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Codon-deoptimized

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STUDY
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Respiratory Syncytial Virus Infections Trial (CodaVax-RSV, Normal Saline)

Not yet recruiting
  • Respiratory Syncytial Virus Infections
  • CodaVax-RSV
  • Normal Saline
  • (no location specified)
Nov 16, 2022

Respiratory Syncytial Virus Infections Trial in Brisbane (CodaVax-RSV, Normal saline)

Completed
  • Respiratory Syncytial Virus Infections
  • CodaVax-RSV
  • Normal saline
  • Brisbane, Queensland, Australia
    Nucleus Network/Q-Pharm
Jun 8, 2021

Each Codon-specific KRAS Mutation in Colorectal Cancer

Completed
  • Colorectal Cancer
  • Mutation
  • Seongnam-si, Gyeonggi-do, Korea, Republic of
    Seoul National University Bundang Hospital
Dec 10, 2022

Pompe Disease Infantile-Onset Trial in China (GC301)

Not yet recruiting
  • Pompe Disease Infantile-Onset
  • GC301
  • Beijing, China
  • +4 more
Apr 2, 2023

Homozygous Familial Hypercholesterolemia Trial in Xi'an (NGGT006)

Not yet recruiting
  • Homozygous Familial Hypercholesterolemia
  • NGGT006
  • Xi'an, Shaanxi, China
    First Affiliated Hospital of Xian Jiaotong University
Nov 5, 2023

NSCLC Trial in Baltimore (Pooled Mutant KRAS-Targeted Long Peptide Vaccine 0.3mg each; 1.8mg total peptides)

Not yet recruiting
  • Non-Small Cell Lung Cancer
  • Pooled Mutant KRAS-Targeted Long Peptide Vaccine 0.3mg each; 1.8mg total peptides
  • Baltimore, Maryland
    Johns Hopkins University
Jun 16, 2022

Infantile-onset Pompe Disease Trial in Beijing (Genetic: GC301)

Recruiting
  • Infantile-onset Pompe Disease
  • Genetic: GC301
  • Beijing, Beijing, China
    Bayi Children's Hospital, Seventh Medical Center, PLA general ho
Sep 30, 2022

Hemophilia A Trial in Little Rock (ASC618)

Recruiting
  • Hemophilia A
  • ASC618
  • Little Rock, Arkansas
    Arkansas Children's Hospital
Jan 30, 2023

Cortisol Metabolism in Familial Partial Lipodystrophy Type 2

Recruiting
  • Familial Partial Lipodystrophy Type 2
  • Biopsy
  • Lille, France
    Hop Claude Huriez
Jun 20, 2022

Hemophilia B Trial in Worldwide (AAV5-hFIXco-Padua)

Active, not recruiting
  • Hemophilia B
  • AAV5-hFIXco-Padua
  • Factor IX (FIX)
  • Phoenix, Arizona
  • +32 more
Sep 26, 2022

Multiple Myeloma, Smoldering Multiple Myeloma Trial in Oslo (TG01)

Not yet recruiting
  • Multiple Myeloma
  • Smoldering Multiple Myeloma
  • TG01
  • Oslo, Norway
    Oslo Myeloma Center
May 2, 2023

Hemophilia B Trial in United States (AAV5-hFIXco-Padua (AMT-061))

Active, not recruiting
  • Hemophilia B
  • AAV5-hFIXco-Padua (AMT-061)
  • Los Angeles, California
  • +3 more
May 17, 2022

HIV Trial in Puerto Rico, United States (Nevirapine, Zidovudine, Didanosine)

Completed
  • HIV Infections
  • Los Angeles, California
  • +58 more
Oct 28, 2021

Spastic Paraplegia Type 50 Trial in Toronto (MELPIDA)

Active, not recruiting
  • Spastic Paraplegia Type 50
  • MELPIDA
  • Toronto, Ontario, Canada
    The Hospital for Sick Children
Oct 5, 2023

Primary Lymphedema and Mutation CELSR1

Recruiting
  • Primary Lymphedema
    • Montpellier, France
      Uhmontpellier
    Jun 2, 2021

    C9orf72 Amyotrophic Lateral Sclerosis (ALS), Frontotemporal Dementia Trial in Gainesville (Metformin)

    Recruiting
    • C9orf72 Amyotrophic Lateral Sclerosis (ALS)
    • Frontotemporal Dementia
    • Gainesville, Florida
      UF Health at the University of Florida
    Sep 7, 2021

    TLR4 Polymorphisms and Risk of Skin Cancer

    Active, not recruiting
    • Skin Cancer
    • Detection of single nucleotide polymorphisms (SNP)
    • Birmingham, Alabama
      The Kirklin Clinic
    Jan 20, 2022

    Cystic Fibrosis Trial in Birmingham (Trikafta, symdeko/Trikafta, Ivacaftor/Trikafta)

    Completed
    • Cystic Fibrosis
    • Birmingham, Alabama
      University of Alabama at Birmingham
    Feb 7, 2022

    Pompe Disease Trial in Gainesville (genetic, drug, other)

    Completed
    • Pompe Disease
    • Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase
    • +7 more
    • Gainesville, Florida
      Clinical and Translational Research Building (CTRB), University
    Mar 24, 2022

    Safety, Vaccine Reaction, Vaccine Adverse Reaction Trial (S.opt.FL COVID-19 pDNA vaccine)

    Not yet recruiting
    • Safety
    • +3 more
    • S.opt.FL COVID-19 pDNA vaccine
    • (no location specified)
    Dec 22, 2021

    Cardiac Amyloidosis, Cardiac Disease Trial in Fort-de-France (Cardiac electro-mapping)

    Not yet recruiting
    • Cardiac Amyloidosis
    • Cardiac Disease
    • Cardiac electro-mapping
    • Fort-de-France, Martinique
      Centre Hospitalier Universitaire de Fort-de-France
    Jul 7, 2021

    Rare CFTR Mutation Cell Collection Protocol (RARE)

    Recruiting
    • Cystic Fibrosis
      • Birmingham, Alabama
      • +5 more
      Aug 22, 2022

      Hereditary Colorectal Cancer Syndromes

      Active, not recruiting
      • Hereditary Colorectal Cancer Syndrome
      • Questionnaires
      • Blood Draw/Saliva Sample
      • Houston, Texas
        University of Texas MD Anderson Cancer Center
      Jan 20, 2022

      Exercise, Insulin Sensitivity, Skeletal Muscle Trial in København (Acute exercise)

      Completed
      • Exercise
      • +2 more
      • Acute exercise
      • København, Denmark
        Department of Exercise, Nutrition and Sports, Faculty of Science
      Jan 5, 2022

      Amino Acid Metabolism, Inborn Errors Trial in Worldwide (Ataluren)

      Terminated
      • Amino Acid Metabolism, Inborn Errors
      • Antwerp, Belgium
      • +8 more
      Jun 22, 2020