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F508del

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STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Cystic Fibrosis Trial in Belfast (FDL169, FDL176)

Suspended
  • Cystic Fibrosis
  • Belfast, United Kingdom
    Celerion GB Ltd
Jan 30, 2020

Cystic Fibrosis Trial in France (Sample collection)

Recruiting
  • Cystic Fibrosis
  • Sample collection
  • Bordeaux, France
  • +14 more
Jul 7, 2023

Cystic Fibrosis Trial in Australia (Tezacaftor/Ivacaftor, Ivacaftor, Placebo)

Completed
  • Cystic Fibrosis
  • Chermside, Australia
  • +8 more
Oct 22, 2019

Cystic Fibrosis Trial in Worldwide (VX-445, TEZ, IVA)

Active, not recruiting
  • Cystic Fibrosis
  • Tucson, Arizona
  • +109 more
Jul 26, 2022

Cystic Fibrosis Trial in Worldwide (VX-659/TEZ/IVA, IVA)

Terminated
  • Cystic Fibrosis
  • Birmingham, Alabama
  • +99 more
Dec 31, 2021

Cystic Fibrosis Trial in Australia, United Kingdom (LUM/IVA, Placebo)

Completed
  • Cystic Fibrosis
  • Melbourne, Victoria, Australia
  • +11 more
Mar 18, 2019

Glucose Tolerance Abnormalities in Cystic Fibrosis Homozygous

Completed
  • Cystic Fibrosis Homozygous for Phe 508 Del CFTR
  • Glucose Intolerance or Newly Diagnosis Diabetes
  • Lumacaftor-Ivacaftor treatment
  • Strasbourg, Alsace, France
  • +12 more
Nov 23, 2021

Cystic Fibrosis, Inflammation Trial in Frankfurt, Bonn, Amsterdam (Genotyping, Lung function, Microbiology)

Recruiting
  • Cystic Fibrosis
  • Inflammation
  • Genotyping
  • +4 more
  • Frankfurt, Hessia, Germany
  • +2 more
Aug 8, 2021

Trikafta/Kaftrio and Pseudomonas Aeruginosa

Recruiting
  • Cystic Fibrosis
    • Milan, Italy
    • +1 more
    Jan 9, 2023

    Cystic Fibrosis Trial in Worldwide (VX-445/TEZ/IVA, TEZ/IVA, IVA)

    Completed
    • Cystic Fibrosis
    • Tucson, Arizona
    • +43 more
    Jan 24, 2020

    CFTR-modulating Triple Therapy Elexacaftor - Tezacaftor -

    Recruiting
    • Cystic Fibrosis
    • Elexacaftor / Ivacaftor / Tezacaftor
    • Erlangen, Bavaria, Germany
      University Hospital Erlange, Department of Pediatrics
    Oct 7, 2022

    Cystic Fibrosis Trial in Canada, United States (TEZ, TEZ/IVA, IVA)

    Completed
    • Cystic Fibrosis
    • Birmingham, Alabama
    • +32 more
    Feb 25, 2020

    The PROMISE Pediatric Study 6 to 11 Years Old

    Active, not recruiting
    • Cystic Fibrosis
    • Cystic Fibrosis in Children
      • Birmingham, Alabama
      • +19 more
      Sep 7, 2022

      Cystic Fibrosis Trial in Birmingham, Atlanta, Houston (Trikafta)

      Recruiting
      • Cystic Fibrosis
      • Birmingham, Alabama
      • +2 more
      Mar 25, 2022

      Biological and Clinical Effects of Significantly Corrected CFTR

      Active, not recruiting
      • Cystic Fibrosis
        • Birmingham, Alabama
        • +55 more
        Sep 7, 2022

        Cystic Fibrosis Trial in Worldwide (TEZ/IVA, IVA, Placebo)

        Completed
        • Cystic Fibrosis
        • New Lambton Heights, Australia
        • +26 more
        Feb 4, 2020

        Orkambi in Cystic Fibrosis Lung Disease by Inhaled Xenon MRI

        Recruiting
        • Cystic Fibrosis
        • Hyperpolarized Xenon
        • Cincinnati, Ohio
          Cincinnati Children's Hospital Medical Center
        Jun 16, 2021

        Cystic Fibrosis Trial in Worldwide (VX-659/TEZ/IVA, TEZ/IVA, IVA)

        Completed
        • Cystic Fibrosis
        • Birmingham, Alabama
        • +45 more
        Sep 26, 2019

        HIV-1 Trial in Panama, South Africa, United States (F/TAF, 3rd ARV agent, Boosted PIs)

        Active, not recruiting
        • HIV-1
        • Los Angeles, California
        • +7 more
        Nov 11, 2022

        Airway Clearance Therapy on Hyperpolarized 129Xenon and MRI

        Completed
        • Cystic Fibrosis
        • hyperpolarized Xenon gas
        • Cincinnati, Ohio
          Cincinnati Children's Hospital Medical Center
        Mar 8, 2022

        ANGIOLITE PMCF Study ( rEPIC04F )

        Recruiting
        • Coronary Artery Disease (CAD)
        • Ischemic Heart Disease
        • ANGIOLITE
        • Barcelona, Spain
        • +5 more
        Jan 12, 2023

        Music Therapy Trial in Varese (Premature family music therapy intervention to support parenting, attachment bond and preterm

        Recruiting
        • Music Therapy
        • Premature family music therapy intervention to support parenting, attachment bond and preterm development
        • Varese, Italy
          Ospedale F. Del Ponte
        Apr 19, 2022

        Gastrointestinal Study at Orkambi Therapy in CF Patients

        Unknown status
        • Cystic Fibrosis
          • Stockholm, Sweden
            Stockholm CF Center
          Feb 28, 2019

          Music Therapy Trial in Varese (The effects of Pacifier Activated Lullaby in very low birth weigt preterm infants. An italian

          Completed
          • Music Therapy
          • The effects of Pacifier Activated Lullaby in very low birth weigt preterm infants. An italian music therapy intervention
          • Varese, Italy
            Ospedale F. Del Ponte
          Apr 19, 2022

          Cystic Fibrosis Trial in Denver, Baltimore, Philadelphia (Ravicti low dose, Ravicti high dose, Placebo)

          Terminated
          • Cystic Fibrosis
          • Ravicti low dose
          • +2 more
          • Denver, Colorado
          • +2 more
          Mar 4, 2022