A Long-term Study for the Outcome of Pompe Disease
Sponsor
National Taiwan University Hospital (Other)
Overall Status
Recruiting
CT.gov ID
NCT02399748
Collaborator
(none)
50
1
236
0.2
Study Details
Study Description
Brief Summary
Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.
| Condition or Disease | Intervention/Treatment | Phase |
|---|---|---|
|
|
Study Design
Study Type:
Observational
Anticipated Enrollment
:
50 participants
Observational Model:
Case-Only
Time Perspective:
Prospective
Official Title:
A Long-term Study for the Outcome of Pompe Disease
Study Start Date
:
Apr 1, 2007
Anticipated Primary Completion Date
:
Dec 1, 2026
Anticipated Study Completion Date
:
Dec 1, 2026
Outcome Measures
Primary Outcome Measures
- all cause morbidities [10 years]
Eligibility Criteria
Criteria
Ages Eligible for Study:
N/A
and Older
Sexes Eligible for Study:
All
Accepts Healthy Volunteers:
No
Inclusion Criteria:
Confirm diagnosis with Pompe disease, is or is preparing receiving enzyme replacement therapy
Exclusion Criteria:
No
Contacts and Locations
Locations
| Site | City | State | Country | Postal Code | |
|---|---|---|---|---|---|
| 1 | National Taiwan University Hospital | Taipei | Taiwan | 100 |
Sponsors and Collaborators
- National Taiwan University Hospital
Investigators
- Principal Investigator: Yin-Hsiu Chien, National Taiwan University Hospital
Study Documents (Full-Text)
None provided.More Information
Publications
None provided.Responsible Party:
National Taiwan University Hospital
ClinicalTrials.gov Identifier:
NCT02399748
Other Study ID Numbers:
- 200703045R
First Posted:
Mar 26, 2015
Last Update Posted:
Jul 18, 2017
Last Verified:
Jul 1, 2017
Additional relevant MeSH terms: