RPE65
Showing 1 - 25 of 162
To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
Not yet recruiting
- To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
- (no location specified)
Aug 29, 2023
Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in Beijing (FT-001 Low Dose, FT-001 Mid Dose, FT-001 High Dose)
Recruiting
- Biallelic RPE65 Mutation-associated Retinal Dystrophy
- FT-001 Low Dose
- +2 more
-
Beijing, Beijing, ChinaPeking Union Medical College Hospital
May 11, 2023
Leber Congenital Amaurosis Trial in Shanghai (HG004)
Recruiting
- Leber Congenital Amaurosis
- HG004
-
Shanghai, Shanghai, ChinaXinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023
Leber Congenital Amaurosis Associated With Mutations in RPE65
Recruiting
- Leber Congenital Amaurosis
-
Ann Arbor, Michigan
- +1 more
Apr 7, 2022
Leber Congenital Amaurosis Trial in Shanghai (HG004)
Recruiting
- Leber Congenital Amaurosis
- HG004
-
Shanghai, Shanghai, ChinaXinhua Hospital affiliated with Shanghai Jiao Tong University Sc
Sep 26, 2023
Inherited Retinal Dystrophy Due to RPE65 Mutations, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia
Active, not recruiting
- Inherited Retinal Dystrophy Due to RPE65 Mutations
- Leber Congenital Amaurosis
- AAV2-hRPE65v2,voretigene neparvovec-rzyl
-
Iowa City, Iowa
- +1 more
Dec 9, 2021
Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)
Active, not recruiting
- Inherited Retinal Dystrophy Due to RPE65 Mutations
- AAV2-hRPE65v2
- (no location specified)
Dec 9, 2021
Amaurosis of Leber, Retinal Diseases Trial in Gainesville, Philadelphia (rAAV2-CBSB-hRPE65)
Active, not recruiting
- Amaurosis of Leber
- Retinal Diseases
- rAAV2-CBSB-hRPE65
-
Gainesville, Florida
- +1 more
Dec 13, 2021
Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in United States (AAV2-hRPE65v2,voretigene
Active, not recruiting
- Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
- AAV2-hRPE65v2,voretigene neparvovec-rzyl
-
Los Angeles, California
- +9 more
Oct 22, 2021
Leber Congenital Amaurosis Trial in Philadelphia (voretigene neparvovec-rzyl)
Completed
- Leber Congenital Amaurosis
- voretigene neparvovec-rzyl
-
Philadelphia, PennsylvaniaThe Children's Hospital of Philadelphia
Oct 30, 2020
Natural History of Eye Diseases Related to ABCA4 Mutations
Active, not recruiting
- Retinal Degeneration
- ABCA4-Related Retinopathies
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Feb 2, 2023
Pulmonary Arterial Hypertension (PAH) Trial in Lahore (aerobic exercises, active alternating movements for the upper limbs)
Not yet recruiting
- Pulmonary Arterial Hypertension (PAH)
- aerobic exercises
- active alternating movements for the upper limbs
-
Lahore, Punjab, PakistanNational hospital and Ittefaq hospital in Lahore
Jul 7, 2023
Panic Attacks and Disorders Trial (Exercise intervention, Placebo)
Completed
- Panic Attacks and Disorders
- Exercise intervention
- Placebo
- (no location specified)
Oct 2, 2023
New Tools to Estimate Intensity of Adapted Physical Activity
Not yet recruiting
- Ageing
- Elderly
-
Nice, FranceGUERIN
Feb 21, 2023
Choroideremia Trial in Edmonton (rAAV2.REP1 vector)
Completed
- Choroideremia
- rAAV2.REP1 vector
-
Edmonton, Alberta, CanadaUniversity of Alberta
May 16, 2022
Physical Fitness Trial in Qingdao (Heart rate based HIIT, VIFT speed-based HIIT with mechanical work)
Recruiting
- Physical Fitness
- Heart rate based HIIT
- VIFT speed-based HIIT with mechanical work
-
Qingdao, Shandong, ChinaLingling ZHANG
Jan 10, 2023
Mild Cognitive Impairment Trial in Hamilton (Self- determined Intensity Interval Training)
Not yet recruiting
- Mild Cognitive Impairment
- Self- determined Intensity Interval Training
-
Hamilton, Ontario, CanadaMcMaster Unviersity
Jan 13, 2023
Endocarditis, Heart Valve Diseases Trial in Tromsø (Aerobic interval training)
Recruiting
- Endocarditis
- Heart Valve Diseases
- Aerobic interval training
-
Tromsø, NorwayUniversity Hospital of North Norway
Jan 18, 2023
Leber Congenital Amaurosis Trial in Jerusalem (rAAV2-hRPE65)
Completed
- Leber Congenital Amaurosis
- rAAV2-hRPE65
-
Jerusalem, IsraelHadassah Medical Organization
Apr 8, 2018
Strength Training Trial in Tel Aviv (Autonomy and Perceptions Approach to Resistance Training (APART), Standard prescription)
Recruiting
- Strength Training
- Autonomy and Perceptions Approach to Resistance Training (APART)
- Standard prescription
-
Tel Aviv, IsraelTel Aviv University
Oct 18, 2022
Cold-water Immersion, Protein-carbohydrates Supplementation, Active Recovery Trial in Puerto Real (Cold-water immersion,
Completed
- Cold-water Immersion
- +3 more
- Cold-water immersion
- +3 more
-
Puerto Real, Cadiz, SpainScience of Education Faculty
Mar 27, 2023
Retinitis Pigmentosa Trial in Bangkoknoi (BM-MSC)
Completed
- Retinitis Pigmentosa
- BM-MSC
-
Bangkoknoi, Bangkok, ThailandSiriraj Hospital Mahidol University
Aug 31, 2021
Coronary Artery Disease Trial in Abbottabad (Power Walking, Standardized Outpatient Cardiac Rehabilitation)
Not yet recruiting
- Coronary Artery Disease
- Power Walking
- Standardized Outpatient Cardiac Rehabilitation
-
Abbottābād, Khyber PkahtoonKhwa, PakistanWomen Institute of Rehabilitation Sciences (WIRS) and Jinnah Int
Jan 22, 2023