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X Linked Severe Combined Immunodeficiency

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Severe Combined Immunodeficiency Disease, X-linked Trial in San Francisco, Memphis, Seattle (genetic, drug, device)

Recruiting
  • Severe Combined Immunodeficiency Disease, X-linked
  • CL20-i4-EF1α-hγc-OPT
  • +2 more
  • San Francisco, California
  • +2 more
Jan 9, 2023

X-linked Severe Combined Immunodeficiency (XSCID) Trial run by the National Institute of Allergy and Infectious Diseases (NIAID)

Suspended
  • X-linked Severe Combined Immunodeficiency (XSCID)
  • Bethesda, Maryland
    National Institutes of Health Clinical Center, 9000 Rockville Pi
Aug 24, 2022

X-linked Severe Combined Immunodeficiency Trial in Paris (Gene transfer)

Completed
  • X-linked Severe Combined Immunodeficiency
  • Gene transfer
  • Paris, France
    Hopital Necker
Sep 22, 2021

Severe Combined Immunodeficiency, X-Linked Trial in London (Lentiviral vector transduced CD34+ cells)

Recruiting
  • Severe Combined Immunodeficiency, X-Linked
  • Lentiviral vector transduced CD34+ cells
  • London, Greater London, United Kingdom
    Great Ormond Street Hospital for Children NHS Foundation Trust
Mar 15, 2022

Severe Combined Immunodeficiency, X Linked, Gene Therapy Trial in United Kingdom, United States (autologous CD34+ cell

Recruiting
  • Severe Combined Immunodeficiency, X Linked
  • Gene Therapy
  • autologous CD34+ cell transduced with G2SCID vector
  • Los Angeles, California
  • +4 more
Jul 19, 2022

Evaluation of Patients With Immune Function Abnormalities

Recruiting
  • Chronic Granulomatous Disease (CGD)
  • +3 more
    • Bethesda, Maryland
      National Institutes of Health Clinical Center, 9000 Rockville Pi
    Aug 24, 2022

    Immune Deficiency Disorders, Severe Combined Immunodeficiency, Chronic Granulomatous Disease Trial in Saint Louis (Transplant

    Recruiting
    • Immune Deficiency Disorders
    • +13 more
    • Transplant preparative regimen of alemtuzumab, fludarabine, thiotepa, and melphalan
    • Saint Louis, Missouri
      Washington University
    Apr 25, 2022

    Gene Therapy Trial in Chongqing (Lentiviral Vector Gene Therapy)

    Recruiting
    • Gene Therapy
    • Lentiviral Vector Gene Therapy
    • Chongqing, Chongqing, China
      Children's Hospital of Chongqing Medical University
    Mar 26, 2020

    Genetic Basis of Immunodeficiency

    Recruiting
    • Severe Combined Immunodeficiency
      • Bethesda, Maryland
        National Institutes of Health Clinical Center
      Jan 21, 2023

      Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,

      Recruiting
      • Bone Marrow Failure Syndrome
      • +15 more
      • Thiotepa--single daily dose
      • Thiotepa--escalated dose
      • Gainesville, Florida
        UF Health Shands Children's Hospital
      Jul 8, 2021

      X-Linked Combined Immunodeficiency Diseases Trial run by the NIAID (CD34+ HSCs transduced with the lentivirus vector, VSV-G

      Unknown status
      • X-Linked Combined Immunodeficiency Diseases
      • CD34+ HSCs transduced with the lentivirus vector, VSV-G pseudotyped CL20-4i-EF1α-hγc-OPT
      • +2 more
      • Bethesda, Maryland
        Laboratory of Host Defenses (LHD), National Institute of Allergy
      Dec 3, 2019

      The Experience of Screening for SCID

      Recruiting
      • Severe Combined Immunodeficiency
      • SCID Screening
      • London, United Kingdom
        King's College London
      Dec 6, 2022

      Artemis (DCLRE1C ) Deficient Severe Combined Immunodeficiency Trial in Paris (ARTEGENE drug product)

      Not yet recruiting
      • Artemis (DCLRE1C ) Deficient Severe Combined Immunodeficiency
      • ARTEGENE drug product
      • Paris, France
        Department of Pediatric Immunology, Hematology and Rheumatology
      Sep 26, 2022

      Severe Combined Immunodeficiency Trial in San Francisco (AProArt, CliniMACS® CD34 Reagent System cell sorter device, Busulfan)

      Recruiting
      • Severe Combined Immunodeficiency
      • San Francisco, California
        University of California, San Francisco (UCSF) Children's Hospit
      Feb 4, 2022

      SCID, X Linked Trial in Beijing, Shenzhen (TYF-IL-2Rg gene-modified autologous stem cells)

      Unknown status
      • SCID, X Linked
      • TYF-IL-2Rg gene-modified autologous stem cells
      • Beijing, Beijing, China
      • +2 more
      Sep 18, 2019

      Neonatal Screening of Severe Combined Immunodeficiencies

      Completed
      • Severe Combined Immunodeficiency
      • Neonatal Screening
        • Shanghai, Shanghai, China
          Children's Hospital of Fudan University
        Jan 3, 2022

        Immunodeficiency, Hematopoietic Stem Cell Transplantation Trial run by the National Cancer Institute (NCI) (drug, radiation,

        Recruiting
        • Immunodeficiency
        • Hematopoietic Stem Cell Transplantation
        • Post-Transplant Cyclophosphamide (PTCY)
        • +8 more
        • Bethesda, Maryland
          National Institutes of Health Clinical Center
        Aug 17, 2022

        Severe Combined Immunodeficiency Due to ADA Deficiency Trial in Milan (STRIMVELIS)

        Completed
        • Severe Combined Immunodeficiency Due to ADA Deficiency
        • Milan, Italy
          Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
        Feb 18, 2022

        Severe Combined Immune Deficiency (SCID) Trial run by the National Institute of Allergy and Infectious Diseases (NIAID)

        Enrolling by invitation
        • Severe Combined Immune Deficiency (SCID)
        • Bethesda, Maryland
          National Institutes of Health Clinical Center
        Aug 24, 2022

        Severe Combined Immunodeficiency Due to RAG1 Deficiency Trial in Leiden (Gene therapy)

        Recruiting
        • Severe Combined Immunodeficiency Due to RAG1 Deficiency
        • Gene therapy
        • Leiden, Netherlands
          Leiden University Medical Center
        Dec 3, 2021

        Severe Combined Immunodeficiency Trial in Memphis (drug, device, other)

        Recruiting
        • Severe Combined Immunodeficiency
        • Anti-thymocyte globulin (rabbit)
        • +5 more
        • Memphis, Tennessee
          St. Jude Children's Research Hospital
        Oct 6, 2021

        Haematological Malignancy, Acute Leukemia, MDS Trial in Lyon (Physical activity program)

        Not yet recruiting
        • Haematological Malignancy
        • +5 more
        • Physical activity program
        • Lyon, France
          Institut d'Hématologie et d'Oncologie Pédiatrique
        Mar 25, 2022

        Haematological Malignancy, Acute Leukemia, MDS Trial in Lyon (Physical activity program)

        Withdrawn
        • Haematological Malignancy
        • +5 more
        • Physical activity program
        • Lyon, France
          Institut d'Hématologie et d'Oncologie Pédiatrique
        Feb 10, 2022

        Adenosine Deaminase Deficiency, Autosomal Recessive Disorder, Immune System Disorder Trial in Seattle (procedure, drug, other,

        Completed
        • Adenosine Deaminase Deficiency
        • +6 more
        • Allogeneic Bone Marrow Transplantation
        • +5 more
        • Seattle, Washington
          Fred Hutch/University of Washington Cancer Consortium
        Jul 26, 2019

        Adenosine Deaminase Severe Combined Immune Deficiency Trial (A cryopreserved formulation of autologous mPB CD34+ hematopoietic

        Not yet recruiting
        • Adenosine Deaminase Severe Combined Immune Deficiency
        • A cryopreserved formulation of autologous mPB CD34+ hematopoietic stem and progenitor cells transduced ex vivo with the EFS-ADA lentiviral vector encoding the human ADA enzyme
        • (no location specified)
        Jun 20, 2022