Mucopolysaccharidoses
Showing 151 - 164 of 164
Psychological Concomitants of Morquio Syndrome (The MAP Study)
Completed
- Morquio Disease
- Mucopolysaccharidosis IV
-
Decatur, GeorgiaEmory University
Dec 2, 2013
Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Puerto Rico, United States (BMN 110)
Approved for marketing
- Mucopolysaccharidosis IVA
- +2 more
- BMN 110
-
Birmingham, Alabama
- +24 more
Mar 31, 2014
Detect Unrecognized Mucopolysaccharidosis in Children Visiting
Terminated
- Mucopolysaccharidoses
- +4 more
- Dried blood spot test for MPS
-
New Brunswick, New Jersey
- +1 more
May 23, 2013
Intraocular Pressure in MPS by Use of Ocular Response Analyzer.
Unknown status
- Mucopolysaccharidosis
- Fabry Disease
-
Mainz, GermanyDepartment of Ophthalmology, University Medical Center, Johannes
Feb 28, 2013
Mucopolysaccharidosis Trial in Teharn (Conditioning regimen, Graft-versus-host disease (GVHD) prophylaxis, Stem Cell
Unknown status
- Mucopolysaccharidosis
- Conditioning regimen
- +2 more
-
Teharn, Tehran, Iran, Islamic Republic ofHematology-Oncology & SCT Research Center
May 31, 2012
Mucopolysaccharidosis VI, Maroteaux-Lamy Syndrome Trial in France, Portugal, United States (Naglazyme)
Completed
- Mucopolysaccharidosis VI
- Maroteaux-Lamy Syndrome
-
Los Angeles, California
- +3 more
Jul 19, 2011
Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase, Placebo/rhASB)
Completed
- Mucopolysaccharidosis VI
- N-acetylgalactosamine 4-sulfatase
- Placebo/rhASB
-
Novato, CaliforniaBioMarin Pharmaceutical Inc.
Jan 26, 2010
Mucopolysaccharidosis VI Trial in Novato (Placebo, N-acetylgalactosamine 4-sulfatase)
Completed
- Mucopolysaccharidosis VI
- Placebo
- N-acetylgalactosamine 4-sulfatase
-
Novato, CaliforniaBioMarin Pharmaceutical Inc.
Dec 18, 2009
Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase)
Completed
- Mucopolysaccharidosis VI
- N-acetylgalactosamine 4-sulfatase
-
Novato, CaliforniaBioMarin Pharmaceutical Inc.
Aug 24, 2009
Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase)
Completed
- Mucopolysaccharidosis VI
- N-acetylgalactosamine 4-sulfatase
-
Novato, CaliforniaBioMarin Pharmaceutical Inc.
Nov 2, 2006
Mucopolysaccharidosis II Trial in Minneapolis (lymphocyte gene therapy)
Completed
- Mucopolysaccharidosis II
- lymphocyte gene therapy
-
Minneapolis, MinnesotaUniversity of Minnesota Medical School
Jun 23, 2005
Pulmonary Complications in Pediatric Storage Disorders
Unknown status
- I Cell Disease
- +11 more
-
Minneapolis, MinnesotaFairview University Medical Center
Jun 23, 2005