Tay Sachs
Showing 26 - 50 of 53
Autism Spectrum Disorder, MDD Trial in Toronto (Active Bilateral Theta Burst Stimulation, Sham Bilateral Theta Burst
Recruiting
- Autism Spectrum Disorder
- Major Depressive Disorder
- Active Bilateral Theta Burst Stimulation
- Sham Bilateral Theta Burst Stimulation
-
Toronto, Ontario, CanadaCentre for Addiction and Mental Health
Jul 12, 2021
Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (Stem Cell Transplant,
Completed
- Adrenoleukodystrophy
- +10 more
- Stem Cell Transplant
- Busulfan, Cyclophosphamide, Antithymocyte Globulin
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Dec 3, 2017
Youth Incarceration, Health Care Utilization Trial in Los Angeles (Whole Person Care (WPC) Reentry Program)
Active, not recruiting
- Youth Incarceration
- Health Care Utilization
- Whole Person Care (WPC) Reentry Program
-
Los Angeles, CaliforniaLos Angeles County Jails
Jun 6, 2022
Respiratory Disease, Respiratory Infections in Children Trial in Hanoi (0.9% NaCl physiological saline, Probiotic 1, Probiotic
Not yet recruiting
- Respiratory Disease
- Respiratory Infections in Children
- 0.9% NaCl physiological saline
- +2 more
-
Hanoi, VietnamSon Tay Province, Hanoi
Nov 18, 2023
Tay Sachs Disease, Canavan Disease, Familial Dysautonomia Trial in Montreal (Online pre-test genetic education tool)
Completed
- Tay Sachs Disease
- +2 more
- Online pre-test genetic education tool
-
Montreal, Quebec, CanadaMontreal General Hospital (MUHC)
Aug 14, 2017
Migraine Trial in Philadelphia (Migranal nasal spray at 1 hour, Migranal nasal spray at 4 hour)
Completed
- Migraine
- Migranal nasal spray at 1 hour
- Migranal nasal spray at 4 hour
-
Philadelphia, PennsylvaniaJefferson Headache Center
Feb 28, 2022
Community-acquired Pneumonia Trial in Stockholm
Completed
- Community-acquired Pneumonia
-
Stockholm, SwedenSachs' Children and Youth Hospital
Nov 20, 2020
Mental Health Literacy, Depression Literacy, Psychological Well-being Trial (Online HOPE intervention)
Unknown status
- Mental Health Literacy
- +3 more
- Online HOPE intervention
- (no location specified)
Feb 9, 2020
Breast Cancer Trial in New York (RealRisks)
Completed
- Breast Cancer
- RealRisks
-
New York, New YorkColumbia University Medical Center
Jan 30, 2019
Gangliosidoses GM2 Trial in Toronto (miglustat)
Completed
- Gangliosidoses GM2
-
Toronto, Ontario, CanadaThe Hospital for Sick Children
May 18, 2016
Dyslipidemias, Cardiovascular Risk Factor Trial in Mexico City (L-Carnitine 500Mg Oral Tablet + Atorvastatin 10 mg, Atorvastatin
Unknown status
- Dyslipidemias
- Cardiovascular Risk Factor
- L-Carnitine 500Mg Oral Tablet + Atorvastatin 10 mg
- Atorvastatin 10mg
-
Mexico City, MexicoLaboratorios Grossman Sa
Feb 25, 2019
Lysosomal Storage Disease, Peroxisomal Disorder Trial in Minneapolis (drug, radiation, biological)
Completed
- Lysosomal Storage Disease
- Peroxisomal Disorder
- Campath-1H
- +6 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Dec 3, 2017
Lysosomal Storage Diseases, Inborn Errors of Metabolism Trial in Durham (ALD-601)
Withdrawn
- Lysosomal Storage Diseases
- Inborn Errors of Metabolism
- ALD-601
-
Durham, North Carolina
- +1 more
Jun 27, 2017
Human Movement Patterns on the Thailand-Myanmar Border
Completed
- Epidemiology
-
Mae Sot, Tak, ThailandShoklo Malaria Research Unit
Jan 7, 2019
Gene Therapy for Tay-Sachs Disease
Completed
- Tay Sachs Disease
- +2 more
-
Tampa, Florida
- +1 more
Dec 3, 2014
Phosphoglycerate Kinase (PGK) Deficiency Trial in Nashville (Unrelated Donor BMT)
Completed
- Phosphoglycerate Kinase (PGK) Deficiency
- Unrelated Donor BMT
-
Nashville, TennesseeVanderbilt Children's Hospital
Nov 22, 2016
Severe Hepatic Veno-Occlusive Disease Trial in Canada, United States (Defibrotide)
Completed
- Severe Hepatic Veno-Occlusive Disease
-
Duarte, California
- +24 more
Dec 2, 2016
Any Single Gene Disorder (Cystic Fibrosis, Tay-Sachs) Trial in Redwood City (preimplantation diagnosis)
Completed
- Any Single Gene Disorder (Cystic Fibrosis, Tay-Sachs)
- preimplantation diagnosis
-
Redwood City, CaliforniaGene Security Network
Apr 1, 2014
Patients With Gaucher Disease and Hepatitis C
Unknown status
- Gaucher Disease
- Hepatitis C
-
Jerusalem, Israel
- +1 more
Nov 18, 2014
Inherited Metabolic Diseases, Lysosomal Storage Disorders, Peroxisomal Storage Diseases Trial in Los Angeles, New York, Durham
Terminated
- Inherited Metabolic Diseases
- +4 more
- ALD-101
-
Los Angeles, California
- +2 more
Jul 7, 2014
Migraine Trial in Philadelphia (dihydroergotamine mesylate)
Completed
- Migraine
- dihydroergotamine mesylate
-
Philadelphia, PennsylvaniaJefferson Headache Center
May 8, 2014
Clinical Use of Parental Support To Detect Single Gene Mutations
Completed
- Single Gene Disorders
- Preimplantation Genetic Diagnosis
-
Redwood City, CaliforniaGene Security Network
Jul 12, 2013
Gangliosidoses, GM2, Sandhoff Disease, Tay-Sachs Disease Trial in Toronto (Pyrimethamine, Leucovorin)
Completed
- Gangliosidoses, GM2
- +2 more
-
Toronto, Ontario, CanadaThe Hospital for Sick Children
Feb 22, 2012