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Achondroplasia

Showing 1 - 25 of 41

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Osteochondrodysplasia Trial in Parkville (SAR442501)

Recruiting
  • Osteochondrodysplasia
  • Parkville, Victoria, Australia
    Investigational Site Number: 0360001
Oct 10, 2023

The Norwegian Adult Achondroplasia Study

Completed
  • Achondroplasia
  • No intervention
  • Nesoddtangen, Akershus, Norway
    Sunnas Rehabilitation Hospital
Oct 28, 2022

Achondroplasia Trial in Parkville (TransCon CNP)

Recruiting
  • Achondroplasia
  • TransCon CNP
  • Parkville, Victoria, Australia
    Ascendis Pharma Investigational Site
Jun 30, 2023

Achondroplasia Trial (Navepegritide, Placebo for Navepegritide)

Not yet recruiting
  • Achondroplasia
  • (no location specified)
Oct 6, 2023

Learn About Recifercept in Patients With Achondroplasia

Active, not recruiting
  • Achondroplasia
  • Recifercept
  • New York, New York
    Pfizer
Dec 19, 2022

Achondroplasia Trial (TransCon CNP, Placebo for TransCon CNP)

Not yet recruiting
  • Achondroplasia
  • TransCon CNP
  • Placebo for TransCon CNP
  • (no location specified)
Jan 11, 2023

Achondroplasia Trial in Parkville, London, Sheffield (vosoritide)

Active, not recruiting
  • Achondroplasia
  • vosoritide
  • Parkville, Victoria, Australia
  • +2 more
Dec 20, 2022

Achondroplasia, Hypochondroplasia Trial in Milan (Registry)

Recruiting
  • Achondroplasia
  • Hypochondroplasia
  • Registry
  • Milan, Italy
    Medical Genetics Unit, Fondazione IRCCS Ca' Granda Ospedale Magg
Apr 21, 2022

Adaption and Testing of Quality of Life in Short Stature Youth

Recruiting
  • Achondroplasia
  • +2 more
  • Questionnaire
  • Hamburg, Germany
    University Medical Center Hamburg-Eppendorf
Oct 28, 2022

Achondroplasia Trial in Worldwide (TransCon CNP, Placebo for TransCon CNP, sWfI Placebo for TransCon CNP)

Active, not recruiting
  • Achondroplasia
  • TransCon CNP
  • +2 more
  • Little Rock, Arkansas
  • +14 more
Dec 20, 2022

Achondroplasia Trial in Worldwide (Recifercept)

Active, not recruiting
  • Achondroplasia
  • Recifercept
  • Irvine, California
  • +13 more
Jan 20, 2023

Achondroplasia Trial in Shanghai (Recombinant human growth hormone)

Not yet recruiting
  • Achondroplasia
  • Recombinant human growth hormone
  • Shanghai, Shanghai, China
    Children's Hospital of Fudan University
Apr 25, 2022

Achondroplasia Trial in Australia, Spain, United Kingdom (Infigratinib)

Recruiting
  • Achondroplasia
  • Parkville, Victoria, Australia
  • +3 more
Apr 5, 2022

Achondroplasia Trial in Worldwide (BMN 111, Placebo)

Completed
  • Achondroplasia
  • BMN 111
  • Placebo
  • Oakland, California
  • +15 more
Dec 15, 2022

Achondroplasia Trial in Dallas (BMN 111 administration via Injector Pen, BMN 111 administration via vial and syringe)

Recruiting
  • Achondroplasia
  • BMN 111 administration via Injector Pen
  • BMN 111 administration via vial and syringe
  • Dallas, Texas
    Labcorp
Apr 2, 2023

Achondroplasia Trial in Worldwide (Recifercept)

Recruiting
  • Achondroplasia
  • Recifercept
  • Aliso Viejo, California
  • +13 more
Aug 3, 2022

Achondroplasia Trial in China (TransCon CNP, Placebo for TransCon CNP)

Recruiting
  • Achondroplasia
  • TransCon CNP
  • Placebo for TransCon CNP
  • Beijing, China
  • +5 more
Feb 9, 2022

Children With Achondroplasia (ACH)

Recruiting
  • Achondroplasia
    • Oakland, California
    • +19 more
    Apr 6, 2022

    Clinical & Anthropometric Characteristics of Achondroplasia.

    Active, not recruiting
    • Achondroplasia
      • Torrance, California
      • +32 more
      Nov 16, 2022

      Achondroplasia Trial in Worldwide (Infigratinib 0.016 mg/kg, Infigratinib 0.032 mg/kg, Infigratinib 0.064 mg/kg)

      Recruiting
      • Achondroplasia
      • Infigratinib 0.016 mg/kg
      • +3 more
      • Oakland, California
      • +17 more
      Apr 5, 2022

      Achondroplasia Trial in Worldwide (BMN 111, Placebo)

      Completed
      • Achondroplasia
      • BMN 111
      • Placebo
      • Oakland, California
      • +23 more
      Feb 4, 2022

      Lifetime Impact Study for Achondroplasia

      Completed
      • Achondroplasia
        • Buenos Aires, Argentina
        • +3 more
        Apr 2, 2021

        Lifetime Impact of Achondroplasia Study in Europe-LIAISE

        Completed
        • Achondroplasia
          • Vienna, Austria
          • +12 more
          Apr 2, 2021

          Pseudoachondroplasia Trial in Houston (resveratrol, Placebo)

          Terminated
          • Pseudoachondroplasia
          • Houston, Texas
            University of Texas Health Science Center
          Nov 16, 2021

          Achondroplasia Trial in Worldwide (BMN 111)

          Completed
          • Achondroplasia
          • BMN 111
          • Oakland, California
          • +8 more
          Dec 22, 2020