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alpha-Mannosidosis

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Alpha-Mannosidosis Trial in Worldwide (Velmanase Alfa (e.g. Lamazym))

Completed
  • Alpha-Mannosidosis
  • Velmanase Alfa (e.g. Lamazym)
  • Wien, Austria
  • +5 more
Oct 18, 2021

European Alpha-Mannosidosis Participant

Terminated
  • Immunodeficiency
  • +5 more
    • Aachen, Germany
    • +18 more
    Jun 10, 2022

    Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)

    Recruiting
    • Adrenoleukodystrophy
    • +11 more
    • DUOC-01
    • Durham, North Carolina
      Duke University Medical Center
    Oct 24, 2022

    Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

    Recruiting
    • Mucopolysaccharidosis Disorders
    • +28 more
    • Stem Cell Transplantation
    • +7 more
    • Minneapolis, Minnesota
      Masonic Cancer Center, University of Minnesota
    Nov 1, 2022

    Biomarker for Mannosidosis Disease (BioMannosidosis)

    Active, not recruiting
    • Alpha-Mannosidase B Deficiency
    • +2 more
      • Rostock, Germany
      • +2 more
      May 12, 2021

      Alpha-Mannosidosis Trial (Velmanase Alfa, Placebo)

      Withdrawn
      • Alpha-Mannosidosis
      • Velmanase Alfa
      • Placebo
      • (no location specified)
      Dec 4, 2020

      Alpha-Mannosidosis Trial in Copenhagen (Lamazym)

      Completed
      • Alpha-Mannosidosis
      • Copenhagen, Denmark
        Center for Metabolic Diseases, Department of Clinical Genetics,
      Nov 18, 2020

      The Natural History of Metachromatic Leukodystrophy

      Recruiting
      • MLD
      • +26 more
      • Palliative Care
      • Hematopoetic Stem Cell Transplantation
      • Pittsburgh, Pennsylvania
        The Program for the Study of Neurodevelopment in Rare Disorders,
      Nov 2, 2021

      Alpha Mannosidosis Trial (Lamazym)

      Completed
      • Alpha Mannosidosis
      • (no location specified)
      Jul 30, 2020

      The Natural History of Alpha-Mannosidosis

      Completed
      • Alpha Mannosidosis
        • Prague, Czechia
        • +3 more
        Jul 30, 2020

        Alpha-Mannosidosis Trial in Worldwide (Lamazym, Placebo)

        Completed
        • Alpha-Mannosidosis
        • Copenhagen, Denmark
        • +5 more
        Jul 30, 2020

        Clinical Biomarkers in Alpha-mannosidosis

        Completed
        • Alpha-Mannosidosis
          • Bethesda, Maryland
            National Institutes of Health Clinical Center, 9000 Rockville Pi
          Nov 30, 2019

          Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

          Recruiting
          • Primary Immunodeficiency (PID)
          • +4 more
          • data collection
          • Pittsburgh, Pennsylvania
            UPMC Children's Hospital of Pittsburgh
          Feb 9, 2022

          Motor Development of Normal Children

          Not yet recruiting
          • Motor Development
          • The Bruininks-Oseretsky Test of Motor Proficiency, Second Edition
          • Cairo, Egypt
            Faculty of physical therapy,Cairo university
          Jul 8, 2023

          Hepatitis B, Chronic Trial in Worldwide (JNJ-73763989, PegIFN-alpha-2a, Tenofovir disoproxil)

          Terminated
          • Hepatitis B, Chronic
          • Hillsborough, New Jersey
          • +11 more
          Dec 28, 2022

          Screening for Alpha Thalassemia in Healthy Volunteers

          Recruiting
          • Alpha Thalassemia
            • Bethesda, Maryland
              National Institutes of Health Clinical Center
            Jan 26, 2023

            Frontal Alpha Asymmetry and Pediatric Emergence Delirium

            Not yet recruiting
            • Emergence Delirium
            • Ophthalmic surgery
            • General anesthesia
            • (no location specified)
            Apr 5, 2023

            Allergic Bronchiolitis Trial (Serum)

            Not yet recruiting
            • Allergic Bronchiolitis
            • Serum
            • (no location specified)
            Nov 14, 2023

            Alpha-1 Antitrypsin Deficiency Trial in Gainesville (Alpha-1 Antitrypsin Genotype)

            Recruiting
            • Alpha-1 Antitrypsin Deficiency
            • Alpha-1 Antitrypsin Genotype
            • Gainesville, Florida
              University of Florida
            Nov 2, 2022

            Rheumatoid Arthritis Trial in Canada, United States (ISIS 104838)

            Completed
            • Rheumatoid Arthritis
            • ISIS 104838
            • Birmingham, Alabama
            • +30 more
            Dec 1, 2022

            Pancreatic Cancer, Unresectable Pancreatic Cancer, Pancreatic Adenocarcinoma Trial (DaRT seeds insertion)

            Not yet recruiting
            • Pancreatic Cancer
            • +2 more
            • DaRT seeds insertion
            • (no location specified)
            Sep 5, 2023

            Pancreatic Ductal Adenocarcinoma, Gastroesophageal Adenocarcinoma, Glioblastoma Multiforme Trial (68Ga-FF58, 177Lu-FF58)

            Not yet recruiting
            • Pancreatic Ductal Adenocarcinoma
            • +2 more
            • (no location specified)
            Jul 28, 2023

            Arthritis, Psoriatic Trial in Worldwide (Guselkumab, Golimumab, Placebo)

            Recruiting
            • Arthritis, Psoriatic
            • Phoenix, Arizona
            • +96 more
            Jan 17, 2023

            Iron, Alpha-Synuclein, and Lymphocyte-activation Gene-3 in

            Not yet recruiting
            • Brain Ischemia
            • Serum Iron
            • +7 more
            • Aswan, Egypt
              Aswan University Hospital
            Mar 7, 2023

            Stone, Urinary Trial in Hong Kong (Silodosin, Tamsulosin)

            Recruiting
            • Stone, Urinary
            • Hong Kong, Hong Kong
              Hong Kong
            Oct 3, 2022