Mucopolysaccharidoses
Showing 26 - 50 of 164
Examinations for Asymptomatic MPS I Infants in Taiwan
Recruiting
- MPS I
- MPS I
-
Taipei, TaiwanMackay Memorial Hospital
Mar 2, 2022
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],
Recruiting
- Mucopolysaccharidosis I
- +2 more
- Adalimumab Injection [Humira]
- Saline Solution for Injection
-
Torrance, CaliforniaThe Lundquist Institute at Harbor-UCLA Medical Center
Aug 9, 2022
Mucopolysaccharidosis Type II (MPS II) Trial in Oakland, Montréal (RGX-121)
Recruiting
- Mucopolysaccharidosis Type II (MPS II)
- RGX-121
-
Oakland, California
- +1 more
Oct 6, 2022
Respiratory Cathepsins, Proteases Inhibitors and
Completed
- Mucopolysaccharidoses
- Sputum
- Tracheal aspiration
-
Angers, France
- +6 more
Jan 3, 2022
Study of Patients With MPS IIIB Treated With ABO-101
Terminated
- Mucopolysaccharidosis III-B
- ABO-101
-
Columbus, Ohio
- +2 more
May 25, 2022
Mucopolysaccharidosis Type II Natural History
Completed
- Mucopolysaccharidosis II
-
Pittsburgh, Pennsylvania
- +2 more
Apr 22, 2022
Natural History of Atypical Morquio A Disease
Active, not recruiting
- Mucopolysaccharidosis IV A
- Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]
-
Bordeaux, Aquitaine, FranceRheumatology department - Bordeaux University Hospital
Feb 15, 2022
MPS IIIA, Sanfilippo Syndrome, Sanfilippo A Trial in Australia, Spain, United States (ABO-102)
Active, not recruiting
- MPS IIIA
- +3 more
- ABO-102
-
Columbus, Ohio
- +4 more
Nov 8, 2022
Mucopolysaccharidosis Type II (MPS II) Trial in Brazil, United States (RGX-121)
Recruiting
- Mucopolysaccharidosis Type II (MPS II)
- RGX-121
-
Oakland, California
- +4 more
Dec 22, 2022
Myozyme® and of Aldurazyme® in Male and Female Participants of
Recruiting
- Pompe Disease
- Mucopolysaccharidosis Type I (MPS I)
-
Italy, ItalyInvestigational site Italy
May 3, 2022
(LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX
Active, not recruiting
- Hemophilia B
- +2 more
- SB-318
- +2 more
-
Oakland, California
- +4 more
Jan 30, 2023
Mucopolysaccharidosis II, Hunter Syndrome Trial in Pusan, Seoul (GC1123)
Not yet recruiting
- Mucopolysaccharidosis II
- Hunter Syndrome
- GC1123
-
Pusan, Korea, Republic of
- +2 more
Jun 16, 2022
MPS-IH (Hurler Syndrome) Trial in Worldwide (Experimental: OTL-203, Active Comparator: Allo-HSCT)
Not yet recruiting
- MPS-IH (Hurler Syndrome)
- Experimental: OTL-203
- Active Comparator: Allo-HSCT
-
Oakland, California
- +6 more
Nov 27, 2023
Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)
Terminated
- Mucopolysaccharidosis Type 3 B
- rAAV9.CMV.hNAGLU
-
Columbus, Ohio
- +3 more
Apr 29, 2022
Mucopolysaccharidosis II Trial in Salt Lake City, Fairfax (Genetic HMI-203)
Recruiting
- Mucopolysaccharidosis II
- Genetic HMI-203
-
Oakland, California
- +5 more
Jan 26, 2023
Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)
Active, not recruiting
- Mucopolysaccharidosis Type IIIB
- MPS III B
- AX 250
-
Oakland, California
- +7 more
Jan 16, 2023
Non-invasive Functional Assessment and Pathogenesis of Morquio A
Recruiting
- Mucopolysaccharidosis IV Type A
- +2 more
- Imaging, gait analysis, growth, joint test, hearing test, questionnaire, etc.
-
Wilmington, DelawareNemours Children's Health, Delaware Valley
Mar 9, 2022
Mucopolysaccharidosis II, MPS II Trial in United States (SB-913)
Terminated
- Mucopolysaccharidosis II
- MPS II
- SB-913
-
Oakland, California
- +4 more
Oct 21, 2022
Mucopolysaccharidosis I, Hurler's Syndrome, Hurler-Scheie Syndrome Trial in Rome (Aldurazyme (laronidase))
Recruiting
- Mucopolysaccharidosis I
- +3 more
- Aldurazyme (laronidase)
-
Rome, ItalyDipartimento di Scienze Pediatriche Medico - Chirurgiche e Neuro
Mar 28, 2022