spinal muscular atrophy
Showing 76 - 100 of 117
Spinal Muscular Atrophy Trial in Dallas (Risdiplam, Midazolam)
Completed
- Spinal Muscular Atrophy
-
Dallas, TexasCovance Research Unit - Dallas
Sep 23, 2020
Duchenne Muscular Dystrophy, Spinal Muscular Atrophy, Congenital Muscular Dystrophy Trial (2011-2012 seasonal flu vaccine
Completed
- Duchenne Muscular Dystrophy
- +2 more
- 2011-2012 seasonal flu vaccine Subcutaneous
- 2011-2012 seasonal flu vaccine Intramuscular
- (no location specified)
Oct 14, 2020
Spinal Muscular Atrophy Trial in Canada, United States (Placebo, Reldesemtiv 150 mg, Reldesemtiv 450 mg)
Completed
- Spinal Muscular Atrophy
- Placebo
- +2 more
-
Los Angeles, California
- +18 more
Aug 21, 2020
Spinal Muscular Atrophy Trial in Columbus (AVXS-101)
Approved for marketing
- Spinal Muscular Atrophy
- AVXS-101
-
Columbus, OhioNationwide Children's Hospital
Aug 26, 2020
The Burden of Primary Caregivers of Spinal Muscular Atrophy
Completed
- Spinal Muscular Atrophy
- Caregiver Burden
- Zarit Burden Interview Scale
- +3 more
-
Istanbul, TurkeyMarmara University School of Medicine Department of Physical Med
May 12, 2020
Muscular Diseases, Spinal Muscular Atrophy Trial in Erlangen (Multispectral Optoacoustic Tomography (MSOT) and Magnetic
Unknown status
- Muscular Diseases
- Spinal Muscular Atrophy
- Multispectral Optoacoustic Tomography (MSOT) and Magnetic Resonance Imaging (MRI)
-
Erlangen, GermanyUniversity Hospital Erlangen
Feb 26, 2020
Mechanisms of Cell Death in Spinal Muscular Atrophy
Completed
- Spinal Muscular Atrophy
-
Wilmington, Delaware
- +1 more
Feb 19, 2020
Infants With Spinal Muscular Atrophy Type I
Terminated
- Spinal Muscular Atrophy
-
Bethesda, MarylandNational Institute of Neurological Disorders and Stroke (NINDS),
Dec 11, 2019
SMN Copy Number Distribution in Mali, West Africa
Completed
- Spinal Muscular Atrophy
-
Bamako, MaliUniversity of Bamako, Faculty of Medicine, Pharmacy and Dentistr
Dec 4, 2019
Spinal Muscular Atrophy, Assessment, Self Trial in Garches (Motor assessment)
Completed
- Spinal Muscular Atrophy
- Assessment, Self
- Motor assessment
-
Garches, France
- +1 more
Nov 22, 2019
Neonatal Spinal Muscular Atrophy (SMA) Screening
Unknown status
- Spinal Muscular Atrophy
- SMA Newborn Screening
-
Kaohsiung, TaiwanKaohsiung Medical University Chung-Ho Memorial Hospital
Jul 24, 2019
Natural History of Types 2 and 3 SMA in Taiwan
Unknown status
- Spinal Muscular Atrophy
-
Kaohsiung, TaiwanKaohsiung Medical University Chung-Ho Memorial Hospital
Jul 24, 2019
Spinal Muscular Atrophy Trial in Nantes, Rouen (blood sampling)
Terminated
- Spinal Muscular Atrophy
- blood sampling
-
Nantes, France
- +1 more
Jul 23, 2019
Spinal Muscular Atrophy, Merosin Deficient Congenital Muscular Dystrophy Trial in Copenhagen (Fasting)
Completed
- Spinal Muscular Atrophy
- Merosin Deficient Congenital Muscular Dystrophy
- Fasting
-
Copenhagen, DenmarkCopenhagen Neuromuscular Center
May 29, 2019
Spinal Muscular Atrophy, Neuromuscular Disorders Trial in Kharkiv (Direct current stimulation of cervical spinal cord)
Withdrawn
- Spinal Muscular Atrophy
- Neuromuscular Disorders
- Direct current stimulation of cervical spinal cord
-
Kharkiv, UkraineSI "Institute of Neurology, Psychiatry and Narcology of NAMS of
Feb 12, 2019
ACTIVE-mini for Quantifying Movement in Infants With Spinal
Completed
- Spinal Muscular Atrophy
- ACTIVE mini
- (no location specified)
Jan 14, 2019
Spinal Muscular Atrophy Trial in Groningen (Itraconazole, Placebo, Risdiplam)
Completed
- Spinal Muscular Atrophy
- Itraconazole
- +2 more
-
Groningen, NetherlandsPra International Group B.V
Oct 2, 2018
Spinal Muscular Atrophy, SMA, Kugelberg-Welander Disease Trial in Utrecht (Pyridostigmine, Placebo)
Completed
- Spinal Muscular Atrophy
- +2 more
- Pyridostigmine
- Placebo
-
Utrecht, NetherlandsUniversity Medical Center of Utrecht (UMCU)
Feb 1, 2018
Measuring Levels of SMN in Blood Samples of SMA Patients
Completed
- Spinal Muscular Atrophy
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Oct 5, 2017
Spinal Muscular Atrophy Trial in Columbus (Valproic Acid (VPA), Placebo)
Completed
- Spinal Muscular Atrophy
- Valproic Acid (VPA)
- Placebo
-
Columbus, OhioOhio State University Medical Center, Dept. of Neurology
Dec 5, 2016
Newborn Screening for Spinal Muscular Atrophy
Completed
- Spinal Muscular Atrophy
- newborn screening test for SMA
-
Taipei, Taiwan,, TaiwanNational Taiwan University Hospital
Oct 31, 2016
Spinal Muscular Atrophy Trial in Salt Lake City (Valproic Acid)
Completed
- Spinal Muscular Atrophy
- Valproic Acid
-
Salt Lake City, UtahUniversity of Utah/Primary Children's Medical Center
Aug 22, 2016
Spinal Muscular Atrophy, Neuromuscular Disease Trial in New York (Exercise)
Completed
- Spinal Muscular Atrophy
- Neuromuscular Disease
- Exercise
-
New York, New YorkColumbia University SMA Clinical Research Center
Aug 11, 2016
Spinal Muscular Atrophy Trial in New York (4-aminopyridine, Placebo)
Completed
- Spinal Muscular Atrophy
- 4-aminopyridine
- Placebo
-
New York, New YorkColumbia University Medical Center
May 17, 2016
Cerebral Palsy, Arthrogryposis, Spinal Muscular Atrophy Trial in Oklahoma City (Power mobility)
Completed
- Cerebral Palsy
- +3 more
- Power mobility
-
Oklahoma City, OklahomaDepartment of Rehabilitation Sciences, Lee Mitchener Tolbert Cen
Jan 13, 2016