alpha-Mannosidosis
Showing 1 - 25 of 2,661
Alpha-Mannosidosis Trial in Worldwide (Velmanase Alfa (e.g. Lamazym))
Completed
- Alpha-Mannosidosis
- Velmanase Alfa (e.g. Lamazym)
-
Wien, Austria
- +5 more
Oct 18, 2021
European Alpha-Mannosidosis Participant
Terminated
- Immunodeficiency
- +5 more
-
Aachen, Germany
- +18 more
Jun 10, 2022
Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)
Recruiting
- Adrenoleukodystrophy
- +11 more
- DUOC-01
-
Durham, North CarolinaDuke University Medical Center
Oct 24, 2022
Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD
Recruiting
- Mucopolysaccharidosis Disorders
- +28 more
- Stem Cell Transplantation
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Nov 1, 2022
Biomarker for Mannosidosis Disease (BioMannosidosis)
Active, not recruiting
- Alpha-Mannosidase B Deficiency
- +2 more
-
Rostock, Germany
- +2 more
May 12, 2021
Alpha-Mannosidosis Trial (Velmanase Alfa, Placebo)
Withdrawn
- Alpha-Mannosidosis
- Velmanase Alfa
- Placebo
- (no location specified)
Dec 4, 2020
Alpha-Mannosidosis Trial in Copenhagen (Lamazym)
Completed
- Alpha-Mannosidosis
-
Copenhagen, DenmarkCenter for Metabolic Diseases, Department of Clinical Genetics,
Nov 18, 2020
The Natural History of Metachromatic Leukodystrophy
Recruiting
- MLD
- +26 more
- Palliative Care
- Hematopoetic Stem Cell Transplantation
-
Pittsburgh, PennsylvaniaThe Program for the Study of Neurodevelopment in Rare Disorders,
Nov 2, 2021
The Natural History of Alpha-Mannosidosis
Completed
- Alpha Mannosidosis
-
Prague, Czechia
- +3 more
Jul 30, 2020
Clinical Biomarkers in Alpha-mannosidosis
Completed
- Alpha-Mannosidosis
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Nov 30, 2019
Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Recruiting
- Primary Immunodeficiency (PID)
- +4 more
- data collection
-
Pittsburgh, PennsylvaniaUPMC Children's Hospital of Pittsburgh
Feb 9, 2022
Motor Development of Normal Children
Not yet recruiting
- Motor Development
- The Bruininks-Oseretsky Test of Motor Proficiency, Second Edition
-
Cairo, EgyptFaculty of physical therapy,Cairo university
Jul 8, 2023
Screening for Alpha Thalassemia in Healthy Volunteers
Recruiting
- Alpha Thalassemia
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 26, 2023
Frontal Alpha Asymmetry and Pediatric Emergence Delirium
Not yet recruiting
- Emergence Delirium
- Ophthalmic surgery
- General anesthesia
- (no location specified)
Apr 5, 2023
Allergic Bronchiolitis Trial (Serum)
Not yet recruiting
- Allergic Bronchiolitis
- Serum
- (no location specified)
Nov 14, 2023
Alpha-1 Antitrypsin Deficiency Trial in Gainesville (Alpha-1 Antitrypsin Genotype)
Recruiting
- Alpha-1 Antitrypsin Deficiency
- Alpha-1 Antitrypsin Genotype
-
Gainesville, FloridaUniversity of Florida
Nov 2, 2022
Rheumatoid Arthritis Trial in Canada, United States (ISIS 104838)
Completed
- Rheumatoid Arthritis
- ISIS 104838
-
Birmingham, Alabama
- +30 more
Dec 1, 2022
Pancreatic Cancer, Unresectable Pancreatic Cancer, Pancreatic Adenocarcinoma Trial (DaRT seeds insertion)
Not yet recruiting
- Pancreatic Cancer
- +2 more
- DaRT seeds insertion
- (no location specified)
Sep 5, 2023
Pancreatic Ductal Adenocarcinoma, Gastroesophageal Adenocarcinoma, Glioblastoma Multiforme Trial (68Ga-FF58, 177Lu-FF58)
Not yet recruiting
- Pancreatic Ductal Adenocarcinoma
- +2 more
- (no location specified)
Jul 28, 2023
Iron, Alpha-Synuclein, and Lymphocyte-activation Gene-3 in
Not yet recruiting
- Brain Ischemia
- Serum Iron
- +7 more
-
Aswan, EgyptAswan University Hospital
Mar 7, 2023