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Zavesca

Showing 1 - 12 of 12

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

GM2 Gangliosidosis, Supportive Care Trial in Kashan, Mashhad, Tehran (Miglustat)

Recruiting
  • GM2 Gangliosidosis
  • Supportive Care
  • Kashan, Isfahan, Iran, Islamic Republic of
  • +2 more
Oct 23, 2022

GM1 Gangliosidoses, GM2 Gangliosidoses, Tay-Sachs Disease Trial in Minneapolis (miglustat, Ketogenic Diet)

Terminated
  • GM1 Gangliosidoses
  • +3 more
  • Minneapolis, Minnesota
    University of Minnesota
Mar 18, 2021

Pompe Disease, Hypersensitivity Reaction Trial (Zavesca® Prescription)

Terminated
  • Pompe Disease
  • Hypersensitivity Reaction
  • Zavesca® Prescription
  • (no location specified)
Dec 4, 2018

Gaucher Disease Trial in Taipei (Miglustat, ERT)

Unknown status
  • Gaucher Disease
  • Taipei, Taiwan
    National Taiwan University Hospital
Mar 28, 2019

Gaucher Disease Type 1 Trial in Worldwide (Miglustat)

Completed
  • Gaucher Disease Type 1
  • San Francisco, California
  • +19 more
Oct 24, 2018

Pompe Disease Undergoing Immune Modulation Therapies

Completed
  • Pompe Disease
  • Gainesville, Florida
    University of Florida
Dec 6, 2017

Gangliosidoses GM2 Trial in Toronto (miglustat)

Completed
  • Gangliosidoses GM2
  • Toronto, Ontario, Canada
    The Hospital for Sick Children
May 18, 2016

Diarrhea Trial in Toronto (Treatment A, Treatment B)

Completed
  • Diarrhea
  • Treatment A
  • Treatment B
  • Toronto, Ontario, Canada
    BioPharma Services Inc.
Mar 9, 2015

Niemann-Pick Type C Disease Trial in New York (miglustat)

Completed
  • Niemann-Pick Type C Disease
  • New York, New York
    Columbia University Medical Center
Mar 24, 2010

Cystic Fibrosis Trial in Barcelona (miglustat, )

Terminated
  • Cystic Fibrosis
  • Barcelona, Spain
    Corporacio Parc Tauli / Parc Tauli Hospital
Feb 11, 2010

Contraception Trial in Seattle (Miglustat (Zavesca))

Completed
  • Contraception
  • Miglustat (Zavesca)
  • Seattle, Washington
    University of Washington
Sep 18, 2008

GM2 Gangliosidoses, Tay-Sachs, Sandhoff Disease Trial in Washington (Zavesca (Miglustat))

Completed
  • GM2 Gangliosidoses
  • +2 more
  • Zavesca (Miglustat)
  • Washington, District of Columbia
    Children's National Medical Center
May 5, 2008