You have 9 free searches left this month | for more free features.

Mucopolysaccharidoses

Showing 151 - 164 of 164

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Psychological Concomitants of Morquio Syndrome (The MAP Study)

Completed
  • Morquio Disease
  • Mucopolysaccharidosis IV
    • Decatur, Georgia
      Emory University
    Dec 2, 2013

    Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Puerto Rico, United States (BMN 110)

    Approved for marketing
    • Mucopolysaccharidosis IVA
    • +2 more
    • BMN 110
    • Birmingham, Alabama
    • +24 more
    Mar 31, 2014

    Detect Unrecognized Mucopolysaccharidosis in Children Visiting

    Terminated
    • Mucopolysaccharidoses
    • +4 more
    • Dried blood spot test for MPS
    • New Brunswick, New Jersey
    • +1 more
    May 23, 2013

    Intraocular Pressure in MPS by Use of Ocular Response Analyzer.

    Unknown status
    • Mucopolysaccharidosis
    • Fabry Disease
      • Mainz, Germany
        Department of Ophthalmology, University Medical Center, Johannes
      Feb 28, 2013

      Spinal Cord Compression, Mucopolysaccharidosis I, Hurler-Scheie Syndrome Trial in Torrance, Helsinki (laronidase)

      Terminated
      • Spinal Cord Compression
      • +4 more
      • Torrance, California
      • +1 more
      Feb 19, 2013

      Mucopolysaccharidosis I, Lysosomal Storage Diseases, Spinal Cord Compression Trial in Torrance, Helsinki (laronidase)

      Terminated
      • Mucopolysaccharidosis I
      • +2 more
      • Torrance, California
      • +1 more
      Feb 20, 2013

      Mucopolysaccharidosis Trial in Teharn (Conditioning regimen, Graft-versus-host disease (GVHD) prophylaxis, Stem Cell

      Unknown status
      • Mucopolysaccharidosis
      • Conditioning regimen
      • +2 more
      • Teharn, Tehran, Iran, Islamic Republic of
        Hematology-Oncology & SCT Research Center
      May 31, 2012

      Mucopolysaccharidosis VI, Maroteaux-Lamy Syndrome Trial in France, Portugal, United States (Naglazyme)

      Completed
      • Mucopolysaccharidosis VI
      • Maroteaux-Lamy Syndrome
      • Los Angeles, California
      • +3 more
      Jul 19, 2011

      Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase, Placebo/rhASB)

      Completed
      • Mucopolysaccharidosis VI
      • N-acetylgalactosamine 4-sulfatase
      • Placebo/rhASB
      • Novato, California
        BioMarin Pharmaceutical Inc.
      Jan 26, 2010

      Mucopolysaccharidosis VI Trial in Novato (Placebo, N-acetylgalactosamine 4-sulfatase)

      Completed
      • Mucopolysaccharidosis VI
      • Placebo
      • N-acetylgalactosamine 4-sulfatase
      • Novato, California
        BioMarin Pharmaceutical Inc.
      Dec 18, 2009

      Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase)

      Completed
      • Mucopolysaccharidosis VI
      • N-acetylgalactosamine 4-sulfatase
      • Novato, California
        BioMarin Pharmaceutical Inc.
      Aug 24, 2009

      Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase)

      Completed
      • Mucopolysaccharidosis VI
      • N-acetylgalactosamine 4-sulfatase
      • Novato, California
        BioMarin Pharmaceutical Inc.
      Nov 2, 2006

      Mucopolysaccharidosis II Trial in Minneapolis (lymphocyte gene therapy)

      Completed
      • Mucopolysaccharidosis II
      • lymphocyte gene therapy
      • Minneapolis, Minnesota
        University of Minnesota Medical School
      Jun 23, 2005

      Pulmonary Complications in Pediatric Storage Disorders

      Unknown status
      • I Cell Disease
      • +11 more
        • Minneapolis, Minnesota
          Fairview University Medical Center
        Jun 23, 2005