Krabbe Disease, also known as Globoid Cell Leukodystrophy
Showing 1 - 25 of >10,000
Leukodystrophy, Globoid Cell Trial in Worldwide (PBKR03)
Recruiting
- Leukodystrophy, Globoid Cell
- PBKR03
-
Chicago, Illinois
- +8 more
Aug 17, 2022
Krabbe Disease Trial in Ann Arbor (FBX-101)
Recruiting
- Krabbe Disease
- FBX-101
-
Ann Arbor, MichiganUniversity of Michigan Hospitals - Michigan Medicine
Feb 13, 2023
Krabbe Disease Trial in Ann Arbor (FBX-101)
Recruiting
- Krabbe Disease
- FBX-101
-
Ann Arbor, MichiganUniversity of Michigan Hospitals - Michigan Medicine
Aug 24, 2022
Krabbe Disease Trial in Buffalo
Recruiting
- Krabbe Disease
-
Buffalo, New YorkState University of New York at Buffalo
Apr 17, 2022
Pediatric Subjects With Globoid Cell Leukodystrophy (GLD)
Withdrawn
- Leukodystrophy, Globoid Cell
- (no location specified)
May 30, 2021
Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human
Completed
- Mucopolysaccharidosis I
- +15 more
- Human Placental Derived Stem Cell
-
Denver, Colorado
- +2 more
Oct 24, 2022
Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)
Recruiting
- Adrenoleukodystrophy
- +11 more
- DUOC-01
-
Durham, North CarolinaDuke University Medical Center
Oct 24, 2022
Biomarker for Krabbe Disease (BioKrabbe)
Active, not recruiting
- Krabbe Disease
-
Cairo, Egypt
- +4 more
May 12, 2021
Leukodystrophy, White Matter Disease, Leukoencephalopathies Trial in United States
Recruiting
- Leukodystrophy
- +21 more
-
Palo Alto, California
- +8 more
Dec 21, 2021
Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD
Recruiting
- Mucopolysaccharidosis Disorders
- +28 more
- Stem Cell Transplantation
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Nov 1, 2022
The Natural History of Metachromatic Leukodystrophy
Recruiting
- MLD
- +26 more
- Palliative Care
- Hematopoetic Stem Cell Transplantation
-
Pittsburgh, PennsylvaniaThe Program for the Study of Neurodevelopment in Rare Disorders,
Nov 2, 2021
Fitness and Lung Function Among Survivors of Heart Transplant,
Not yet recruiting
- Chronic Lung Disease
- +3 more
- Physical activity
- (no location specified)
Mar 25, 2022
Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Recruiting
- Primary Immunodeficiency (PID)
- +4 more
- data collection
-
Pittsburgh, PennsylvaniaUPMC Children's Hospital of Pittsburgh
Feb 9, 2022
Collecting Medical Information and Tissue Samples From
Recruiting
- Islet Cell Tumor
- +2 more
- medical chart review
- +2 more
-
Rochester, MinnesotaMayo Clinic Cancer Center
Sep 28, 2021
Metachromatic Leukodystrophy, Adrenoleukodystrophy Trial in Shenzhen (transduced CD34+ hematopoietic stem cell)
Recruiting
- Metachromatic Leukodystrophy
- Adrenoleukodystrophy
- transduced CD34+ hematopoietic stem cell
-
Shenzhen, Guangdong, ChinaShenzhen Second People's Hospital, The First Affiliated Hospital
May 25, 2022
Lysosomal Storage Disease, Metachromatic Leukodystrophy Trial in Milan (OTL-200 Gene Therapy)
Active, not recruiting
- Lysosomal Storage Disease
- Metachromatic Leukodystrophy
- OTL-200 Gene Therapy
-
Milan, ItalyOspedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 4, 2022
Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (drug, procedure,
Completed
- Adrenoleukodystrophy
- +8 more
- Clofarabine
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Jul 10, 2019
Lysosomal Storage Diseases, Metachromatic Leukodystrophy Trial in Milan (OTL-200)
Recruiting
- Lysosomal Storage Diseases
- Metachromatic Leukodystrophy
- OTL-200
-
Milan, ItalyOspedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 16, 2022
Metastatic Pancreatic Cancer Trial in Rotterdam (MesoPher, Mitazalimab)
Recruiting
- Metastatic Pancreatic Cancer
- MesoPher
- Mitazalimab
-
Rotterdam, Zuid-Holland, NetherlandsErasmus MC
Dec 6, 2022
Sickle Cell Disease Trial (Plant-based omega-3-FA)
Not yet recruiting
- Sickle Cell Disease
- Plant-based omega-3-FA
- (no location specified)
Mar 6, 2023
Single Cell Mutations inPanel of Known Oncogenes in NSCLC
Recruiting
- NSCLC
- Tapestry technology
-
Monza, MB, ItalyFondazione IRCCS San Gerardo dei Tintori
Sep 15, 2023
Recurrent Severe Aplastic Anemia, Refractory Severe Aplastic Anemia Trial in Duarte (biological, procedure, drug, other)
Not yet recruiting
- Recurrent Severe Aplastic Anemia
- Refractory Severe Aplastic Anemia
- Anti-Thymocyte Globulin
- +7 more
-
Duarte, CaliforniaCity of Hope Medical Center
Feb 23, 2023
Leukodystrophy: An Observational Study at Sohag University
Not yet recruiting
- Children With Leukodystrophy
- MRI
- (no location specified)
Mar 2, 2021
The Gut Virome asTrigger for IBD: From Metagenomics to
Recruiting
- IBD
- Additional biopsies collection
-
Milan, ItalyIRCCS Ospedale San Raffaele
Jun 7, 2023
Acute Myeloid Leukemia, MDS, Myeloproliferative Tumor Trial in Boston (CIML NK, Fludarabine, Cyclophosphamide)
Recruiting
- Acute Myeloid Leukemia
- +3 more
- CIML NK
- +2 more
-
Boston, Massachusetts
- +1 more
Jan 6, 2023