congenital muscular dystrophy
Showing 26 - 50 of 5,129
Duchenne Muscular Dystrophy Trial in Chengdu (JWK007 Single intravenous infusion administration)
Recruiting
- Duchenne Muscular Dystrophy
- JWK007 Single intravenous infusion administration
-
Chengdu, Sichuan, ChinaWest China Hospital, Sichuan University
Oct 29, 2023
FSHD Trial (MSOT Acuity Echo)
Not yet recruiting
- FSHD
- MSOT Acuity Echo
- (no location specified)
Jun 5, 2023
pwFSHD (Patient With Facioscapulohumeral Muscular Dystrophy)
Completed
- Facio-Scapulo-Humeral Dystrophy
-
Istanbul, TurkeyIstanbul University-Cerrahpaşa
Nov 7, 2022
Duchenne Muscular Dystrophy Video Assessment Registry
Recruiting
- Duchenne Muscular Dystrophy
-
Plymouth, MassachusettsCasimir
Feb 1, 2023
Duchenne Muscular Dystrophy Trial in Ankara (telerehabilitation-based motor imagery training, telerehabilitation-based
Not yet recruiting
- Duchenne Muscular Dystrophy
- telerehabilitation-based motor imagery training
- telerehabilitation-based physiotheraphy training
-
Ankara, TurkeyHacettepe University
Oct 27, 2023
NSAA NON-Interventional Study Protocol
Not yet recruiting
- Duchenne Muscular Dystrophy
- Remote Administration of NSAA
- (no location specified)
Sep 19, 2023
Facio-Scapulo-Humeral Dystrophy Trial (ARO-DUX4 for Injection, Placebo)
Not yet recruiting
- Facio-Scapulo-Humeral Dystrophy
- ARO-DUX4 for Injection
- Placebo
- (no location specified)
Nov 13, 2023
Duchenne Muscular Dystrophy Trial in Portland (NS-089/NCNP-02)
Not yet recruiting
- Duchenne Muscular Dystrophy
-
Portland, OregonShriners Hospital for Children
Aug 16, 2023
Duchenne Muscular Dystrophy Trial in Los Angeles, Columbus (SGT-003)
Not yet recruiting
- Duchenne Muscular Dystrophy
- SGT-003
-
Los Angeles, California
- +1 more
Nov 14, 2023
Duchenne Muscular Dystrophy Trial in Columbus (rAAVrh74.MCK.GALGT2)
Active, not recruiting
- Duchenne Muscular Dystrophy
- rAAVrh74.MCK.GALGT2
-
Columbus, OhioNationwide Children's Hospital
Jul 26, 2022
Muscular Dystrophies, Spinal Muscular Atrophy, Duchenne Muscular Dystrophy Trial in Saint Paul (Abilitech Assist)
Recruiting
- Muscular Dystrophies
- +6 more
- Abilitech Assist
-
Saint Paul, MinnesotaGillette Children's
Dec 1, 2022
Duchenne Muscular Dystrophy Trial (Givinostat, Placebo)
Not yet recruiting
- Duchenne Muscular Dystrophy
- Givinostat
- Placebo
- (no location specified)
Jun 27, 2023
Muscular Dystrophy, Duchenne Type Trial (trunk oriented exercise, whole body vibration)
Not yet recruiting
- Muscular Dystrophy, Duchenne Type
- trunk oriented exercise
- whole body vibration
- (no location specified)
Jan 8, 2023
Duchenne Muscular Dystrophy Trial in United States (EDG-5506 Dose 1, EDG-5506 Dose 2, Placebo)
Not yet recruiting
- Duchenne Muscular Dystrophy
- EDG-5506 Dose 1
- +2 more
-
Los Angeles, California
- +6 more
Oct 26, 2023
Facioscapulohumeral Muscular Dystrophy (FSHD) Trial (Placebo, RO7204239)
Recruiting
- Facioscapulohumeral Muscular Dystrophy (FSHD)
- Placebo
- RO7204239
-
København Ø, DenmarkRigshospitalet; Klinik for Nerve- og Muskelsygdomme
Feb 2, 2023
AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Boys
Recruiting
- Duchenne Muscular Dystrophy
- AAV8 DetectCDx
-
Atlanta, GeorgiaRare Disease Research
Jan 12, 2023
Duchenne Muscular Dystrophy With Small Mutations
Recruiting
- Muscular Dystrophy, Duchenne
- MUSCLE MAGNETIC RESONANCE IMAGING (MRI)
-
Rome, ItalyClaudia Brogna
Apr 17, 2023
Unraveling Metabolic Involvement in Facioscapulohumeral
Not yet recruiting
- Facioscapulohumeral Muscular Dystrophy
- metabolomic on plasma sample
- (no location specified)
Oct 11, 2023
Duchenne Muscular Dystrophy Trial in Ankara (Bicycle Ergometer Training, Home-based exercise group)
Completed
- Duchenne Muscular Dystrophy
- Bicycle Ergometer Training
- Home-based exercise group
-
Ankara, Altındağ, TurkeyHacettepe University, Faculty of Physical Therapy and Rehabilita
Dec 14, 2022
Type 1 Facioscapulohumeral Muscular Dystrophy Trial in Lille, Paris, Nice (Remote monitoring program)
Not yet recruiting
- Type 1 Facioscapulohumeral Muscular Dystrophy
- Remote monitoring program
-
Lille, Hauts De France, France
- +2 more
Mar 31, 2023
Duchenne Muscular Dystrophy Trial in Garches (Phase 1, SQY51, Phase 2a, SQY51 (cohort 1), Phase 2a, SQY51 (cohort 2))
Recruiting
- Duchenne Muscular Dystrophy
- Phase 1, SQY51
- +3 more
-
Garches, FranceHôpital Raymond Poincaré
Mar 7, 2023
Limb Girdle Muscular Dystrophy Trial in Columbus (SRP-9003)
Enrolling by invitation
- Limb Girdle Muscular Dystrophy
- SRP-9003
-
Columbus, OhioNationwide Children's Hospital
May 17, 2023
DMCRN-02-001: Assessing Pediatric Endpoints in DM1
Recruiting
- Congenital Myotonic Dystrophy
- +3 more
-
Los Angeles, California
- +6 more
Jan 31, 2023
Duchenne Muscular Dystrophy Trial in Paris (Cardiac MRI, Blood assays)
Not yet recruiting
- Duchenne Muscular Dystrophy
- Cardiac MRI
- Blood assays
-
Paris, FranceNecker Hospital
Sep 26, 2022
Duchenne Muscular Dystrophy Trial (delandistrogene moxeparvovec)
Not yet recruiting
- Duchenne Muscular Dystrophy
- delandistrogene moxeparvovec
- (no location specified)
Nov 8, 2023