spinal muscular atrophy
Showing 51 - 75 of 117
Spinal Muscular Atrophy Trial in Worldwide (nusinersen)
Active, not recruiting
- Spinal Muscular Atrophy
-
Los Angeles, California
- +46 more
Nov 7, 2021
Public AttitudesTowards SMA and DMD Awareness, Newborn and
Not yet recruiting
- Spinal Muscular Atrophy
- +2 more
- Questionnaire
- (no location specified)
Nov 8, 2021
(MUNE) in Adults With Spinal Muscular Atrophy (SMA)
Recruiting
- Spinal Muscular Atrophy
-
Columbus, OhioThe Ohio State University Medical Center
Nov 3, 2021
Spinal Muscular Atrophy Trial in France
Completed
- Spinal Muscular Atrophy
-
Brest, France
- +5 more
Sep 10, 2021
Spinraza in Adult Spinal Muscular Atrophy
Active, not recruiting
- Spinal Muscular Atrophy
- +2 more
- Observational study to examine safety, tolerability, and effectiveness of SPINRAZA® prescribed as part of standard of care
-
Phoenix, Arizona
- +10 more
Jul 1, 2021
Spinal Muscular Atrophy Trial in Paris (Motor function measurement using inertial sensors)
Not yet recruiting
- Spinal Muscular Atrophy
- Motor function measurement using inertial sensors
-
Paris, FranceHôpital Necker-Enfants Malades
Jun 26, 2021
Spinal Muscular Atrophy Trial in New York (Nusinersen Treatments)
Withdrawn
- Spinal Muscular Atrophy
- Nusinersen Treatments
-
New York, New YorkNYU Langone Health
Jun 25, 2021
Spinal Muscular Atrophy Trial in Liège (Actimyo)
Enrolling by invitation
- Spinal Muscular Atrophy
- Actimyo
-
Liège, BelgiumCentre Hospitalier Régional de la Citadelle
May 11, 2021
Spinal Muscular Atrophy Trial in Brazil (Nusinersen Injectable Product)
Completed
- Spinal Muscular Atrophy
- Nusinersen Injectable Product
-
Belo Horizonte, Brazil
- +8 more
Apr 23, 2021
Spinal Muscular Atrophy Trial in Ratchathewi
Recruiting
- Spinal Muscular Atrophy
-
Ratchathewi, Bangkok, ThailandFaculty of Medicine, Ramathibodi Hospital, Mahidol University
Apr 21, 2021
Genetics of Pediatric-Onset Motor Neuron and Neuromuscular
Recruiting
- Spinal Muscular Atrophy
- +7 more
- sample collection
-
Wilmington, Delaware
- +2 more
Mar 10, 2021
Sun May Arise on SMA : Newborn Screening of Spinal Muscular
Completed
- Spinal Muscular Atrophy
- test for SMN1 exon 7 deletion
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Mar 8, 2021
Spinal Muscular Atrophy Trial in Giessen (Flexible Endoscopic Evaluation of Swallowing)
Active, not recruiting
- Spinal Muscular Atrophy
- Flexible Endoscopic Evaluation of Swallowing
-
Giessen, Hesse, GermanyUniversity Hospital Giessen and Marburg, Campus Giessen
Feb 25, 2021
Osteopenia, Spinal Muscular Atrophy, Cerebral Palsy Trial in Saint Paul (Assisted Standing Treatment Program)
Completed
- Osteopenia
- +5 more
- Assisted Standing Treatment Program
-
Saint Paul, MinnesotaGillette Children's Specialty Healthcare
Feb 19, 2021
Spinal Muscular Atrophy Trial in Germany, United States (Nusinersen, Sham Procedure)
Terminated
- Spinal Muscular Atrophy
- Nusinersen
- Sham Procedure
-
Los Angeles, California
- +6 more
Feb 12, 2021
Spinal Muscular Atrophy Trial in Worldwide (nusinersen, Sham procedure)
Terminated
- Spinal Muscular Atrophy
- nusinersen
- Sham procedure
-
Los Angeles, California
- +30 more
Feb 12, 2021
Spinal Muscular Atrophy Trial in Worldwide (Nusinersen, Sham procedure)
Completed
- Spinal Muscular Atrophy
- Nusinersen
- Sham procedure
-
Los Angeles, California
- +23 more
Feb 12, 2021
Clinical Study of Spinal Muscular Atrophy
Active, not recruiting
- Spinal Muscular Atrophy
-
New York, New YorkColumbia University SMA Clinical Research Center
Jan 14, 2021
MFM-20 in SMA Patients Treated With Nusinersen
Not yet recruiting
- Spinal Muscular Atrophy
-
Angers, France
- +7 more
Nov 20, 2020
Muscular Diseases, Spinal Muscular Atrophy Trial in Erlangen (Multispectral Optoacoustic Tomography (MSOT))
Completed
- Muscular Diseases
- Spinal Muscular Atrophy
- Multispectral Optoacoustic Tomography (MSOT)
-
Erlangen, Bavaria, GermanyDepartment of Pediatrics and Adolescent Medicine
Nov 17, 2020