mucopolysaccharidosis
Showing 201 - 205 of 205
Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase)
Completed
- Mucopolysaccharidosis VI
- N-acetylgalactosamine 4-sulfatase
-
Novato, CaliforniaBioMarin Pharmaceutical Inc.
Aug 24, 2009
Morquio's Disease Trial (physiotherapeutic treatment)
Terminated
- Morquio's Disease
- physiotherapeutic treatment
- (no location specified)
Oct 17, 2008
Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase)
Completed
- Mucopolysaccharidosis VI
- N-acetylgalactosamine 4-sulfatase
-
Novato, CaliforniaBioMarin Pharmaceutical Inc.
Nov 2, 2006
Mucopolysaccharidosis II Trial in Minneapolis (lymphocyte gene therapy)
Completed
- Mucopolysaccharidosis II
- lymphocyte gene therapy
-
Minneapolis, MinnesotaUniversity of Minnesota Medical School
Jun 23, 2005
Pulmonary Complications in Pediatric Storage Disorders
Unknown status
- I Cell Disease
- +11 more
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Minneapolis, MinnesotaFairview University Medical Center
Jun 23, 2005