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Severe congenital protein C deficiency

Showing 26 - 50 of >10,000

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IGF1 Deficiency Trial in Worldwide (Increlex®)

Recruiting
  • IGF1 Deficiency
  • Miami, Florida
  • +50 more
Dec 29, 2022

Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency, Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy

Recruiting
  • Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency
  • +51 more
    • Lakewood, California
      Congenital Muscle Disease International Registry (www.cmdir.org)
    Aug 3, 2021

    Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (AG-348)

    Completed
    • Pyruvate Kinase Deficiency
    • Anemia, Hemolytic
    • Oakland, California
    • +18 more
    Dec 14, 2021

    Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia

    Active, not recruiting
    • Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
    • +36 more
    • Buffalo, New York
      Roswell Park Cancer Institute
    Jan 23, 2023

    Hypoplasminogenemia, Congenital Plasminogen Deficiency Trial in Indianapolis, Oslo (Plasminogen (Human) intravenous)

    Completed
    • Hypoplasminogenemia
    • Congenital Plasminogen Deficiency
    • Plasminogen (Human) intravenous
    • Indianapolis, Indiana
    • +1 more
    Jul 30, 2021

    Plasminogen Deficiency Trial in Saskatoon (Aliquoted allogeneic donor plasma in patient's conjunctiva)

    Not yet recruiting
    • Plasminogen Deficiency
    • Aliquoted allogeneic donor plasma in patient's conjunctiva
    • Saskatoon, Saskatchewan, Canada
      University of Saskatchewan
    Nov 7, 2022

    Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (Placebo, AG-348)

    Completed
    • Pyruvate Kinase Deficiency
    • Anemia, Hemolytic
    • Little Rock, Arkansas
    • +45 more
    May 20, 2022

    Congenital Adrenal Hyperplasia Trial in United States (Abiraterone acetate, Placebo, Hydrocortisone)

    Withdrawn
    • Congenital Adrenal Hyperplasia
    • Abiraterone acetate
    • +3 more
    • Los Angeles, California
    • +3 more
    Jan 30, 2023

    Obesity, Iron Deficiency Anemia Trial (Calorie-restricted diet with red meat, Calorie-restricted diet without red meat)

    Not yet recruiting
    • Obesity
    • Iron Deficiency Anemia
    • Calorie-restricted diet with red meat
    • Calorie-restricted diet without red meat
    • (no location specified)
    Oct 23, 2023

    High Sensitivity C Reactive Protein and Total Leucocytic Count

    Not yet recruiting
    • Abortion Early
    • maternal serum C reactive protein
    • +2 more
    • Banī Suwayf, Beni Suef, Egypt
      Beni-suef university Hospital
    Aug 1, 2023

    Patterns of Hemophilia Care in Assiut Children Patients

    Not yet recruiting
    • Hemophilia A
    • Hemophilia B
      • (no location specified)
      Jul 29, 2023

      Antithrombin III Deficiency Trial in Brussel (observation)

      Not yet recruiting
      • Antithrombin III Deficiency
      • observation
      • Brussel, Belgium
        UZ Brussel
      May 26, 2023

      Prediction of Renal Parenchymal Damage of CAKUT

      Recruiting
      • CAKUT
      • combined diagnosis of renal parenchymal damage
      • Shanghai, China
        Children's Hospital of Fudan University
      Nov 30, 2022

      Ghrelin Levels in Patients With Protein C Deficiency

      Unknown status
      • Protein C Deficiency
      • Protein C deficiency
      • (no location specified)
      Nov 25, 2019

      Incidence of cCPHD in Denmark - a National Observational Study

      Active, not recruiting
      • Combined Pituitary Hormone Deficiency Genetic Form
      • Combined Pituitary Hormone Deficiency
        • Odense, Denmark
          HCA Research, Odense University Hospital
        Jul 3, 2022

        Pyruvate Dehydrogenase Complex Deficiency Trial in United States (drug, other, genetic)

        Recruiting
        • Pyruvate Dehydrogenase Complex Deficiency
        • Dichloroacetate (DCA)
        • +2 more
        • Orange, California
        • +8 more
        Jul 29, 2021

        Hereditary Thrombotic Thrombocytopenic Purpura

        Recruiting
        • Thrombotic Thrombocytopenic Purpura
        • +4 more
        • Observation
        • Oklahoma City, Oklahoma
        • +6 more
        Nov 1, 2022

        Nutrition in Congenital Heart Disease

        Not yet recruiting
        • Congenital Heart Disease
          • (no location specified)
          May 26, 2023

          Iron Deficiencies Trial in Zürich (soy protein concentrate-meat analog, soy protein concentrate-meat analog_dephytinization,

          Not yet recruiting
          • Iron Deficiencies
          • soy protein concentrate-meat analog
          • +3 more
          • Zürich, Switzerland
            Fernfachhochschule Schweiz (FFHS) - Campus Gleisarena
          Sep 12, 2023

          Newborns With Congenital Diaphragmatic Hernia

          Recruiting
          • Congenital Diaphragmatic Hernia
          • +4 more
            • Stockholm, Sweden
              Department of Pediatric Anesthesia and Intensive Care. Karolinsk
            Sep 21, 2023

            Balloon Pulmonary Valvuloplasty in Congenital Pulmonary Stenosis

            Recruiting
            • Congenital Heart Disease
            • Pulmonary Valve Stenoses
              • Assiut, Egypt
                Faculty of medicine Assiut university
              Apr 12, 2023

              Lung Diseases, Respiratory Distress Syndrome, Newborn, Pulmonary Surfactant Trial in Saint Louis

              Recruiting
              • Lung Diseases
              • +3 more
                • Saint Louis, Missouri
                  Washington University School of Medicine
                Nov 22, 2022

                Idiopathic Pulmonary Fibrosis Trial in Shanghai (Cell Free Fat Extract(CEFFE))

                Recruiting
                • Idiopathic Pulmonary Fibrosis
                • Cell Free Fat Extract(CEFFE)
                • Shanghai, Shanghai, China
                  The Ninth People's Hospital Affiliated to Shanghai Jiao Tong Uni
                May 22, 2023

                Long-chain Fatty Acid Oxidation Disorders (LC-FAOD), Carnitine Palmitoyltransferase (CPT II) Deficiency, Very Long Chain

                Completed
                • Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
                • +4 more
                • Washington, District of Columbia
                • +9 more
                Jan 21, 2021

                Pregnancy, Malaria, Nutrition Trial (L-citrulline)

                Not yet recruiting
                • Pregnancy
                • +5 more
                • L-citrulline
                • (no location specified)
                Jun 28, 2023