Transfusion dependent
Showing 51 - 75 of 5,970
MDS Trial in Tampa (cenersen, Dexamethasone)
Terminated
- Myelodysplastic Syndromes
-
Tampa, FloridaH. Lee Moffitt Cancer Center & Research Institute
Feb 18, 2021
Beta Thalassemia Intermedia Trial in Worldwide (IONIS TMPRSS6-LRx)
Active, not recruiting
- Beta Thalassemia Intermedia
-
Camperdown, New South Wales, Australia
- +18 more
Sep 23, 2022
MDS, Del(5Q), Anemia Trial in Italy (Luspatercept Injection [Reblozyl])
Recruiting
- Myelodysplastic Syndromes
- +3 more
- Luspatercept Injection [Reblozyl]
-
Alessandria, Italy
- +22 more
Jun 20, 2023
Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)
Recruiting
- Beta-Thalassemia
- Sirolimus 0.5 mg
-
Ferrara, FE, Italy
- +3 more
Nov 11, 2021
Primary Myelofibrosis (PMF), Post-polycythemia Vera (Post-PV) Myelofibrosis, Postessential Thrombocythemia (Post-ET)
Completed
- Primary Myelofibrosis (PMF)
- +2 more
-
Phoenix, Arizona
- +12 more
Jan 12, 2021
Endocrine Function During Deferasirox Therapy
Completed
- Iron Overload
- +2 more
-
Naples, ItalyUniversità degli Studi della Campania Luigi Vanvitelli
Aug 13, 2020
Transfusion Dependent Thalassemia Trial in Worldwide (Mirasol Red Blood Cells (MIR RBCs), Reference Red Blood Cells (REF RBCs))
Terminated
- Transfusion Dependent Thalassemia
- Mirasol Red Blood Cells (MIR RBCs)
- Reference Red Blood Cells (REF RBCs)
-
Oakland, California
- +8 more
Mar 31, 2021
Beta Thalassemia Major Anemia, Iron Overload Trial in Cairo, Jakarta (Deferiprone oral solution, Placebo)
Completed
- Beta Thalassemia Major Anemia
- Iron Overload
- Deferiprone oral solution
- Placebo
-
Cairo, Egypt
- +3 more
Feb 9, 2021
Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in
Recruiting
- Non-transfusion-dependent Thalassemia
- +2 more
- SLN124
- Placebo
-
Düsseldorf, Germany
- +19 more
Mar 18, 2022
Hereditary Hemorrhagic Telangiectasia, Idiopathic Vascular Ectasia Trial in Cleveland (Pomalidomide)
Completed
- Hereditary Hemorrhagic Telangiectasia
- Idiopathic Vascular Ectasia
-
Cleveland, OhioCleveland Clinic
Jul 13, 2020
Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome Trial in Bulgaria, United Kingdom (SLN124 is a GalNAc
Withdrawn
- Non-transfusion-dependent Thalassemia
- Low Risk Myelodysplastic Syndrome
- SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as Placebo
-
Kyustendil, Bulgaria
- +4 more
Apr 23, 2020
Anemia, Myelodysplastic Syndrome Trial in Seattle (Deferasirox, Laboratory Biomarker Analysis)
Terminated
- Anemia
- Myelodysplastic Syndrome
- Deferasirox
- Laboratory Biomarker Analysis
-
Seattle, WashingtonFred Hutch/University of Washington Cancer Consortium
Jun 12, 2020
MDS Trial in France, Germany, United States (Oral rigosertib)
Completed
- Myelodysplastic Syndromes
- Oral rigosertib
-
Stanford, California
- +13 more
Jun 15, 2021
Myelodysplastic Syndrome Trial in New York (rigosertib)
Withdrawn
- Myelodysplastic Syndrome
-
New York, New YorkColumbia University Medical Center
Jun 29, 2020
MDS Trial in Worldwide (Luspatercept, Epoetin Alfa)
Not yet recruiting
- Myelodysplastic Syndromes
- Luspatercept
- Epoetin Alfa
-
Concord, California
- +100 more
Jul 20, 2023
Chronic Iron Overload Trial in Worldwide (Deferiprone, Deferasirox)
Completed
- Chronic Iron Overload
-
Lushnjë, Albania
- +21 more
Apr 8, 2021
Non-transfusion Dependent Thalassemia Trial in Worldwide (deferasirox)
Completed
- Non-transfusion Dependent Thalassemia
-
Nanning, Guangxi, China
- +10 more
Sep 19, 2019
ß-thalassemia, Ineffective Erythropoiesis Trial in Worldwide (PTG-300)
Completed
- β-thalassemia
- Ineffective Erythropoiesis
-
Oakland, California
- +15 more
Jul 12, 2021
Aplastic Anemia Trial in Moscow (ICL670, Chelation, No chelation)
Terminated
- Aplastic Anemia
- ICL670
- +2 more
-
Moscow, Russian FederationNovartis Investigative Site
Jul 8, 2019
Erythrocyte Transfusion, Beta-Thalassemia Trial in Worldwide (Luspatercept, Placebo)
Completed
- Erythrocyte Transfusion
- Beta-Thalassemia
- Luspatercept
- Placebo
-
Los Angeles, California
- +72 more
Jan 21, 2022