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Mucopolysaccharidoses

Showing 26 - 50 of 164

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Examinations for Asymptomatic MPS I Infants in Taiwan

Recruiting
  • MPS I
  • MPS I
  • Taipei, Taiwan
    Mackay Memorial Hospital
Mar 2, 2022

Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],

Recruiting
  • Mucopolysaccharidosis I
  • +2 more
  • Adalimumab Injection [Humira]
  • Saline Solution for Injection
  • Torrance, California
    The Lundquist Institute at Harbor-UCLA Medical Center
Aug 9, 2022

Mucopolysaccharidosis II Trial in Japan (JR-141)

Completed
  • Mucopolysaccharidosis II
  • Gifu, Japan
  • +7 more
Nov 10, 2022

Mucopolysaccharidosis I Trial in Brazil, Japan, United States (JR-171)

Active, not recruiting
  • Mucopolysaccharidosis I
  • Oakland, California
  • +4 more
Aug 16, 2022

Mucopolysaccharidosis Type II (MPS II) Trial in Oakland, Montréal (RGX-121)

Recruiting
  • Mucopolysaccharidosis Type II (MPS II)
  • RGX-121
  • Oakland, California
  • +1 more
Oct 6, 2022

Respiratory Cathepsins, Proteases Inhibitors and

Completed
  • Mucopolysaccharidoses
  • Sputum
  • Tracheal aspiration
  • Angers, France
  • +6 more
Jan 3, 2022

Mucopolysaccharidosis I Trial in Brazil, Japan, United States (JR-171)

Completed
  • Mucopolysaccharidosis I
  • Oakland, California
  • +5 more
Aug 16, 2022

Mucopolysaccharidosis II Trial in Netherlands, United States (DNL310)

Recruiting
  • Mucopolysaccharidosis II
  • Oakland, California
  • +4 more
Nov 14, 2022

Study of Patients With MPS IIIB Treated With ABO-101

Terminated
  • Mucopolysaccharidosis III-B
  • ABO-101
  • Columbus, Ohio
  • +2 more
May 25, 2022

Mucopolysaccharidosis Type II Natural History

Completed
  • Mucopolysaccharidosis II
    • Pittsburgh, Pennsylvania
    • +2 more
    Apr 22, 2022

    Mucopolysaccharidosis II Trial in Worldwide (JR-141, Idursulfase, JR-141 or Idursulfase)

    Recruiting
    • Mucopolysaccharidosis II
    • Oakland, California
    • +8 more
    Dec 2, 2022

    Natural History of Atypical Morquio A Disease

    Active, not recruiting
    • Mucopolysaccharidosis IV A
    • Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]
    • Bordeaux, Aquitaine, France
      Rheumatology department - Bordeaux University Hospital
    Feb 15, 2022

    MPS IIIA, Sanfilippo Syndrome, Sanfilippo A Trial in Australia, Spain, United States (ABO-102)

    Active, not recruiting
    • MPS IIIA
    • +3 more
    • ABO-102
    • Columbus, Ohio
    • +4 more
    Nov 8, 2022

    Mucopolysaccharidosis Type II (MPS II) Trial in Brazil, United States (RGX-121)

    Recruiting
    • Mucopolysaccharidosis Type II (MPS II)
    • RGX-121
    • Oakland, California
    • +4 more
    Dec 22, 2022

    Myozyme® and of Aldurazyme® in Male and Female Participants of

    Recruiting
    • Pompe Disease
    • Mucopolysaccharidosis Type I (MPS I)
      • Italy, Italy
        Investigational site Italy
      May 3, 2022

      (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

      Active, not recruiting
      • Hemophilia B
      • +2 more
      • SB-318
      • +2 more
      • Oakland, California
      • +4 more
      Jan 30, 2023

      Mucopolysaccharidosis II, Hunter Syndrome Trial in Pusan, Seoul (GC1123)

      Not yet recruiting
      • Mucopolysaccharidosis II
      • Hunter Syndrome
      • GC1123
      • Pusan, Korea, Republic of
      • +2 more
      Jun 16, 2022

      MPS-IH (Hurler Syndrome) Trial in Worldwide (Experimental: OTL-203, Active Comparator: Allo-HSCT)

      Not yet recruiting
      • MPS-IH (Hurler Syndrome)
      • Experimental: OTL-203
      • Active Comparator: Allo-HSCT
      • Oakland, California
      • +6 more
      Nov 27, 2023

      Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)

      Terminated
      • Mucopolysaccharidosis Type 3 B
      • rAAV9.CMV.hNAGLU
      • Columbus, Ohio
      • +3 more
      Apr 29, 2022

      Mucopolysaccharidosis II Trial in Salt Lake City, Fairfax (Genetic HMI-203)

      Recruiting
      • Mucopolysaccharidosis II
      • Genetic HMI-203
      • Oakland, California
      • +5 more
      Jan 26, 2023

      Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)

      Active, not recruiting
      • Mucopolysaccharidosis Type IIIB
      • MPS III B
      • AX 250
      • Oakland, California
      • +7 more
      Jan 16, 2023

      Non-invasive Functional Assessment and Pathogenesis of Morquio A

      Recruiting
      • Mucopolysaccharidosis IV Type A
      • +2 more
      • Imaging, gait analysis, growth, joint test, hearing test, questionnaire, etc.
      • Wilmington, Delaware
        Nemours Children's Health, Delaware Valley
      Mar 9, 2022

      Mucopolysaccharidosis II, MPS II Trial in United States (SB-913)

      Terminated
      • Mucopolysaccharidosis II
      • MPS II
      • SB-913
      • Oakland, California
      • +4 more
      Oct 21, 2022

      Mucopolysaccharidosis I, Hurler's Syndrome, Hurler-Scheie Syndrome Trial in Rome (Aldurazyme (laronidase))

      Recruiting
      • Mucopolysaccharidosis I
      • +3 more
      • Aldurazyme (laronidase)
      • Rome, Italy
        Dipartimento di Scienze Pediatriche Medico - Chirurgiche e Neuro
      Mar 28, 2022