 21, 2021
Pregnancy, Malaria, Nutrition Trial (L-citrulline)
Not yet recruiting
- Pregnancy
- +5 more
- L-citrulline
- (no location specified)
Jun 28, 2023