You have 9 free searches left this month | for more free features.

RPE65

Showing 1 - 25 of 162

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)

Not yet recruiting
  • To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
  • (no location specified)
Aug 29, 2023

Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in Beijing (FT-001 Low Dose, FT-001 Mid Dose, FT-001 High Dose)

Recruiting
  • Biallelic RPE65 Mutation-associated Retinal Dystrophy
  • FT-001 Low Dose
  • +2 more
  • Beijing, Beijing, China
    Peking Union Medical College Hospital
May 11, 2023

Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023

Leber Congenital Amaurosis Associated With Mutations in RPE65

Recruiting
  • Leber Congenital Amaurosis
    • Ann Arbor, Michigan
    • +1 more
    Apr 7, 2022

    Leber Congenital Amaurosis Trial (HG004)

    Not yet recruiting
    • Leber Congenital Amaurosis
    • (no location specified)
    Jun 13, 2023

    Leber Congenital Amaurosis Trial in Shanghai (HG004)

    Recruiting
    • Leber Congenital Amaurosis
    • HG004
    • Shanghai, Shanghai, China
      Xinhua Hospital affiliated with Shanghai Jiao Tong University Sc
    Sep 26, 2023

    Inherited Retinal Dystrophy Due to RPE65 Mutations, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia

    Active, not recruiting
    • Inherited Retinal Dystrophy Due to RPE65 Mutations
    • Leber Congenital Amaurosis
    • AAV2-hRPE65v2,voretigene neparvovec-rzyl
    • Iowa City, Iowa
    • +1 more
    Dec 9, 2021

    Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

    Active, not recruiting
    • Inherited Retinal Dystrophy Due to RPE65 Mutations
    • AAV2-hRPE65v2
    • (no location specified)
    Dec 9, 2021

    Amaurosis of Leber, Retinal Diseases Trial in Gainesville, Philadelphia (rAAV2-CBSB-hRPE65)

    Active, not recruiting
    • Amaurosis of Leber
    • Retinal Diseases
    • rAAV2-CBSB-hRPE65
    • Gainesville, Florida
    • +1 more
    Dec 13, 2021

    Leber Congenital Amaurosis Trial in Ann Arbor, London (AAV RPE65)

    Completed
    • Leber Congenital Amaurosis
    • AAV RPE65
    • Ann Arbor, Michigan
    • +1 more
    Jun 17, 2021

    Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in United States (AAV2-hRPE65v2,voretigene

    Active, not recruiting
    • Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
    • AAV2-hRPE65v2,voretigene neparvovec-rzyl
    • Los Angeles, California
    • +9 more
    Oct 22, 2021

    Leber Congenital Amaurosis Trial in Philadelphia (voretigene neparvovec-rzyl)

    Completed
    • Leber Congenital Amaurosis
    • voretigene neparvovec-rzyl
    • Philadelphia, Pennsylvania
      The Children's Hospital of Philadelphia
    Oct 30, 2020

    Natural History of Eye Diseases Related to ABCA4 Mutations

    Active, not recruiting
    • Retinal Degeneration
    • ABCA4-Related Retinopathies
      • Bethesda, Maryland
        National Institutes of Health Clinical Center
      Feb 2, 2023

      Pulmonary Arterial Hypertension (PAH) Trial in Lahore (aerobic exercises, active alternating movements for the upper limbs)

      Not yet recruiting
      • Pulmonary Arterial Hypertension (PAH)
      • aerobic exercises
      • active alternating movements for the upper limbs
      • Lahore, Punjab, Pakistan
        National hospital and Ittefaq hospital in Lahore
      Jul 7, 2023

      Panic Attacks and Disorders Trial (Exercise intervention, Placebo)

      Completed
      • Panic Attacks and Disorders
      • Exercise intervention
      • Placebo
      • (no location specified)
      Oct 2, 2023

      New Tools to Estimate Intensity of Adapted Physical Activity

      Not yet recruiting
      • Ageing
      • Elderly
      • Nice, France
        GUERIN
      Feb 21, 2023

      Choroideremia Trial in Edmonton (rAAV2.REP1 vector)

      Completed
      • Choroideremia
      • rAAV2.REP1 vector
      • Edmonton, Alberta, Canada
        University of Alberta
      May 16, 2022

      Physical Fitness Trial in Qingdao (Heart rate based HIIT, VIFT speed-based HIIT with mechanical work)

      Recruiting
      • Physical Fitness
      • Heart rate based HIIT
      • VIFT speed-based HIIT with mechanical work
      • Qingdao, Shandong, China
        Lingling ZHANG
      Jan 10, 2023

      Mild Cognitive Impairment Trial in Hamilton (Self- determined Intensity Interval Training)

      Not yet recruiting
      • Mild Cognitive Impairment
      • Self- determined Intensity Interval Training
      • Hamilton, Ontario, Canada
        McMaster Unviersity
      Jan 13, 2023

      Endocarditis, Heart Valve Diseases Trial in Tromsø (Aerobic interval training)

      Recruiting
      • Endocarditis
      • Heart Valve Diseases
      • Aerobic interval training
      • Tromsø, Norway
        University Hospital of North Norway
      Jan 18, 2023

      Leber Congenital Amaurosis Trial in Jerusalem (rAAV2-hRPE65)

      Completed
      • Leber Congenital Amaurosis
      • rAAV2-hRPE65
      • Jerusalem, Israel
        Hadassah Medical Organization
      Apr 8, 2018

      Strength Training Trial in Tel Aviv (Autonomy and Perceptions Approach to Resistance Training (APART), Standard prescription)

      Recruiting
      • Strength Training
      • Autonomy and Perceptions Approach to Resistance Training (APART)
      • Standard prescription
      • Tel Aviv, Israel
        Tel Aviv University
      Oct 18, 2022

      Cold-water Immersion, Protein-carbohydrates Supplementation, Active Recovery Trial in Puerto Real (Cold-water immersion,

      Completed
      • Cold-water Immersion
      • +3 more
      • Cold-water immersion
      • +3 more
      • Puerto Real, Cadiz, Spain
        Science of Education Faculty
      Mar 27, 2023

      Retinitis Pigmentosa Trial in Bangkoknoi (BM-MSC)

      Completed
      • Retinitis Pigmentosa
      • BM-MSC
      • Bangkoknoi, Bangkok, Thailand
        Siriraj Hospital Mahidol University
      Aug 31, 2021

      Coronary Artery Disease Trial in Abbottabad (Power Walking, Standardized Outpatient Cardiac Rehabilitation)

      Not yet recruiting
      • Coronary Artery Disease
      • Power Walking
      • Standardized Outpatient Cardiac Rehabilitation
      • Abbottābād, Khyber PkahtoonKhwa, Pakistan
        Women Institute of Rehabilitation Sciences (WIRS) and Jinnah Int
      Jan 22, 2023