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Transfusion dependent

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ß-thalassemia, Ineffective Erythropoiesis, Chronic Anemia Trial in Worldwide (PTG-300)

Completed
  • β-thalassemia
  • +2 more
  • Oakland, California
  • +32 more
Jul 13, 2021

MDS Trial in Tampa (cenersen, Dexamethasone)

Terminated
  • Myelodysplastic Syndromes
  • Tampa, Florida
    H. Lee Moffitt Cancer Center & Research Institute
Feb 18, 2021

Beta Thalassemia Intermedia Trial in Worldwide (IONIS TMPRSS6-LRx)

Active, not recruiting
  • Beta Thalassemia Intermedia
  • Camperdown, New South Wales, Australia
  • +18 more
Sep 23, 2022

MDS, Del(5Q), Anemia Trial in Italy (Luspatercept Injection [Reblozyl])

Recruiting
  • Myelodysplastic Syndromes
  • +3 more
  • Luspatercept Injection [Reblozyl]
  • Alessandria, Italy
  • +22 more
Jun 20, 2023

Beta-Thalassemia Trial in Worldwide (LJPC-401)

Terminated
  • Beta-Thalassemia
  • Oakland, California
  • +21 more
Jul 28, 2021

Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)

Recruiting
  • Beta-Thalassemia
  • Sirolimus 0.5 mg
  • Ferrara, FE, Italy
  • +3 more
Nov 11, 2021

Primary Myelofibrosis (PMF), Post-polycythemia Vera (Post-PV) Myelofibrosis, Postessential Thrombocythemia (Post-ET)

Completed
  • Primary Myelofibrosis (PMF)
  • +2 more
  • Phoenix, Arizona
  • +12 more
Jan 12, 2021

Endocrine Function During Deferasirox Therapy

Completed
  • Iron Overload
  • +2 more
    • Naples, Italy
      Università degli Studi della Campania Luigi Vanvitelli
    Aug 13, 2020

    Iron Overload, Beta-Thalassemia Trial in Worldwide (SP-420)

    Withdrawn
    • Iron Overload
    • Beta-Thalassemia
    • Toronto, Canada
    • +3 more
    Sep 30, 2020

    Transfusion Dependent Thalassemia Trial in Worldwide (Mirasol Red Blood Cells (MIR RBCs), Reference Red Blood Cells (REF RBCs))

    Terminated
    • Transfusion Dependent Thalassemia
    • Mirasol Red Blood Cells (MIR RBCs)
    • Reference Red Blood Cells (REF RBCs)
    • Oakland, California
    • +8 more
    Mar 31, 2021

    Beta Thalassemia Major Anemia, Iron Overload Trial in Cairo, Jakarta (Deferiprone oral solution, Placebo)

    Completed
    • Beta Thalassemia Major Anemia
    • Iron Overload
    • Deferiprone oral solution
    • Placebo
    • Cairo, Egypt
    • +3 more
    Feb 9, 2021

    Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in

    Recruiting
    • Non-transfusion-dependent Thalassemia
    • +2 more
    • Düsseldorf, Germany
    • +19 more
    Mar 18, 2022

    Hereditary Hemorrhagic Telangiectasia, Idiopathic Vascular Ectasia Trial in Cleveland (Pomalidomide)

    Completed
    • Hereditary Hemorrhagic Telangiectasia
    • Idiopathic Vascular Ectasia
    • Cleveland, Ohio
      Cleveland Clinic
    Jul 13, 2020

    Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome Trial in Bulgaria, United Kingdom (SLN124 is a GalNAc

    Withdrawn
    • Non-transfusion-dependent Thalassemia
    • Low Risk Myelodysplastic Syndrome
    • SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as Placebo
    • Kyustendil, Bulgaria
    • +4 more
    Apr 23, 2020

    Anemia, Myelodysplastic Syndrome Trial in Seattle (Deferasirox, Laboratory Biomarker Analysis)

    Terminated
    • Anemia
    • Myelodysplastic Syndrome
    • Seattle, Washington
      Fred Hutch/University of Washington Cancer Consortium
    Jun 12, 2020

    MDS Trial in France, Germany, United States (Oral rigosertib)

    Completed
    • Myelodysplastic Syndromes
    • Oral rigosertib
    • Stanford, California
    • +13 more
    Jun 15, 2021

    Myelodysplastic Syndrome Trial in New York (rigosertib)

    Withdrawn
    • Myelodysplastic Syndrome
    • New York, New York
      Columbia University Medical Center
    Jun 29, 2020

    MDS Trial in Worldwide (Luspatercept, Epoetin Alfa)

    Not yet recruiting
    • Myelodysplastic Syndromes
    • Luspatercept
    • Epoetin Alfa
    • Concord, California
    • +100 more
    Jul 20, 2023

    MDS Trial in Japan (Eltrombopag, Placebo)

    Recruiting
    • Myelodysplastic Syndromes
    • Narita, Chiba, Japan
    • +21 more
    Jan 19, 2023

    Chronic Iron Overload Trial in Worldwide (Deferiprone, Deferasirox)

    Completed
    • Chronic Iron Overload
    • Lushnjë, Albania
    • +21 more
    Apr 8, 2021

    Non-transfusion Dependent Thalassemia Trial in Worldwide (deferasirox)

    Completed
    • Non-transfusion Dependent Thalassemia
    • Nanning, Guangxi, China
    • +10 more
    Sep 19, 2019

    ß-thalassemia, Ineffective Erythropoiesis Trial in Worldwide (PTG-300)

    Completed
    • β-thalassemia
    • Ineffective Erythropoiesis
    • Oakland, California
    • +15 more
    Jul 12, 2021

    MDS Trial in Boston, New York (Tipifarnib)

    Terminated
    • Myelodysplastic Syndromes
    • Boston, Massachusetts
    • +1 more
    Jan 30, 2020

    Aplastic Anemia Trial in Moscow (ICL670, Chelation, No chelation)

    Terminated
    • Aplastic Anemia
    • Moscow, Russian Federation
      Novartis Investigative Site
    Jul 8, 2019

    Erythrocyte Transfusion, Beta-Thalassemia Trial in Worldwide (Luspatercept, Placebo)

    Completed
    • Erythrocyte Transfusion
    • Beta-Thalassemia
    • Los Angeles, California
    • +72 more
    Jan 21, 2022